DMD Voice: Qualitative Interviews With Patients and Caregivers
NCT ID: NCT06925269
Last Updated: 2025-04-30
Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.
RECRUITING
68 participants
OBSERVATIONAL
2025-03-31
2026-12-31
Brief Summary
Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.
This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.
Related Clinical Trials
Explore similar clinical trials based on study characteristics and research focus.
Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of Families
NCT03680365
Longitudinal Study of the Natural History of Duchenne Muscular Dystrophy (DMD)
NCT00468832
Correlation Between Functional Capacity and Functional Capability in Duchenne Muscular Dystrophy
NCT05249361
Breathlessness Assessment in Adult Patients With Myotonic Dystrophy Type 1
NCT04835298
phenotypeS in Non Ambulant Duchenne Muscular Dystrophy
NCT06366815
Detailed Description
Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.
Conditions
See the medical conditions and disease areas that this research is targeting or investigating.
Study Design
Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.
COHORT
RETROSPECTIVE
Study Groups
Review each arm or cohort in the study, along with the interventions and objectives associated with them.
Subsample A - Caregivers
Caregivers of individuals with DMD treated with givinostat for at least 2 years
No interventions assigned to this group
Subsample A - Patients
Patients with DMD treated with givinostat for at least 2 years
No interventions assigned to this group
Subsample B - Caregivers
Caregivers of individuals with DMD never treated with givinostat
No interventions assigned to this group
Eligibility Criteria
Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.
Inclusion Criteria
Eligible participants for Subsample A must:
* Have been treated with Givinostat for at least 2 years
* Be at least 10 years of age with signed consent of a parent or legal guardian
* Be currently taking givinostat
* Willing and able to participate in a video and/or audio recorded interview
Subsample A - Caregivers
Eligible caregivers for Subsample A must:
* Be a parent or legal guardian of an individual with DMD that has been taking givinostat for at least two years
* Willing and able to participate in a video and/or audio recorded interview
Subsample B - Caregivers
Eligible caregivers for Subsample B must:
* Provide care to an individual with DMD who is unable to raise their hands above their head as confirmed by the caregiver
* Reside in the United States or Canada
* Able to read, speak, and understand English
* Willing and able to participate in a video and/or audio recorded interview Have access to a stable internet connection
Exclusion Criteria
10 Years
MALE
No
Sponsors
Meet the organizations funding or collaborating on the study and learn about their roles.
Italfarmaco S.A
INDUSTRY
Red Nucleus Enterprise Solutions, LLC
INDUSTRY
Responsible Party
Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.
Principal Investigators
Learn about the lead researchers overseeing the trial and their institutional affiliations.
Mindy Leffler, M.Ed.
Role: PRINCIPAL_INVESTIGATOR
Red Nucleus Solutions
Locations
Explore where the study is taking place and check the recruitment status at each participating site.
Red Nucleus
Yardley, Pennsylvania, United States
Countries
Review the countries where the study has at least one active or historical site.
Central Contacts
Reach out to these primary contacts for questions about participation or study logistics.
Facility Contacts
Find local site contact details for specific facilities participating in the trial.
Other Identifiers
Review additional registry numbers or institutional identifiers associated with this trial.
CAS-ITF001-01
Identifier Type: -
Identifier Source: org_study_id
More Related Trials
Additional clinical trials that may be relevant based on similarity analysis.