The Burden of Access in Duchenne Muscular Dystrophy in the US

NCT ID: NCT03951675

Last Updated: 2020-08-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

57 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-06-18

Study Completion Date

2020-05-28

Brief Summary

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This study is being conducted to determine if DMD patients / families and healthcare providers experience burdens related to access, and if so, to identify them, and to determine life impacts to the patient, if any, of these burdens. Data from healthcare providers will be collected by an online survey and from patients/families by one on one telephone interview.

Detailed Description

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Patient/Parent Portion

In this non-interventional study, DMD patients / parents of DMD patients will be interviewed to gather qualitative input, in the patient's voice, regarding challenges associated with access to medications, services and medical equipment, and how these burdens impact quality of life.

Healthcare Provider Portion

In this non-interventional study, healthcare providers who see patients with DMD and who deal with insurance issues on behalf of DMD patients will participate in an online survey designed to determine the burden associated with access to medications, services and medical equipment.

Conditions

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Duchenne Muscular Dystrophy

Study Design

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Observational Model Type

CASE_CONTROL

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Individuals Living with DMD

90 patients/parents

No interventions assigned to this group

Healthcare Providers to Patients with DMD

40 healthcare providers

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

Patient/Parent interviews

* Patients residing in the US who have been diagnosed with DMD who are age 18 years or older, or the parent / legal guardian of a person of any age who has been diagnosed with DMD,
* Have provide "Proof of DMD" to ensure that they are impacted by the disease,
* Who have provided sufficient information in the RSVP process to determine their functional status; ambulatory, transitional or non-ambulatory,
* State that they are the person who deals with insurance issues for the affected patient and,
* Who are able to understand and consent to participation in the study

Healthcare Provider survey

* Healthcare providers (physicians, nurse practitioners, and physician assistants) currently involved in the care of patients with DMD
* Are currently practicing in the US,
* Who have provided sufficient information in the survey screening to determine that they currently care for DMD patients,
* State that they and/or persons on their staff interface with insurance companies for DMD patients related to access to medications, services and/or medical equipment and,
* Who are able to understand and consent to participation in the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Engage Health Inc.

INDUSTRY

Sponsor Role collaborator

University of Florida

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kara Godwin, MSN,APRN

Role: PRINCIPAL_INVESTIGATOR

University of Florida

Locations

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University of Florida

Gainesville, Florida, United States

Site Status

Countries

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United States

Other Identifiers

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LHF0001

Identifier Type: OTHER

Identifier Source: secondary_id

OCR21561

Identifier Type: -

Identifier Source: org_study_id

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