Extension Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy

NCT ID: NCT01239758

Last Updated: 2013-02-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

11 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-10-31

Study Completion Date

2011-05-31

Brief Summary

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To evaluate the long-term safety and tolerability of ACE-031 administration in subjects with Duchenne muscular dystrophy (DMD) who participated in Study A031-03. \[Note: This study was terminated based on preliminary safety data. Pending further analysis of safety data and discussion with health authorities, a new ACE-031 trial will be planned.\]

Detailed Description

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Conditions

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Duchenne Muscular Dystrophy

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ACE-031 (Extension of cohort 1 from core study, A031-03)

Group Type EXPERIMENTAL

ACE-031 (Extension of cohort 1 from core study, A031-03)

Intervention Type BIOLOGICAL

ACE-031 0.5 mg/kg subcutaneously once every 4 weeks for 24 weeks.

ACE-031 (Extension of cohort 2 from core study, A031-03)

Group Type EXPERIMENTAL

ACE-031 (Extension of cohort 2 from core study, A031-03)

Intervention Type BIOLOGICAL

Up to 1.0 mg/kg subcutaneously once every 2 weeks for 24 weeks.

ACE-031 (Extension of cohort 3 from core study, A031-03)

Group Type EXPERIMENTAL

ACE-031 (Extension of cohort 3 from core study, A031-03)

Intervention Type BIOLOGICAL

Up to 2.5 mg/kg subcutaneously once every 4 weeks for 24 weeks.

Interventions

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ACE-031 (Extension of cohort 1 from core study, A031-03)

ACE-031 0.5 mg/kg subcutaneously once every 4 weeks for 24 weeks.

Intervention Type BIOLOGICAL

ACE-031 (Extension of cohort 2 from core study, A031-03)

Up to 1.0 mg/kg subcutaneously once every 2 weeks for 24 weeks.

Intervention Type BIOLOGICAL

ACE-031 (Extension of cohort 3 from core study, A031-03)

Up to 2.5 mg/kg subcutaneously once every 4 weeks for 24 weeks.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Completion of participation in Study A031-03 and Investigator approval
* Continuation of corticosteroid therapy at the same absolute dose and schedule as on Study A031-03

Exclusion Criteria

* Participation in any other therapeutic clinical trial
* Plans to have surgery during the course of the study
Minimum Eligible Age

4 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Acceleron Investigative Site

Calgary, Alberta, Canada

Site Status

Acceleron Investigative Site

Hamilton, Ontario, Canada

Site Status

Acceleron Investigative Site

London, Ontario, Canada

Site Status

Acceleron Investigative Site

Ottawa, Ontario, Canada

Site Status

Countries

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Canada

Other Identifiers

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A031-06

Identifier Type: -

Identifier Source: org_study_id

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