Open Label Study of GSK2402968 in Subjects With Duchenne Muscular Dystrophy

NCT ID: NCT01480245

Last Updated: 2017-03-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

233 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-09-30

Study Completion Date

2014-03-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to explore long-term safety, tolerability and efficacy of GSK2402968 in DMD subjects who previously participated in either DMD114117 or DMD114044.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Muscular Dystrophies

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Continuous Dosing

GSK2402968 6mg/kg/week

Group Type EXPERIMENTAL

GSK2402968

Intervention Type DRUG

6mg/kg/week

Intermittent Dosing

GSK2402968 6mg/kg/week

Group Type EXPERIMENTAL

GSK2402968

Intervention Type DRUG

6mg/kg/week

Natural History Observation

The objective of this arm will be to explore DMD disease progression in a naturalistic setting once discontinuing active treatment

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

GSK2402968

6mg/kg/week

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Previous participation in either DMD114117 or DMD114044
* Continued use of glucocorticoids
* Willing and able to comply with all protocol requirements
* Able to give informed consent
* French subjects: Eligible for inclusion only if either affiliated to or a beneficiary of a social security category.

Exclusion Criteria

* Subject experienced a serious adverse event or who met safety stopping criteria that remains unresolved from DMD114117 or DMD114044, which in opinion of the investigator could have been attributable to study medication and is ongoing,
* Use of anticoagulants, antithrombotics or antiplatelet agents, previous treatment with investigational drugs,except GSK2402968, within 1 month of the first administration of study medication,
* Current or anticipated participation in any investigational clinical studies,
* History of significant medical disorder which may confound the interpretation of either efficacy or safety data e.g. current history of renal or liver disease/impairment, history of inflammatory disease.
Minimum Eligible Age

5 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

GlaxoSmithKline

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

GSK Clinical Trials

Role: STUDY_DIRECTOR

GlaxoSmithKline

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

GSK Investigational Site

Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

Site Status

GSK Investigational Site

Westmead, New South Wales, Australia

Site Status

GSK Investigational Site

Parkville, Victoria, Australia

Site Status

GSK Investigational Site

Ghent, , Belgium

Site Status

GSK Investigational Site

Leuven, , Belgium

Site Status

GSK Investigational Site

Curitiba, Paraná, Brazil

Site Status

GSK Investigational Site

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

GSK Investigational Site

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

GSK Investigational Site

Ribeirão Preto, São Paulo, Brazil

Site Status

GSK Investigational Site

Santo André, São Paulo, Brazil

Site Status

GSK Investigational Site

São Paulo, São Paulo, Brazil

Site Status

GSK Investigational Site

Sofia, , Bulgaria

Site Status

GSK Investigational Site

Vancouver, British Columbia, Canada

Site Status

GSK Investigational Site

London, Ontario, Canada

Site Status

GSK Investigational Site

Montreal, Quebec, Canada

Site Status

GSK Investigational Site

Temuco, Región de La Araucania, Chile

Site Status

GSK Investigational Site

Santiago, Región Metro de Santiago, Chile

Site Status

GSK Investigational Site

Santiago, , Chile

Site Status

GSK Investigational Site

Brno, , Czechia

Site Status

GSK Investigational Site

Prague, , Czechia

Site Status

GSK Investigational Site

Koebenhavn Oe, , Denmark

Site Status

GSK Investigational Site

Bordeaux, , France

Site Status

GSK Investigational Site

Lille, , France

Site Status

GSK Investigational Site

Marseille, , France

Site Status

GSK Investigational Site

Montpellier, , France

Site Status

GSK Investigational Site

Nantes, , France

Site Status

GSK Investigational Site

Paris, , France

Site Status

GSK Investigational Site

Paris, , France

Site Status

GSK Investigational Site

Pau, , France

Site Status

GSK Investigational Site

Toulouse, , France

Site Status

GSK Investigational Site

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status

GSK Investigational Site

Munich, Bavaria, Germany

Site Status

GSK Investigational Site

Göttingen, Lower Saxony, Germany

Site Status

GSK Investigational Site

Essen, North Rhine-Westphalia, Germany

Site Status

GSK Investigational Site

Kiel, Schleswig-Holstein, Germany

Site Status

GSK Investigational Site

Budapest, , Hungary

Site Status

GSK Investigational Site

Jerusalem, , Israel

Site Status

GSK Investigational Site

Ferrara, Emilia-Romagna, Italy

Site Status

GSK Investigational Site

Rome, Lazio, Italy

Site Status

GSK Investigational Site

Rome, Lazio, Italy

Site Status

GSK Investigational Site

Milan, Lombardy, Italy

Site Status

GSK Investigational Site

Messina, Sicily, Italy

Site Status

GSK Investigational Site

Hyōgo, , Japan

Site Status

GSK Investigational Site

Kumamoto, , Japan

Site Status

GSK Investigational Site

Saitama, , Japan

Site Status

GSK Investigational Site

Tokyo, , Japan

Site Status

GSK Investigational Site

Leiden, , Netherlands

Site Status

GSK Investigational Site

Nijmegen, , Netherlands

Site Status

GSK Investigational Site

Oslo, , Norway

Site Status

GSK Investigational Site

Warsaw, , Poland

Site Status

GSK Investigational Site

Moscow, , Russia

Site Status

GSK Investigational Site

Seoul, , South Korea

Site Status

GSK Investigational Site

Esplugues de Llobregat. Barcelona, , Spain

Site Status

GSK Investigational Site

Madrid, , Spain

Site Status

GSK Investigational Site

Valencia, , Spain

Site Status

GSK Investigational Site

Kaohsiung City, , Taiwan

Site Status

GSK Investigational Site

Ankara, , Turkey (Türkiye)

Site Status

GSK Investigational Site

London, , United Kingdom

Site Status

GSK Investigational Site

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Argentina Australia Belgium Brazil Bulgaria Canada Chile Czechia Denmark France Germany Hungary Israel Italy Japan Netherlands Norway Poland Russia South Korea Spain Taiwan Turkey (Türkiye) United Kingdom

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

114349

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Extension Study of NS-089/NCNP-02 in DMD
NCT05135663 ACTIVE_NOT_RECRUITING PHASE2
Exploratory Study of NS-089/NCNP-02 in DMD
NCT04129294 COMPLETED PHASE1/PHASE2
Phase I/II Study of SRP-4053 in DMD Patients
NCT02310906 COMPLETED PHASE1/PHASE2