Evaluate the Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
NCT ID: NCT07223489
Last Updated: 2025-10-31
Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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RECRUITING
200 participants
OBSERVATIONAL
2025-10-10
2026-12-30
Brief Summary
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Detailed Description
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Conditions
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Study Design
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CASE_ONLY
RETROSPECTIVE
Interventions
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Telephone Interview
Telephone interviews to gather qualitative data on SMA patients' diagnostic journey, access to treatment and barriers encountered, understanding of their disease, and quality of life measures
Eligibility Criteria
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Inclusion Criteria
Exclusion Criteria
18 Years
ALL
No
Sponsors
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Medstar Health Research Institute
OTHER
Responsible Party
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Nicholas Streicher
Physician
Locations
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MedStar Health Research Institute
Washinton, District of Columbia, United States
Countries
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Central Contacts
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Facility Contacts
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Gabrielle Edwards, BS
Role: primary
Other Identifiers
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ML46436
Identifier Type: -
Identifier Source: org_study_id