Breathlessness Assessment in Adult Patients With Myotonic Dystrophy Type 1
NCT ID: NCT04835298
Last Updated: 2022-06-15
Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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COMPLETED
34 participants
OBSERVATIONAL
2020-07-03
2022-06-14
Brief Summary
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Dyspnea, one of the main respiratory symptoms, has been little studied in patients with DM1.
The main objective of this study is to provide the first multidimensional description of dyspnea in patients with DM1.
The secondary objectives are:
* To compare respiratory symptoms according to the presence or not of criteria from respiratory function testing to initiate NIV
* To assess associations between dyspnea and respiratory function testing
* To assess associations between dyspnea and number of Cytosine Thymine Guanine (CTG) repeats
* To assess associations between dyspnea and muscular strength
* To assess associations between dyspnea and BMI
* To assess associations between dyspnea and anxiety or depression
* To assess associations between dyspnea and cognitive impairment
* To assess associations between dyspnea and quality of life.
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Detailed Description
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Conditions
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Study Design
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CASE_ONLY
PROSPECTIVE
Study Groups
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Myotonic dystrophy type 1
adult patients with myotonic dystrophy type 1
Dyspnea
questionnaires
Interventions
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Dyspnea
questionnaires
Eligibility Criteria
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Inclusion Criteria
* with an age older than 18 years
Exclusion Criteria
* patient already under non-invasive mechanical ventilation
18 Years
ALL
No
Sponsors
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CHU de Reims
OTHER
Responsible Party
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Locations
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Chu Reims
Reims, , France
Countries
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Other Identifiers
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PO20065*
Identifier Type: -
Identifier Source: org_study_id
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