CSL312_3003 Safety and Pharmacokinetic Study in Subjects 2 to 11 Years of Age With Hereditary Angioedema

NCT ID: NCT05819775

Last Updated: 2026-01-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

22 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-30

Study Completion Date

2025-11-19

Brief Summary

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The purpose of this study is to investigate the safety, PK / PD, and efficacy of SC CSL312 for prophylactic treatment of pediatric subjects with HAE.

Detailed Description

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Conditions

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Hereditary Angioedema (HAE)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CSL312

Ages 2-5 years and 6-11 years will have specific subcutaneous dosing schedules

Group Type EXPERIMENTAL

CSL312

Intervention Type BIOLOGICAL

Fully human immunoglobulin G subclass 4/lambda recombinant inhibitor monoclonal antibody administered subcutaneously (SC)

Interventions

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CSL312

Fully human immunoglobulin G subclass 4/lambda recombinant inhibitor monoclonal antibody administered subcutaneously (SC)

Intervention Type BIOLOGICAL

Other Intervention Names

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Garadacimab

Eligibility Criteria

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Inclusion Criteria

* 1\. Male or female
* 2\. Aged 2 to 11 years, inclusive, with body weight ? 10th percentile based on age
* 3\. Diagnosed with clinically confirmed C1-INH HAE
* 4\. Experienced ? 2 HAE attacks during the 6 months before Screening

Exclusion Criteria

* 1\. Concomitant diagnosis of another form of angioedema, such as idiopathic or acquired angioedema, recurrent angioedema associated with urticaria, or HAE type 3
* 2\. Use of C1-INH products, androgens, antifibrinolytics, approved or future approved medications, or other small molecule medications for routine prophylaxis against HAE attacks within a minimum of 2 weeks before the Treatment Period
* 3\. Participation in another interventional clinical study during the 30 days before the Treatment Period or within 5 half-lives of the final dose of the investigational product administered during the previous interventional study, whichever is longer
* 4\. Having laboratory clinical abnormalities assessed as clinically significant by the investigator in results of hematology or chemistry assessments performed during Screening
* 5\. Currently receiving a therapy not permitted during the study
* 6\. Being pregnant or breastfeeding.
Minimum Eligible Age

2 Years

Maximum Eligible Age

11 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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Research Solutions of Arizona

Litchfield Park, Arizona, United States

Site Status

Medical Research of Arizona

Scottsdale, Arizona, United States

Site Status

Donald S. Levy M.D.

Orange, California, United States

Site Status

Raffi Tachdjian MD, Inc.

Santa Monica, California, United States

Site Status

Bernstein Clinical Research

Cincinnati, Ohio, United States

Site Status

PennState Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

Campbelltown Hospital, Western Sydney University

Campbelltown, , Australia

Site Status

Ottawa Allergy Research Corp

Ottawa, , Canada

Site Status

HZRM Hämophilie Zentrum Rhein Main GmbH

Frankfurt am Main, Hesse, Germany

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Frankfurt

Frankfurt am Main, , Germany

Site Status

Barzilai University Medical Center

Ashkelon, , Israel

Site Status

Countries

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United States Australia Canada Germany Israel

Other Identifiers

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2022-502386-13-00

Identifier Type: CTIS

Identifier Source: secondary_id

CSL312_3003

Identifier Type: -

Identifier Source: org_study_id

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