Safety Study in Subjects ≥ 12 Years of Age With Hereditary Angioedema Switching to Garadacimab

NCT ID: NCT06806657

Last Updated: 2025-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE4

Total Enrollment

30 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-19

Study Completion Date

2026-06-15

Brief Summary

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This study is designed to evaluate the safety after switching to garadacimab from another prophylactic hereditary angioedema (HAE) treatment (marketed kallikrein \[KK\] inhibitor or plasma-derived C1-esterase inhibitor \[pdC1INH\]prophylactic) when administered once monthly for approximately 3 months in participants aged greater than or equal to (\>=) 12 years with HAE.

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

PREVENTION

Blinding Strategy

NONE

Study Groups

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Garadacimab

Group Type EXPERIMENTAL

Garadacimab

Intervention Type BIOLOGICAL

Participants will receive a loading dose of garadacimab, followed by once monthly garadacimab administration for 2 months. Garadacimab will be given as a subcutaneous injection. The timing for the administration of the loading dose (first administration of garadacimab) is determined by the dosing schedule of the current HAE prophylactic treatment. No washout necessary.

Interventions

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Garadacimab

Participants will receive a loading dose of garadacimab, followed by once monthly garadacimab administration for 2 months. Garadacimab will be given as a subcutaneous injection. The timing for the administration of the loading dose (first administration of garadacimab) is determined by the dosing schedule of the current HAE prophylactic treatment. No washout necessary.

Intervention Type BIOLOGICAL

Other Intervention Names

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CSL312 and Factor XIIa inhibitor monoclonal antibody

Eligibility Criteria

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Inclusion Criteria

* Aged \>= 12 years at the time of providing written informed consent / assent.
* Have a history of response to on-demand HAE treatment for the treatment of acute HAE attacks.
* Documented laboratory diagnosis in medical records of C1-esterase inhibitor hereditary angioedema (HAE-C1INH) type 1 or type 2:

* Documented clinical history consistent with HAE (subcutaneous or mucosal, nonpruritic swelling episodes without accompanying urticaria),
* C1-esterase inhibitor (C1INH) antigen concentration or functional activity less than (\<) 50% of normal as documented in the participant's medical record, or
* C4-antigen concentration below the lower limit of the reference range as documented in the participant's medical record.

For HAE-nC1INH: Documented clinical history consistent with HAE (subcutaneous or mucosal, nonpruritic swelling episodes without accompanying urticaria); an HAE-associated FXII gene mutation (eg, FXII point mutation Thr328Lys or Thr328Arg, or deletion of 72 base pairs \[c.971\_1018 + 24del72\], or duplication of 18 base pairs \[c.892-909dup\]), as documented in the participant's medical record, OR an HAE-associated plasminogen gene mutation (PLG) gene mutation (eg, PLG point mutation Lys330Glu), as documented in the participant's medical record; C1INH antigen concentration or functional activity 70 to 120% of the normal level, as documented in the participant's medical record.

• Use of lanadelumab, berotralstat, or pdC1INH for the prophylactic treatment of HAE and be on a stable (consistent) dose / regimen of such medication for at least 3 months prior to Screening.

Exclusion Criteria

* Concomitant diagnosis of another form of angioedema, such as idiopathic or acquired angioedema or recurrent angioedema associated with urticaria.
* Use of androgens, antifibrinolytics, or investigational products (other than garadacimab) for routine prophylaxis against HAE attacks.
* Known or suspected hypersensitivity to monoclonal antibody therapy or hypersensitivity to the active substance (garadacimab) or to any of the excipients.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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Research Solutions of Arizona

Litchfield Park, Arizona, United States

Site Status RECRUITING

Allergy and Asthma Clinic of Northwest Arkansas

Bentonville, Arkansas, United States

Site Status RECRUITING

Donald Levy M.D.

Orange, California, United States

Site Status RECRUITING

Raffi Tachdjian MD, Inc.

Santa Monica, California, United States

Site Status RECRUITING

Bernstein Clinical Research Center, LLC

Cincinnati, Ohio, United States

Site Status RECRUITING

Clinique Spécialisée en Allergie de la Capitale

Québec, , Canada

Site Status RECRUITING

Countries

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United States Canada

Central Contacts

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Trial Registration Coordinator

Role: CONTACT

+1 610-878-4697

Facility Contacts

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Trial Information Contact

Role: primary

Trial Information Contact

Role: primary

Trial Information Contact

Role: primary

Trial Information Contact

Role: primary

Trial Information Contact

Role: primary

Trial Information Contact

Role: primary

Other Identifiers

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2024-517757-27-00

Identifier Type: OTHER

Identifier Source: secondary_id

CSL312_4002

Identifier Type: -

Identifier Source: org_study_id

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