A Study to Investigate CSL312 in Subjects With Hereditary Angioedema (HAE)

NCT ID: NCT03712228

Last Updated: 2022-11-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

44 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-29

Study Completion Date

2021-10-15

Brief Summary

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This is a multicenter, randomized, placebo-controlled, parallel-arm, phase 2 study to investigate the clinical efficacy, pharmacokinetics, and safety of CSL312 as prophylaxis to prevent attacks in subjects with HAE.

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Subjects are assigned to 1 of 2 or more groups in parallel for the duration of the study
Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double blind

Study Groups

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Placebo

Subjects with C1-INH HAE receiving buffer only

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Buffer without active ingredient

CSL312 (low)

Subjects with C1-INH HAE receiving low dose CSL312

Group Type ACTIVE_COMPARATOR

Factor XIIa antagonist monoclonal antibody

Intervention Type BIOLOGICAL

Factor XIIa antagonist monoclonal antibody for intravenous and subcutaneous use

CSL312 (med)

Subjects with C1-INH HAE receiving medium dose CSL312

Group Type ACTIVE_COMPARATOR

Factor XIIa antagonist monoclonal antibody

Intervention Type BIOLOGICAL

Factor XIIa antagonist monoclonal antibody for intravenous and subcutaneous use

CSL312 (high)

Subjects with C1-INH HAE receiving high dose CSL312

Group Type ACTIVE_COMPARATOR

Factor XIIa antagonist monoclonal antibody

Intervention Type BIOLOGICAL

Factor XIIa antagonist monoclonal antibody for intravenous and subcutaneous use

CSL312 (med/high)

Subjects with C1-INH HAE receiving medium/high dose CSL312

Group Type ACTIVE_COMPARATOR

Factor XIIa antagonist monoclonal antibody

Intervention Type BIOLOGICAL

Factor XIIa antagonist monoclonal antibody for intravenous and subcutaneous use

Interventions

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Factor XIIa antagonist monoclonal antibody

Factor XIIa antagonist monoclonal antibody for intravenous and subcutaneous use

Intervention Type BIOLOGICAL

Placebo

Buffer without active ingredient

Intervention Type DRUG

Other Intervention Names

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CSL312

Eligibility Criteria

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Inclusion Criteria

* Male or female
* Aged ≥ 18 to ≤ 65 years
* A diagnosis of C1-INH HAE or FXII/PLG HAE;
* For subjects with C1-INH HAE: ≥ 4 HAE attacks over a consecutive 2-month period during the 3 months before Screening, as documented in the subject's medical record.

Exclusion Criteria

* History of clinically significant arterial or venous thrombosis, or current clinically significant prothrombotic risk
* History of an uncontrolled, abnormal bleeding event due to a coagulopathy, or a current clinically significant coagulopathy or clinically significant risks for bleeding events
* Known incurable malignancies
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring LLC

Locations

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Donald S. Levy

Orange, California, United States

Site Status

Allergy & Asthma Clinical Research

Walnut Creek, California, United States

Site Status

Immunoe Health Centers

Centennial, Colorado, United States

Site Status

Institute for Asthma and Allergy

Chevy Chase, Maryland, United States

Site Status

The Mount Sinai Hospital

New York, New York, United States

Site Status

Pennsylvania State University

Hershey, Pennsylvania, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

Campbelltown Hospital

Campbelltown, New South Wales, Australia

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

Allergy and Clinical Immunology McMaster University

Hamilton, Ontario, Canada

Site Status

Ottawa Allergy Research Corp

Ottawa, Ontario, Canada

Site Status

Charité Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Frankfurt Goethe-Universität

Frankfurt, , Germany

Site Status

Hautklinik und Poliklinik der Universitätsklinik Mainz

Mainz, , Germany

Site Status

HZRM Hämophilie Zentrum Rhein Main GmbH

Mörfelden-Walldorf, , Germany

Site Status

Barzilai University Medical Center

Ashkelon, , Israel

Site Status

Countries

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United States Australia Canada Germany Israel

References

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Craig TJ, Levy DS, Reshef A, Lumry WR, Martinez-Saguer I, Jacobs JS, Yang WH, Ritchie B, Aygoren-Pursun E, Keith PK, Busse P, Feuersenger H, Alexandru Bica M, Jacobs I, Pragst I, Magerl M. Garadacimab for hereditary angioedema attack prevention: long-term efficacy, quality of life, and safety data from a phase 2, randomised, open-label extension study. Lancet Haematol. 2024 Jun;11(6):e436-e447. doi: 10.1016/S2352-3026(24)00081-4. Epub 2024 May 3.

Reference Type DERIVED
PMID: 38710185 (View on PubMed)

Beard N, Frese M, Smertina E, Mere P, Katelaris C, Mills K. Interventions for the long-term prevention of hereditary angioedema attacks. Cochrane Database Syst Rev. 2022 Nov 3;11(11):CD013403. doi: 10.1002/14651858.CD013403.pub2.

Reference Type DERIVED
PMID: 36326435 (View on PubMed)

Craig T, Magerl M, Levy DS, Reshef A, Lumry WR, Martinez-Saguer I, Jacobs JS, Yang WH, Ritchie B, Aygoren-Pursun E, Keith PK, Busse P, Feuersenger H, Pawaskar D, Jacobs I, Pragst I, Doyle MK. Prophylactic use of an anti-activated factor XII monoclonal antibody, garadacimab, for patients with C1-esterase inhibitor-deficient hereditary angioedema: a randomised, double-blind, placebo-controlled, phase 2 trial. Lancet. 2022 Mar 5;399(10328):945-955. doi: 10.1016/S0140-6736(21)02225-X. Epub 2022 Feb 24.

Reference Type DERIVED
PMID: 35219377 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-000605-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CSL312_2001

Identifier Type: -

Identifier Source: org_study_id

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