A Study of Lanadelumab in Persons With Hereditary Angioedema (HAE) Type I or II in North America

NCT ID: NCT03845400

Last Updated: 2023-03-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

168 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-03-30

Study Completion Date

2022-10-22

Brief Summary

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The main aim of this study is to compare the HAE attack rate before and after lanadelumab treatment was started in persons with Hereditary Angioedeme Type I or II.

Data from participants will be collected for at least 24 months. Participants will report information in a smartphone application at study start and then every 3 months until the study ends; data will also be collected by the study doctor during routine clinic visits.

Detailed Description

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Conditions

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Hereditary Angioedema (HAE)

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Type I or Type II HAE Participants

Participants with Type I or Type II HAE will be followed for 24 or 36 months depending upon enrollment date. Data collection will cease at the end of follow-up period, at the time of withdrawal, lost to follow-up, or death whichever comes first.

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Voluntarily provide written, signed, and dated (personally or via a legally-authorized representative) informed consent/and assent as applicable to participate in the study. Expression of understanding and agreement by fully informed parent(s) or legal guardian is required to permit the investigator to enroll a child in this study. The choice of the terms parental consent or parental permission in different regions may reflect local legal/regulatory and ethical considerations.
* Diagnosis of HAE Type I or Type II.
* Ability to use a mobile device for data collection in the study.

Exclusion Criteria

* Participation in any interventional clinical trial at the time of enrollment.
* Unable to provide written, signed, and dated informed consent/assent.
* Investigator believes that the participant is not a suitable candidate for the study.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda Development Center Americas, Inc.

INDUSTRY

Sponsor Role collaborator

Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Shire

Locations

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Clinical Research Center of Alabama

Birmingham, Alabama, United States

Site Status

Medical Research of Arizona

Scottsdale, Arizona, United States

Site Status

University of California San Diego

San Diego, California, United States

Site Status

AIRE Medical of Los Angeles

Santa Monica, California, United States

Site Status

Asthma and Allergy Associates, PC

Colorado Springs, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

University of South Florida Asthma, Allergy & Immunology

Tampa, Florida, United States

Site Status

University of Kansas Medical Center Research Institute, Inc.

Kansas City, Kansas, United States

Site Status

Institute for Asthma & Allergy - Chevy Chase

Chevy Chase, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Mid West Immunology Clinic

Plymouth, Minnesota, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Riverside Medical Group, Belleville

Belleville, New Jersey, United States

Site Status

Jay M Kashkin, MD Allergy, Asthma and Immunology

Fair Lawn, New Jersey, United States

Site Status

Mount Sinai

New York, New York, United States

Site Status

Clinical Research of Charlotte

Charlotte, North Carolina, United States

Site Status

Duke Asthma, Allergy & Airway Center

Durham, North Carolina, United States

Site Status

Bernstein Clinical Research Center, LLC

Cincinnati, Ohio, United States

Site Status

Portland Clinical Research/AAIM Care

Happy Valley, Oregon, United States

Site Status

Penn State Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

Seattle Allergy & Asthma Research Institute

Seattle, Washington, United States

Site Status

University of Calgary - Heritage Medical Research Clinic

Calgary, Alberta, Canada

Site Status

McMaster University Health Sciences Center

Hamilton, Ontario, Canada

Site Status

St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

CHUM Hôtel-Dieu

Montreal, Quebec, Canada

Site Status

Clinique Specialisée en Allergie de la Capitale

Québec, , Canada

Site Status

Rafael H Zaragoza-Urdaz

San Juan, , Puerto Rico

Site Status

Countries

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United States Canada Puerto Rico

References

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Zanichelli A, Wuillemin WA, Aygoren-Pursun E, Banerji A, Busse PJ, Betschel SD, Cancian M, Gagnon R, Goodyear MD, Kinaciyan T, Kessel A, Magerl M, Recke A, Wedner HJ, Estepan DN, Watt M, Andresen I, Juethner S, Khutoryansky N, Martinez-Saguer I. Lanadelumab's impact on hereditary angioedema control and quality of life across disease activity subgroups: Real-world evidence. Ann Allergy Asthma Immunol. 2025 Sep 5:S1081-1206(25)00393-X. doi: 10.1016/j.anai.2025.07.025. Online ahead of print.

Reference Type DERIVED
PMID: 40769455 (View on PubMed)

Bernstein JA, Betschel SD, Busse PJ, Banerji A, Wedner HJ, Manning M, Zaragoza-Urdaz RH, Anderson J, Gagnon R, Baptist AP, Soteres D, Lumry WR, Craig T, Petroni D, Hsu FI, Nova Estepan D, Juethner S, Watt M, Khutoryansky N, Zuraw BL; EMPOWER Investigators. Sustained Effectiveness, Tolerability, and Safety of Long-Term Prophylaxis with Lanadelumab in Hereditary Angioedema: The Prospective, Phase 4, Noninterventional EMPOWER Real-World Study. Adv Ther. 2025 Aug;42(8):3882-3901. doi: 10.1007/s12325-025-03226-3. Epub 2025 Jun 12.

Reference Type DERIVED
PMID: 40504359 (View on PubMed)

Tachdjian R, Banerji A, Busse PJ, Agmon-Levin N, Anderson J, Cancian M, Spadaro G, Enciu C, Estepan DN, Khutoryansky N, Jain S, Recke A. Effective long-term prophylaxis with lanadelumab in adolescents with hereditary angioedema: EMPOWER/ENABLE. Pediatr Allergy Immunol. 2025 Apr;36(4):e70072. doi: 10.1111/pai.70072.

Reference Type DERIVED
PMID: 40171989 (View on PubMed)

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f6b5fdc4db2bf003ab47320

To obtain more information on the study, click here/on this link

Other Identifiers

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TAK-743-403

Identifier Type: OTHER

Identifier Source: secondary_id

SHP643-403

Identifier Type: -

Identifier Source: org_study_id

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