A Study in Teenagers and Adults With Hereditary Angioedema (HAE) Type I or Type II Who Use Lanadelumab as Long-Term Prophylaxis

NCT ID: NCT04861090

Last Updated: 2023-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

207 participants

Study Classification

OBSERVATIONAL

Study Start Date

2021-09-15

Study Completion Date

2022-06-30

Brief Summary

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The main aims of this study are to learn how many people with HAE Type I or Type II are attack-free when treated with lanadelumab in real life. This includes the number of people that are attack-free when lanadelumab is given every 2 and every 4 weeks.

This study is about collecting existing data only; participants will not receive lanadelumab as part of this study. No new information will be collected during this study. Only data already available at the participant's doctor's office will be reviewed and collected for this study.

Participants do not need to visit their doctor in addition to their normal visits.

Detailed Description

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Conditions

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Hereditary Angioedema (HAE)

Study Design

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Observational Model Type

COHORT

Study Time Perspective

RETROSPECTIVE

Study Groups

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Participants With Hereditary Angioedema

Participants with HAE type I or type II who had initiated long-term prophylaxis (LTP) treatment with lanadelumab which was administered every two weeks (Q2W) or every four weeks (Q4W) or every six weeks (Q6W) or every eight weeks (Q8W) in accordance to Summary of Product Characteristics (SmPC), during a routine clinical setting will be followed up to 38 months.

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Participant is aged \>= 12 years at the time of the last documented HAE attack in the eligibility period.
* Participant has a physician-confirmed diagnosis (or confirmation in medical records) of HAE type I or type II.
* Participant had initiated LTP with lanadelumab during the eligibility period.
* Participant provides informed consent or assent prior to the initiation of any study procedures (where required by local regulations).

Exclusion Criteria

* Participant was enrolled in a therapeutic investigational drug or device trial during the observation period.
* Participant without documented HAE attacks in the pre-index period and/or without available participant diary or systematic documentation of HAE attacks in the medical records during the post index period.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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LKH-Universitätsklinikum Klinikum Graz

Graz, , Austria

Site Status

Kepler Universitätsklinikum Linz

Linz, , Austria

Site Status

Medizinische Universitat Wien (Medical University of Vienna)

Vienna, , Austria

Site Status

CHU de Grenoble

Grenoble, , France

Site Status

CHRU Lille

Lille, , France

Site Status

Groupement Hospitalier Edouard Herriot

Lyon, , France

Site Status

CHU Montpellier - Hôpital St Eloi

Montpellier, , France

Site Status

Hôtel Dieu de Paris Hospital

Paris, , France

Site Status

Hôpital Saint Antoine

Paris, , France

Site Status

Centre Hospitalier Universitaire Hopitaux de Rouen

Rouen, , France

Site Status

Charitè Campus Mitte

Berlin, , Germany

Site Status

Universitätsklinikum Frankfurt

Frankfurt am Main, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Hämophilie Zentrum Rhein Main GmbH

Mörfelden-Walldorf, , Germany

Site Status

Klinikum rechts der Isa der Technischen Universitaet Muenchen

Munich, , Germany

Site Status

Universitatsklinikum Munster

Münster, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Navy Hospital of Athens

Athens, , Greece

Site Status

Laiko General Hospital of Athens

Athens, , Greece

Site Status

University General Hospital of Larissa

Larissa, , Greece

Site Status

Countries

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Austria France Germany Greece

References

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Magerl M, Bouillet L, Martinez-Saguer I, Gavini F, Bent-Ennakhil N, Sayegh L, Andresen I. Real-World Effectiveness of Lanadelumab in Hereditary Angioedema: Multicountry INTEGRATED Observational Study. J Allergy Clin Immunol Pract. 2025 Feb;13(2):378-387.e2. doi: 10.1016/j.jaip.2024.12.008. Epub 2024 Dec 17.

Reference Type DERIVED
PMID: 39701274 (View on PubMed)

Related Links

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https://clinicaltrials.takeda.com/study-detail/608ac7aef89629001e47b4e8

To obtain more information on the study, click here/on this link

Other Identifiers

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MACS-2020-081002

Identifier Type: OTHER

Identifier Source: secondary_id

TAK-743-4006

Identifier Type: -

Identifier Source: org_study_id

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