Safety and Efficacy Study of Repeated Doses of DX-88 (Ecallantide) to Treat Attacks of Hereditary Angioedema (HAE)

NCT ID: NCT00456508

Last Updated: 2021-06-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

147 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-04-01

Study Completion Date

2010-09-01

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of repeated doses of ecallantide in the treatment of acute attacks of hereditary angioedema and to allow HAE patients continued access to ecallantide. In addition, patients enrolled in DX-88/20 (EDEMA4) trial will be followed up and treated for subsequent attacks in this trial.

Detailed Description

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This is an open label trial.

The study is designed to assess the efficacy and safety of 30 mg subcutaneous ecallantide in the treatment of acute attacks of hereditary angioedema. This study is designed to provide efficacy and safety data on repeated use of ecallantide. These data are intended to support the marketing authorization of ecallantide in the treatment of acute attacks of hereditary angioedema. Efficacy and safety of ecallantide will be evaluated in this study.

Conditions

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Hereditary Angioedema (HAE)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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DX-88 (ecallantide)

DX-88 (ecallantide) Patients were treated with DX-88 (ecallantide) when they experienced an HAE attack. 30 mg dose of ecallantide given via 3 SC injections; a second 30 mg dose can be administered if needed. Patients were to be assessed until 4 hrs post-dose. Patients were asked to return for 3 follow-up visits: 7 days, 28 days and 90 days post-dose.

Group Type EXPERIMENTAL

ecallantide

Intervention Type DRUG

solution for SC injection, one 30 mg dose per HAE attack

Interventions

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ecallantide

solution for SC injection, one 30 mg dose per HAE attack

Intervention Type DRUG

Other Intervention Names

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DX-88

Eligibility Criteria

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Inclusion Criteria

* 10 years of age or older
* Documented diagnosis of HAE (Type I or II)
* Willing and able to give informed consent
* Acute HAE attack at time of presentation

Exclusion Criteria

* Receipt of an investigational drug or device, within 30 days prior to study treatment, other than DX-88 (ecallantide)
* Pregnancy or breastfeeding
* Receipt of non-investigational C1-INH or DX-88 within 72 hours of treatment
* Patients eligible for current, ongoing clinical trial in which DX 88 (ecallantide) is offered
Minimum Eligible Age

10 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Aaron Davis

Scottsdale, Arizona, United States

Site Status

Arkansas Children's Hospital

Little Rock, Arkansas, United States

Site Status

Little Rock Allergy & Asthma Clinic

Little Rock, Arkansas, United States

Site Status

Alta Bates Summit Comprehensive Cancer Center

Berkeley, California, United States

Site Status

Pacific Coast Allergy

Crescent City, California, United States

Site Status

Jacob Offenberger

Granada Hills, California, United States

Site Status

UCLA David Geffen School of Medicine, Department of Medicine

Los Angeles, California, United States

Site Status

Asthma and Allergy Associates, P.C.

Colorado Springs, Colorado, United States

Site Status

Christiana Hospital, Christiana Care Health Services

Newark, Delaware, United States

Site Status

Georgetown University Medical Center, Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

University of Miami, General Clinical Research Center

Miami, Florida, United States

Site Status

University of South Florida, Asthma, Allergy and Immunology Clinical Research Unit

Tampa, Florida, United States

Site Status

Roberson Allergy and Asthma

West Palm Beach, Florida, United States

Site Status

Family Allergy & Asthma Center, PC

Atlanta, Georgia, United States

Site Status

Allergy Center of Brookstone

Columbus, Georgia, United States

Site Status

University Consultants in Allergy and Immunology

Chicago, Illinois, United States

Site Status

Muncie Allergy Center

Muncie, Indiana, United States

Site Status

Kansas City Allergy & Asthma

Overland Park, Kansas, United States

Site Status

Institute for Asthma and Allergy

Wheaton, Maryland, United States

Site Status

Brigham and Women's Hospital

Chestnut Hill, Massachusetts, United States

Site Status

Asthma and Allergy Institutes of Michigan

Clinton Township, Michigan, United States

Site Status

Respiratory Medicine Research Institute of Michigan, PLC

Ypsilanti, Michigan, United States

Site Status

Nevada Access to Research and Education Society

Las Vegas, Nevada, United States

Site Status

University of Nevada School of Medicine

Reno, Nevada, United States

Site Status

UMDNJ- New Jersey Medical School

Newark, New Jersey, United States

Site Status

Allergy Partners of Albuquerque

Albuquerque, New Mexico, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Allergy Partners of Western North Carolina

Asheville, North Carolina, United States

Site Status

University of Cincinnati, Division of Internal Medicine

Cincinnati, Ohio, United States

Site Status

Optimed Research, LLC

Columbus, Ohio, United States

Site Status

Penn State Milton S Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Asthma Allergy and Pulmonary Associates

Philadelphia, Pennsylvania, United States

Site Status

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Highlands Allergy and Asthma Center, PC

Bristol, Tennessee, United States

Site Status

The Paull Allergy and Asthma Clinic, P.A

Bryan, Texas, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

University of Utah Health Sciences Center

Salt Lake City, Utah, United States

Site Status

Clinical Research Associates of Tidewater

Norfolk, Virginia, United States

Site Status

Puget Sound Allergy, Asthma, & Immunology

Tacoma, Washington, United States

Site Status

Allergy and Asthma Research Centre

Ottawa, Ontario, Canada

Site Status

Jordan University Hospital

Amman, , Jordan

Site Status

Countries

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United States Canada Jordan

References

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Rubinstein E, Stolz LE, Sheffer AL, Stevens C, Bousvaros A. Abdominal attacks and treatment in hereditary angioedema with C1-inhibitor deficiency. BMC Gastroenterol. 2014 Apr 9;14:71. doi: 10.1186/1471-230X-14-71.

Reference Type DERIVED
PMID: 24712435 (View on PubMed)

MacGinnitie AJ, Davis-Lorton M, Stolz LE, Tachdjian R. Use of ecallantide in pediatric hereditary angioedema. Pediatrics. 2013 Aug;132(2):e490-7. doi: 10.1542/peds.2013-0646. Epub 2013 Jul 22.

Reference Type DERIVED
PMID: 23878046 (View on PubMed)

Sheffer AL, MacGinnitie AJ, Campion M, Stolz LE, Pullman WE. Outcomes after ecallantide treatment of laryngeal hereditary angioedema attacks. Ann Allergy Asthma Immunol. 2013 Mar;110(3):184-188.e2. doi: 10.1016/j.anai.2012.12.007. Epub 2013 Jan 5.

Reference Type DERIVED
PMID: 23548529 (View on PubMed)

Li HH, Campion M, Craig TJ, Soteres DF, Riedl M, Lumry WR, MacGinnitie AJ, Shea EP, Bernstein JA. Analysis of hereditary angioedema attacks requiring a second dose of ecallantide. Ann Allergy Asthma Immunol. 2013 Mar;110(3):168-72. doi: 10.1016/j.anai.2012.12.004. Epub 2013 Jan 8.

Reference Type DERIVED
PMID: 23548526 (View on PubMed)

Other Identifiers

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DX-88/19

Identifier Type: -

Identifier Source: org_study_id

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