A Study of Lanadelumab in Persons With Hereditary Angioedema (HAE) Type I or II

NCT ID: NCT04130191

Last Updated: 2025-09-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

140 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-12-11

Study Completion Date

2024-09-09

Brief Summary

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The main aim of this study is to compare the number of HAE attacks occuring in persons using lanadelumab with the number of HAE attacks before lanadelumab treatment was started.

Data from participants who start the study after 1 March 2021, will be collected for 24 months; data from all other participants (who started the study before 1 March 2021) will be collected for 36 months. Participants will report information in a smartphone application at study start and for the next 3 months and then every 6 months until the study ends; data will also be collected by the study doctor during routine clinic visits

Detailed Description

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Conditions

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Hereditary Angioedema (HAE)

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Participants with hereditary angioedema (HAE)

Participants who initiate treatment with lanadelumab according to current product labelling will be enrolled and followed for up to 24 or 36 months (depending on their enrollment date).

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Voluntarily provision of written, signed, and dated (personally or via a legally authorized representative) informed consent to participate in the study.
* Initiation of treatment with lanadelumab in accordance with current product labelling. Decision to start treatment with lanadelumab must be made before and be independent from enrollment in the study.
* Availability of information for HAE attack-related variables assessed at study enrollment for the previous three months.
* Ability to use a smartphone for data collection in this study.

Exclusion Criteria

* Inability to provide written, signed, and dated informed consent.
* Participation in the study not considered appropriate by the treating physician/investigator.
* Contraindication to treatment with lanadelumab according to current product labelling.
* Pregnant or breastfeeding.
* Concomitant exposure to any investigational therapy (including medications not used for HAE).
* Current or planned participation in other interventional studies.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda Development Center Americas, Inc.

INDUSTRY

Sponsor Role collaborator

Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Medical University of Vienna

Vienna, , Austria

Site Status

Klinikum der Johann-Wolfgang Goethe-Universitat

Frankfurt am Main, Hesse, Germany

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitatsklinikum Dusseldorf

Düsseldorf, , Germany

Site Status

Universitatsklinikum Schleswig-Holstein

Lübeck, , Germany

Site Status

Hämophilie Zentrum Rhein Main GmbH

Mörfelden-Walldorf, , Germany

Site Status

Klinikum rechts der Isar der Technischen Universität München

München, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Bnai Zion Medical Center

Haifa, , Israel

Site Status

Sheba Medical Center - PPDS

Ramat Gan, , Israel

Site Status

Azienda Ospedaliera Universitaria Federico II

Napoli, Campania, Italy

Site Status

ASST Fatebenefratelli Sacco - Ospedale Luigi Sacco

Milan, , Italy

Site Status

Azienda Ospedale Università Padova

Padua, , Italy

Site Status

Al-Rashed Allergy Center

Kuwait City, , Kuwait

Site Status

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Vall d'Hebron - PPDS

Barcelona, , Spain

Site Status

Universitätsspital Basel

Basel, , Switzerland

Site Status

Luzerner Kantonsspital LUKS

Lucerne, , Switzerland

Site Status

Countries

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Austria Germany Israel Italy Kuwait Spain Switzerland

References

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Zanichelli A, Wuillemin WA, Aygoren-Pursun E, Banerji A, Busse PJ, Betschel SD, Cancian M, Gagnon R, Goodyear MD, Kinaciyan T, Kessel A, Magerl M, Recke A, Wedner HJ, Estepan DN, Watt M, Andresen I, Juethner S, Khutoryansky N, Martinez-Saguer I. Lanadelumab's impact on hereditary angioedema control and quality of life across disease activity subgroups: Real-world evidence. Ann Allergy Asthma Immunol. 2025 Sep 5:S1081-1206(25)00393-X. doi: 10.1016/j.anai.2025.07.025. Online ahead of print.

Reference Type DERIVED
PMID: 40769455 (View on PubMed)

Tachdjian R, Banerji A, Busse PJ, Agmon-Levin N, Anderson J, Cancian M, Spadaro G, Enciu C, Estepan DN, Khutoryansky N, Jain S, Recke A. Effective long-term prophylaxis with lanadelumab in adolescents with hereditary angioedema: EMPOWER/ENABLE. Pediatr Allergy Immunol. 2025 Apr;36(4):e70072. doi: 10.1111/pai.70072.

Reference Type DERIVED
PMID: 40171989 (View on PubMed)

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f6b5fdc4db2bf003ab47313

To obtain more information on the study, click here/on this link.

Other Identifiers

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TAK-743-402

Identifier Type: OTHER

Identifier Source: secondary_id

SHP643-402

Identifier Type: -

Identifier Source: org_study_id

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