Study to Evaluate the Clinical Efficacy and Safety of Subcutaneously Administered C1 Esterase Inhibitor for the Prevention of Angioedema Attacks in Adolescents and Adults With Hereditary Angioedema

NCT ID: NCT02584959

Last Updated: 2021-06-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

75 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-11-01

Study Completion Date

2017-07-24

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to assess the efficacy and safety of subcutaneous administration of a liquid formulation of C1 esterase inhibitor for the prevention of angioedema attacks in adolescent and adult subjects with hereditary angioedema.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Hereditary Angioedema (HAE)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

PREVENTION

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Experimental/Placebo

Subjects will be randomized to receive C1 Esterase Inhibitor in the 1st Treatment period and then switch to Placebo in the 2nd treatment period.

Group Type EXPERIMENTAL

C1 esterase inhibitor [human] liquid

Intervention Type DRUG

C1 Esterase Inhibitor \[Human\] Liquid administered Subcutaneously as specified on specified days

Placebo

Intervention Type DRUG

Placebo

Placebo/Experimental

Subjects will be randomized to receive a placebo treatment in the 1st Treatment period and then switch to receive C1 Esterase Inhibitor in the 2nd treatment period.

Group Type EXPERIMENTAL

C1 esterase inhibitor [human] liquid

Intervention Type DRUG

C1 Esterase Inhibitor \[Human\] Liquid administered Subcutaneously as specified on specified days

Placebo

Intervention Type DRUG

Placebo

Experimental/ Experimental

Subjects will be randomized and receive C1 Esterase Inhibitor in both 1st as well as the 2nd treatment period

Group Type EXPERIMENTAL

C1 esterase inhibitor [human] liquid

Intervention Type DRUG

C1 Esterase Inhibitor \[Human\] Liquid administered Subcutaneously as specified on specified days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

C1 esterase inhibitor [human] liquid

C1 Esterase Inhibitor \[Human\] Liquid administered Subcutaneously as specified on specified days

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

The maximum duration of participation is approximately 9 months. Patients will complete a screening period of up to 21 days. Following screening, eligible patients will be randomly assigned to 1 of 3 treatment sequences. Each patient will undergo 2 14-week treatment periods for a total of 28 weeks (Treatment Period 1 and Treatment Period 2). After completing the 2 treatment periods, patients will enter a 1-month follow-up period.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Shire

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Medical Research of Arizona

Scottsdale, Arizona, United States

Site Status

AIRE Medical of Los Angeles

Santa Monica, California, United States

Site Status

Bay Area Allergy

Walnut Creek, California, United States

Site Status

IMMUNOe Research Centers

Centennial, Colorado, United States

Site Status

Asthma and Allergy Associates PC

Colorado Springs, Colorado, United States

Site Status

Atlanta Allergy and Asthma Clinic

Marietta, Georgia, United States

Site Status

Institute For Asthma and Allergy

Chevy Chase, Maryland, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Allergy Asthma and Immunology

Fair Lawn, New Jersey, United States

Site Status

Allergy Treatment Center of New Jersey

Iselin, New Jersey, United States

Site Status

Clinical Research of Charlotte

Charlotte, North Carolina, United States

Site Status

Bernstein Clinical Research Center Inc

Cincinnati, Ohio, United States

Site Status

Clinical Research Solutions

Middleburg Heights, Ohio, United States

Site Status

Allergy Clinic of Tulsa

Tulsa, Oklahoma, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

Premier Clinical Research

Spokane, Washington, United States

Site Status

McMaster University Medical Center

Hamilton, Ontario, Canada

Site Status

Ottawa Allergy Research Corporation

Ottawa, Ontario, Canada

Site Status

Hämophilie Zentrum Rhein Main GmbH

Mörfelden-Walldorf, , Germany

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

MediQuest Clinical Research Center

Târgu Mureş, , Romania

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada Germany Hungary Israel Romania Spain

References

Explore related publications, articles, or registry entries linked to this study.

Beard N, Frese M, Smertina E, Mere P, Katelaris C, Mills K. Interventions for the long-term prevention of hereditary angioedema attacks. Cochrane Database Syst Rev. 2022 Nov 3;11(11):CD013403. doi: 10.1002/14651858.CD013403.pub2.

Reference Type DERIVED
PMID: 36326435 (View on PubMed)

Lumry WR, Martinez-Saguer I, Yang WH, Bernstein JA, Jacobs J, Moldovan D, Riedl MA, Johnston DT, Li HH, Tang Y, Schranz J, Lu P, Vardi M, Farkas H; SAHARA study group. Fixed-Dose Subcutaneous C1-Inhibitor Liquid for Prophylactic Treatment of C1-INH-HAE: SAHARA Randomized Study. J Allergy Clin Immunol Pract. 2019 May-Jun;7(5):1610-1618.e4. doi: 10.1016/j.jaip.2019.01.021. Epub 2019 Jan 23.

Reference Type DERIVED
PMID: 30682573 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol: Protocol

View Document

Document Type: Study Protocol: Amendment1

View Document

Document Type: Study Protocol: Amendment2

View Document

Document Type: Study Protocol: Amendment3

View Document

Document Type: Study Protocol: Amendment4

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

SHP616-300

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.