Efficacy and Safety Study of DX-88 to Treat Acute Attacks of Hereditary Angioedema (HAE)

NCT ID: NCT00262080

Last Updated: 2021-06-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

91 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-12-31

Study Completion Date

2007-02-28

Brief Summary

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The purpose of this study is to determine if a subcutaneous dose of DX-88 (ecallantide; an investigational product) is safe and relieves symptoms of HAE in patients suffering from moderate to severe acute attacks of HAE.

Detailed Description

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Conditions

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Hereditary Angioedema (HAE)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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DX-88 (ecallantide)

DX-88 (ecallantide) 30 mg given as three 10 mg/mL subcutaneous injections.

Group Type EXPERIMENTAL

ecallantide

Intervention Type DRUG

dose of 30 mg (10 mg/ml) given as 3 subcutaneous injections.

Placebo

Phosphate Buffer Saline (PBS), pH 7.0 given as 3 subcutaneous injections.

Group Type PLACEBO_COMPARATOR

Phosphate Buffer Saline (PBS),

Intervention Type DRUG

given as three 1mL subcutaneous injections.

Interventions

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ecallantide

dose of 30 mg (10 mg/ml) given as 3 subcutaneous injections.

Intervention Type DRUG

Phosphate Buffer Saline (PBS),

given as three 1mL subcutaneous injections.

Intervention Type DRUG

Other Intervention Names

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DX-88

Eligibility Criteria

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Inclusion Criteria

* Age 10 and older
* Documented diagnosis of HAE, Type I or II
* Executed informed consent
* Presentation for treatment within 8 hours of patient recognition of moderate to severe HAE attack

Exclusion Criteria

* Receipt of investigational drug or device, other than DX-88, within 30 days of treatment
* Receipt of non-investigational C1-INH (C1 esterase inhibitor) within 7 days of treatment
* Diagnostic of acquired angioedema, estrogen-dependent angioedema or drug induced angioedema
* Pregnancy or breastfeeding
* Patients who have received DX-88 within 7 days of presentation for dosing in the Double-blind Phase
Minimum Eligible Age

10 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Institute for Asthma and Allergy

Wheaton, Maryland, United States

Site Status

Countries

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United States

References

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Rubinstein E, Stolz LE, Sheffer AL, Stevens C, Bousvaros A. Abdominal attacks and treatment in hereditary angioedema with C1-inhibitor deficiency. BMC Gastroenterol. 2014 Apr 9;14:71. doi: 10.1186/1471-230X-14-71.

Reference Type DERIVED
PMID: 24712435 (View on PubMed)

MacGinnitie AJ, Davis-Lorton M, Stolz LE, Tachdjian R. Use of ecallantide in pediatric hereditary angioedema. Pediatrics. 2013 Aug;132(2):e490-7. doi: 10.1542/peds.2013-0646. Epub 2013 Jul 22.

Reference Type DERIVED
PMID: 23878046 (View on PubMed)

Sheffer AL, MacGinnitie AJ, Campion M, Stolz LE, Pullman WE. Outcomes after ecallantide treatment of laryngeal hereditary angioedema attacks. Ann Allergy Asthma Immunol. 2013 Mar;110(3):184-188.e2. doi: 10.1016/j.anai.2012.12.007. Epub 2013 Jan 5.

Reference Type DERIVED
PMID: 23548529 (View on PubMed)

Bernstein JA, Shea EP, Koester J, Iarrobino R, Pullman WE. Assessment of rebound and relapse following ecallantide treatment for acute attacks of hereditary angioedema. Allergy. 2012 Sep;67(9):1173-80. doi: 10.1111/j.1398-9995.2012.02864.x. Epub 2012 Jul 5.

Reference Type DERIVED
PMID: 22765833 (View on PubMed)

Riedl M, Campion M, Horn PT, Pullman WE. Response time for ecallantide treatment of acute hereditary angioedema attacks. Ann Allergy Asthma Immunol. 2010 Dec;105(6):430-436.e2. doi: 10.1016/j.anai.2010.09.005. Epub 2010 Oct 25.

Reference Type DERIVED
PMID: 21130380 (View on PubMed)

Cicardi M, Levy RJ, McNeil DL, Li HH, Sheffer AL, Campion M, Horn PT, Pullman WE. Ecallantide for the treatment of acute attacks in hereditary angioedema. N Engl J Med. 2010 Aug 5;363(6):523-31. doi: 10.1056/NEJMoa0905079.

Reference Type DERIVED
PMID: 20818887 (View on PubMed)

Other Identifiers

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EDEMA3 (DX-88/14)

Identifier Type: -

Identifier Source: org_study_id

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