Long-term Safety and Efficacy of CSL312 (Garadacimab) in the Prophylactic Treatment of Hereditary Angioedema Attacks

NCT ID: NCT04739059

Last Updated: 2026-01-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

171 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-04-29

Study Completion Date

2025-11-21

Brief Summary

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This phase 3b study will evaluate long-term safety and efficacy of CSL312 (also known as garadacimab) when administered subcutaneously (SC)

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

PREVENTION

Blinding Strategy

NONE

Study Groups

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CSL312

Fully human immunoglobulin G subclass 4/lambda recombinant inhibitor monoclonal antibody administered subcutaneously

Group Type EXPERIMENTAL

CSL312

Intervention Type BIOLOGICAL

Fully human immunoglobulin G subclass 4/lambda recombinant inhibitor monoclonal antibody

Interventions

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CSL312

Fully human immunoglobulin G subclass 4/lambda recombinant inhibitor monoclonal antibody

Intervention Type BIOLOGICAL

Other Intervention Names

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Factor XIIa inhibitor monoclonal antibody garadacimab

Eligibility Criteria

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Inclusion Criteria

* \- Males and females aged ≥ 12 years
* \- Diagnosed with clinically confirmed C1-INH HAE
* \- Experienced ≥ 3 HAE attacks during the 3 months before Screening
* \- Participated in the Run-in Period for at least 1 month (CSL312-naïve subjects only)
* \- Experienced at least an average of 1 HAE attack per month during the Run-in Period

Exclusion Criteria

* \- Concomitant diagnosis of another form of angioedema, such as idiopathic or acquired angioedema or recurrent angioedema associated with urticaria
* \- Use of C1-INH products, androgens, antifibrinolytics or other small molecule medications for routine prophylaxis against HAE attacks at least 2 weeks before the first day of the Run-in Period
* \- Use of monoclonal antibodies such as lanadelumab (Takhzyro®) 3 months before the first day of the Run-in Period.
* \- Female subjects use estrogen-containing oral contraceptives or hormone replacement therapy within 4 weeks prior to screening
* \- Female or male subjects who are fertile and sexually active not using or not willing to use an acceptable method of contraception to avoid pregnancy during the study and for 30 days after receipt of the last dose of CSL312
* \- Pregnant, breastfeeding, or not willing to cease breastfeeding
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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Clinical Research Center of Alabama

Birmingham, Alabama, United States

Site Status

Research Solutions of Arizona

Litchfield Park, Arizona, United States

Site Status

Medical Research of Arizona

Scottsdale, Arizona, United States

Site Status

Little Rock Allergy & Asthma Clinic

Little Rock, Arkansas, United States

Site Status

Donald S. Levy M.D.

Orange, California, United States

Site Status

Raffi Tachdjian MD, Inc.

Santa Monica, California, United States

Site Status

Allergy & Asthma Clinical Research

Walnut Creek, California, United States

Site Status

Institute for Asthma and Allergy PC

Chevy Chase, Maryland, United States

Site Status

Bernstein Clinical Research Center, LLC

Cincinnati, Ohio, United States

Site Status

PennState Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

Campbelltown Hospital / Western Sydney University

Campbelltown, New South Wales, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Fiona Stanley Hospital, Department of Clinical Immunology

Murdoch, Western Australia, Australia

Site Status

University of Alberta - Research Transition Facility

Edmonton, Alberta, Canada

Site Status

McMaster University

Hamilton, Ontario, Canada

Site Status

Ottawa Allergy Research Corp

Ottawa, Ontario, Canada

Site Status

Gordon Sussman Clinical Research

Toronto, Ontario, Canada

Site Status

Montreal Clinical Research Institute

Montreal, Quebec, Canada

Site Status

University hospital St. Anna Ustav klinicke imunologie a alergologie, Fakultní nemocnice u sv. Anny v Brně

Brno, , Czechia

Site Status

University Hospital Motol

Prague, , Czechia

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Frankfurt

Frankfurt, , Germany

Site Status

Johannes Gutenberg-Universität KöR, Hautklinik und Poliklinik der Universitätsmedizin, Clinical Research Center

Mainz, , Germany

Site Status

HZRM Haemophilie Zentrum Rhein Main GmbH

Mörfelden-Walldorf, , Germany

Site Status

The University of Hong Kong, Queen Mary Hospital

Hong Kong, , Hong Kong

Site Status

Semmelweis Egyetem Altalanos Orvostudományi Kar Belgyógyászati és Hematológiai Klinika

Budapest, , Hungary

Site Status

Barzilai University Medical Center

Ashkelon, , Israel

Site Status

Koga Community Hospital

Shizuoka, Daikakuji Yaizu-shi, Japan

Site Status

Mie University Hospital

Mie, Edobashi, Tsu-shi, Japan

Site Status

Juntendo University Hospital

Tokyo, Hongo Bunkyo-ku, Japan

Site Status

Saitama Medical Center

Saitama, Kamoda Kawagoe-shi, Japan

Site Status

St. Marianna University School of Medicine Hospital

Kanagawa, Kawasaki-shi, Japan

Site Status

Clover Hospital

Kanagawa, Kugenumaishigami, Fujisawa-shi, Japan

Site Status

Saiyu Soka Hospital

Saitama, Matsubara Soka-shi, Japan

Site Status

National Hospital Organization Disaster Medical Center

Tokyo, Midoricho, Tachikawa-shi, Japan

Site Status

Saga University Hospital

Saga, Nebeshima, Saga-shi, Japan

Site Status

Local Incorporated Administrative Agency Osaka City Hospital Organization Osaka City General Hospital

Miyakojima-ku, Osaka-shi, Japan

Site Status

Amsterdam UMC, location AMC

Amsterdam, , Netherlands

Site Status

Auckland City Hospital

Grafton, Auckland, New Zealand

Site Status

NRC Institute of Immunology FMBA Russia

Moscow, , Russia

Site Status

Hospital Universitari General de La Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Gregorio Marañón, Servicio de Alergia

Madrid, , Spain

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

Countries

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United States Australia Canada Czechia Germany Hong Kong Hungary Israel Japan Netherlands New Zealand Russia Spain Taiwan

Other Identifiers

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2020-003918-12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CSL312_3002

Identifier Type: -

Identifier Source: org_study_id

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