Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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RECRUITING
60 participants
OBSERVATIONAL
2023-12-20
2030-03-31
Brief Summary
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Detailed Description
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Conditions
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Study Design
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COHORT
PROSPECTIVE
Study Groups
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Prospective Cohort
No intervention
No intervention
Retrospective Cohort
No intervention
No intervention
Interventions
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No intervention
No intervention
Eligibility Criteria
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Exclusion Criteria
1. Concurrent enrollment in any other clinical investigation involving use of an investigational agent for any condition at time of enrollment to this study that could confound interpretation of this study
2. Previous treatment with a gene therapy
Prospective Cohort:
3. Prior mechanical circulatory support at time of enrollment to this study
4. Prior cardiac transplantation at time of enrollment to this study
Female patients:
5. Age \>51 years at enrollment
8 Years
ALL
No
Sponsors
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Rocket Pharmaceuticals Inc.
INDUSTRY
Responsible Party
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Locations
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Phoenix Children's Hospital
Phoenix, Arizona, United States
University of California, San Diego
La Jolla, California, United States
Children's Hospital Colorado
Aurora, Colorado, United States
University of Florida College of Medicine
Gainesville, Florida, United States
University of Michigan
Ann Arbor, Michigan, United States
Washington University
St Louis, Missouri, United States
Columbia University Medical Center/New York Presbyterian
New York, New York, United States
Texas Children's Hospital
Houston, Texas, United States
German Heart Center Munich
München, , Germany
Sheba Medical Center
Ramat Gan, , Israel
Azienda Ospedaliero Universitaria
Florence, , Italy
Hospital Universitario Puerta de Hierro Majadahonda
Majadahonda, Madrid, Spain
University College London - Great Ormond Street Institute of Child Health
London, , United Kingdom
Countries
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Central Contacts
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Facility Contacts
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Other Identifiers
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RP-NI-A501-0223
Identifier Type: -
Identifier Source: org_study_id
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