A Study to Assess the Long-term Safety and Efficacy of AXS-05 in Subjects With Alzheimer's Disease Agitation

NCT ID: NCT04947553

Last Updated: 2025-12-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

456 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-17

Study Completion Date

2024-12-21

Brief Summary

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This study will evaluate the long-term safety and efficacy of AXS-05 in subjects with Alzheimer's disease (AD) agitation.

Detailed Description

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This study is a multi-center trial consisting of an open-label segment of up to 52 weeks, followed by a double-blind, placebo-controlled, randomized withdrawal segment. Subjects participating in the randomized-withdrawal segment will be randomized in a 1:1 ratio either to continue to receive AXS-05 or switch to placebo, for up to 24 weeks.

Conditions

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Agitation in Patients With Dementia of the Alzheimer's Type Alzheimer Disease Agitation, Psychomotor

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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AXS-05 (dextromethorphan-bupropion)

* Up to 52 weeks in the open-label segment;
* Up to 24 weeks in the randomized double-blind segment (if applicable)

Group Type EXPERIMENTAL

AXS-05 (dextromethorphan-bupropion)

Intervention Type DRUG

AXS-05 tablets, taken twice daily

Placebo

Up to 24 weeks in the randomized double-blind segment (if applicable)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo tablets, taken twice daily

Interventions

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AXS-05 (dextromethorphan-bupropion)

AXS-05 tablets, taken twice daily

Intervention Type DRUG

Placebo

Placebo tablets, taken twice daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participation in Study AXS-05-AD-302 or Study AXS-05-AD-304.
* Caregiver is willing to communicate with site personnel, comply with all required study procedures, and oversee administration and compliance with the subject's study treatment.

Exclusion Criteria

* Caregiver is unwilling or unable, in the opinion of the investigator, to comply with study instructions.
* Subject is hospitalized in a mental health facility (e.g., psychiatric hospital or ward), living in a nursing home, or living alone.
* Any concurrent medical condition that might interfere with the conduct of the study, confound the interpretation of study results, or endanger the subject's well-being.
* Initiation of a new medication since enrolling in AXS-05-AD-302 or AXS-05-AD-304 which may pose a safety risk when taken concurrently with AXS-05.
Minimum Eligible Age

65 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Axsome Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Research Site

Peoria, Arizona, United States

Site Status

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Tempe, Arizona, United States

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Long Beach, California, United States

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Santa Ana, California, United States

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Temecula, California, United States

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Walnut Creek, California, United States

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Bonita Springs, Florida, United States

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Brandon, Florida, United States

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Coral Springs, Florida, United States

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Greenacres City, Florida, United States

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Hialeah, Florida, United States

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Hollywood, Florida, United States

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Kissimmee, Florida, United States

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Lake City, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Gardens, Florida, United States

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Miami Lakes, Florida, United States

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Orlando, Florida, United States

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Pembroke Pines, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Trinity, Florida, United States

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Columbus, Georgia, United States

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Wichita, Kansas, United States

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Braintree, Massachusetts, United States

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Flint, Michigan, United States

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Rochester Hills, Michigan, United States

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Chesterfield, Missouri, United States

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Toms River, New Jersey, United States

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Brooklyn, New York, United States

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New Windsor, New York, United States

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Staten Island, New York, United States

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Charlotte, North Carolina, United States

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Hickory, North Carolina, United States

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Austin, Texas, United States

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Cypress, Texas, United States

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Mesquite, Texas, United States

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Sugar Land, Texas, United States

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Arlington, Virginia, United States

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Kelowna, British Columbia, Canada

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San Juan, , Puerto Rico

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Countries

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United States Canada Puerto Rico

Related Links

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http://www.axsome.com

Axsome Therapeutics Website

Other Identifiers

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AXS-05-AD-303

Identifier Type: -

Identifier Source: org_study_id

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