Study to Assess the Efficacy, Safety, and Tolerability of AVP-786 for the Treatment of Agitation in Patients With Dementia of the Alzheimer's Type

NCT ID: NCT04464564

Last Updated: 2025-05-30

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

241 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-11

Study Completion Date

2024-06-28

Brief Summary

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This study was conducted to evaluate the efficacy, safety, and tolerability of AVP-786 (deudextromethorphan hydrobromide \[d6-DM\]/quinidine sulfate \[Q\]) compared to placebo for the treatment of agitation in participants with dementia of the Alzheimer's type.

Detailed Description

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Eligible participants for this study had a diagnosis of probable Alzheimer's disease (AD) and had clinically significant, moderate/severe agitation secondary to AD.

This was multicenter, randomized, double-blind, placebo-controlled study, consisting of 12 weeks of treatment. Screening occurred within 4 weeks prior to randomization. Following screening procedures for assessment of inclusion and exclusion criteria, eligible participants were randomized into the study.

241 participants were enrolled into the study.

Study medication was administered orally twice daily from Day 1 through Day 85.

Conditions

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Agitation in Patients With Dementia of the Alzheimer's Type

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786 matching placebo capsules, twice a day, for 11 weeks in Period B.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

oral capsules

AVP-786-18

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786-18 (d6-DM 18 milligrams (mg)/Q 4.9 mg) capsules, twice a day, for 11 weeks in Period B.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

AVP-786-42.63

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786-42.63 (d6-DM 42.63 mg/Q 4.9 mg) capsules, twice a day, for 11 weeks in Period B.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

Interventions

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AVP-786

oral capsules

Intervention Type DRUG

Placebo

oral capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participants with a diagnosis of probable Alzheimer's disease according to the 2011 Neuropsychiatric Inventory Agitation/Aggression (NPI-AA) working groups criteria
* Participants with clinically significant, moderate-to-severe agitation for at least 2 weeks prior to Screening that interferes with daily routine per the Investigator's judgment
* Participants who require pharmacotherapy for the treatment of agitation per the Investigator's judgment after an evaluation of reversible factors and a course of nonpharmacological interventions
* Diagnosis of agitation must meet the International Psychogeriatric Association (IPA) provisional definition of agitation.
* Participants meeting an additional predetermined blinded eligibility criterion, which will remain blinded to the clinical study site Investigators and staff
* Participants with a reliable caregiver who is able and willing to comply with all study procedures, including adherence to administering study drug and not administering any prohibited medications during the course of the study, and who spends a minimum of 2 hours per day for 4 days per week with the participant

Exclusion Criteria

* Participants with dementia predominantly of the non-Alzheimer's type (e.g., vascular dementia, frontotemporal dementia, Parkinson's disease, substance-induced dementia)
* Participants with symptoms of agitation that are not secondary to Alzheimer's dementia (e.g., secondary to pain, other psychiatric disorder, or delirium)
* Participants with co-existent clinically significant or unstable systemic diseases that could confound the interpretation of the safety results of the study (e.g., malignancy \[except skin basal-cell carcinoma\], poorly controlled diabetes, poorly controlled hypertension, unstable pulmonary, renal or hepatic disease, unstable ischemic cardiac disease, dilated cardiomyopathy, or unstable valvular heart disease)
* Participants with myasthenia gravis
Minimum Eligible Age

50 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Otsuka Pharmaceutical Development & Commercialization, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Research Site #840-020

Phoenix, Arizona, United States

Site Status

Clinical Research Site #840-047

Anaheim, California, United States

Site Status

Clinical Research Site #840-090

Costa Mesa, California, United States

Site Status

Clinical Research Site #840-059

Lafayette, California, United States

Site Status

Clinical Research Site #840-048

Lomita, California, United States

Site Status

Clinical Research Site #840-095

Long Beach, California, United States

Site Status

Clinical Research Site #840-004

Los Angeles, California, United States

Site Status

Clinical Research Site #840-006

Panorama City, California, United States

Site Status

Clinical Research Site

San Diego, California, United States

Site Status

Clinical Research Site #840-070

Apopka, Florida, United States

Site Status

Clinical Research Site #840-055

Bradenton, Florida, United States

Site Status

Clinical Research Site #840-096

Cape Coral, Florida, United States

Site Status

Clinical Research Site #840-077

Clermont, Florida, United States

Site Status

Clinical Research Site #840-066

Coral Springs, Florida, United States

Site Status

Clinical Research Site #840-039

Hallandale, Florida, United States

Site Status

Clinical Research Site #840-089

Kissimmee, Florida, United States

Site Status

Clinical Research Site #840-034

Lady Lake, Florida, United States

Site Status

Clinical Research Site #840-037

Miami, Florida, United States

Site Status

Clinical Research Site #840-092

Miami, Florida, United States

Site Status

Clinical Research Site #840-041

Miami, Florida, United States

Site Status

Clinical Research Site #840-007

Miami, Florida, United States

Site Status

Clinical Research Site #840-103

Miami, Florida, United States

Site Status

Clinical Research Site #840-042

Miami, Florida, United States

Site Status

Clinical Research Site #840-051

Naples, Florida, United States

Site Status

Clinical Research Site #840-087

Orlando, Florida, United States

Site Status

Clinical Research Site 840-028

Pensacola, Florida, United States

Site Status

Clinical Research Site # 840-105

Tampa, Florida, United States

Site Status

Clinical Research Site #840-104

Tampa, Florida, United States

Site Status

Clinical Research Site #840-049

West Palm Beach, Florida, United States

Site Status

Clinical Research Site #840-036

Winter Park, Florida, United States

Site Status

Clinical Research Site #840-065

Atlanta, Georgia, United States

Site Status

Clinical Research Site #840-030

Chicago, Illinois, United States

Site Status

Clinical Research Site #840-073

Boston, Massachusetts, United States

Site Status

Clinical Research Site #840-014

Bloomfield Township, Michigan, United States

Site Status

Clinical Research Site #840-022

Detroit, Michigan, United States

Site Status

Clinical Research Site #840-024

O'Fallon, Missouri, United States

Site Status

Clinical Research Site #840-031

Buffalo, New York, United States

Site Status

Clinical Research Site #840-021

Manhasset, New York, United States

Site Status

Clinical Research Site #840-058

New Hyde Park, New York, United States

Site Status

Clinical Research Site #840-035

Cypress, Texas, United States

Site Status

Clinical Research Site #840-053

Dallas, Texas, United States

Site Status

Clinical Research Site #840-093

El Paso, Texas, United States

Site Status

Clinical Research Site #840-072

Houston, Texas, United States

Site Status

Clinical Research Site #840-057

Houston, Texas, United States

Site Status

Clinical Research Site #840-086

Mesquite, Texas, United States

Site Status

Clinical Research Site #840-044

Fairfax, Virginia, United States

Site Status

Clinical Research Site #056-005

Alken, Limburg, Belgium

Site Status

Clinical Research Site #056-004

Brussels, , Belgium

Site Status

Clinical Research Site #056-003

Leuven, , Belgium

Site Status

Clinical Research Site # 056-002

Liège, , Belgium

Site Status

Clinical Research Site #124-003

Kelowna, British Columbia, Canada

Site Status

Clinical Research Site #124-008

Québec, Quebec, Canada

Site Status

Clinical Research Site #152-007

Viña Del Mar, Santiago Metropolitan, Chile

Site Status

Clinical Research Site #152-002

Antofagasta, , Chile

Site Status

Clinical Research Site #152-005

Independencia, , Chile

Site Status

Clinical Research Site #152-001

Santiago, , Chile

Site Status

Clinical Research Site #152-003

Santiago, , Chile

Site Status

Clinical Research Site #152-006

Santiago, , Chile

Site Status

Clinical Research Site #170-003

Bogotá, Columbia, Colombia

Site Status

Clinical Research Site #170-002

Pereira, Columbia, Colombia

Site Status

Clinical Research Site #170-007

Floridablanca, Santander Department, Colombia

Site Status

Clinical Research Site #170-006

Bello, , Colombia

Site Status

Clinical Research Site #170-001

Bogotá, , Colombia

Site Status

Clinical Research Site #170-004

Bogotá, , Colombia

Site Status

Clinical Research Site #191-008

Pula, Istria County, Croatia

Site Status

Clinical Research Site# 191-006

Rijeka, , Croatia

Site Status

Clinical Research Site# 191-001

Zagreb, , Croatia

Site Status

Clinical Research Site #191-003

Zagreb, , Croatia

Site Status

Clinical Research Site #191-005

Zagreb, , Croatia

Site Status

Clinical Research Site #191-002

Zagreb, , Croatia

Site Status

Clinical Research Site #348-002

Gyöngyös, Heves County, Hungary

Site Status

Clinical Research Site #384-001

Budapest, , Hungary

Site Status

Clinical Research Site #384-003

Budapest, , Hungary

Site Status

Clinical Research Site #348-004

Zalaegerszeg, , Hungary

Site Status

Clinical Research Site #372-002

Cork, , Ireland

Site Status

Clinical Research Site #372-003

Cork, , Ireland

Site Status

Clinical Research Site #372-004

Dublin, , Ireland

Site Status

Clinical Research Site #372-001

Dublin, , Ireland

Site Status

Clinical Research Site # 484-004

Mexico City, , Mexico

Site Status

Clinical Research Site #484-008

Mérida, , Mexico

Site Status

Clinical Research Site #484-006

Monterrey, , Mexico

Site Status

Clinical Research Site #484-005

Monterrey, , Mexico

Site Status

Clinical Research Site # 484-003

Monterrey, , Mexico

Site Status

Clinical Research Site #484-010

Saltillo, , Mexico

Site Status

Clinical Research Site # 484-002

Sinaloa, , Mexico

Site Status

Clinical Research Site #484-009

Tlalnepantla, , Mexico

Site Status

Clinical Trial Site #528-001

Amsterdam, , Netherlands

Site Status

Clinical Research Site #703-009

Dubnica Nad Váhom, Bratislava Region, Slovakia

Site Status

Clinical Research Site #703-104

Rimavská Sobota, Sobota, Slovakia

Site Status

Clinical Research Site #703-006

Banská Bystrica, , Slovakia

Site Status

Clinical Research Site #703-002

Bardejov, , Slovakia

Site Status

Clinical Research Site #703-005

Košice, , Slovakia

Site Status

Clinical Research Site #703-003

Trenčín, , Slovakia

Site Status

Clinical Research Site #703-001

Vranov nad Topľou, , Slovakia

Site Status

Clinical Research Site #705-006

Murska Sobota, Brezovica, Slovenia

Site Status

Clinical Research Site #705-004

Begunje na Gorenjskem, , Slovenia

Site Status

Clinical Research Site #705-003

Ljubljana, , Slovenia

Site Status

Clinical Research Site #705-002

Ljubljana, , Slovenia

Site Status

Clinical Research Site #705-005

Maribor, , Slovenia

Site Status

Clinical Research Site #705-001

Nova Gorica, , Slovenia

Site Status

Clinical Research Site #724-013

Seville, Andalusia, Spain

Site Status

Clinical Research Site #724-011

Palma de Mallorca, Balearic Islands, Spain

Site Status

Clinical Research Site #724-012

Alicante, Valenciana, Comunitat, Spain

Site Status

Clinical Research Site # 724-007

Coslada, , Spain

Site Status

Clinical Research Site #724-009

Madrid, , Spain

Site Status

Clinical Research Site #724-006

Madrid, , Spain

Site Status

Countries

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United States Belgium Canada Chile Colombia Croatia Hungary Ireland Mexico Netherlands Slovakia Slovenia Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-000799-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-504991-31-00

Identifier Type: CTIS

Identifier Source: secondary_id

20-AVP-786-307

Identifier Type: -

Identifier Source: org_study_id

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