Assessment of the Efficacy, Safety, and Tolerability of AVP-786 (Deudextromethorphan Hydrobromide [d6-DM]/Quinidine Sulfate [Q]) for the Treatment of Agitation in Patients With Dementia of the Alzheimer's Type

NCT ID: NCT03393520

Last Updated: 2024-11-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

601 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-10-13

Study Completion Date

2023-12-14

Brief Summary

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This study will be conducted to evaluate the efficacy, safety, and tolerability of AVP-786 compared to placebo, for the treatment of agitation in participants with dementia of the Alzheimer's type.

Detailed Description

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Eligible participants for this study must have a diagnosis of probable Alzheimer's disease (AD) and must have clinically significant, moderate/severe agitation secondary to AD.

This is a multicenter, randomized, double-blind, placebo-controlled, parallel-design study, consisting of 12 weeks of treatment.

Approximately 550 participants will be enrolled at approximately 90 centers worldwide.

Study medication will be administered orally twice-daily from Day 1 through Day 85. Screening will occur within approximately 4 weeks prior to randomization. Following screening procedures for assessment of inclusion and exclusion criteria, eligible participants will be randomized into the study.

Conditions

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Agitation in Patients With Dementia of the Alzheimer's Type

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Participants will be assigned to treatment with placebo capsules administered twice a day over a 12-week period.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

oral capsules

AVP-786; Dose 1

Participants will receive AVP-786 (Dose 1) capsules administered twice a day over a 12-week period.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

AVP-786; Dose 2

Participants will receive AVP-786 (Dose 2) capsules administered twice a day over a 12-week period.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

Interventions

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Placebo

oral capsules

Intervention Type DRUG

AVP-786

oral capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of probable Alzheimer's Disease (AD) according to the 2011 National Institute on Aging-Alzheimer's Association (NIA-AA) working groups criteria
* Participants with clinically significant, moderate/severe agitation at the time of screening and for at least 2 weeks prior to baseline that interferes with their daily routine and for which a prescription medication has been indicated, in the opinion of the investigator
* The diagnosis of agitation must meet the provisional consensus definition of agitation in participants with cognitive disorders developed by the International Psychogeriatric Association (IPA) Agitation Definition Work Group.
* A Clinical Global Impression of Severity of Illness scale for Agitation (CGIS-Agitation) score of ≥ 4 (moderately ill) at screening and baseline
* Participants must have a reliable caregiver who is able and willing to comply with study procedures, including not administering any prohibited medications during the course of the study.
* Caregiver who is able and willing to comply with all required study procedures. In order to qualify as a reliable informant (i.e., caregiver) capable of assessing changes in participant's condition during the study, the individual must spend a minimum of 2 hours per day for 4 days per week with the participant.

Exclusion Criteria

* Participants with dementia predominantly of the non-Alzheimer's type (e.g., vascular dementia, frontotemporal dementia, Parkinson's disease, substance-induced dementia)
* Participants with symptoms of agitation that are not secondary to AD (e.g., secondary to pain, other psychiatric disorder, or delirium)
* Participants with co-existent clinically significant or unstable systemic diseases that could confound the interpretation of the safety results of the study (e.g., malignancy, poorly controlled diabetes, poorly controlled hypertension, unstable pulmonary, renal or hepatic disease, unstable ischemic cardiac disease, dilated cardiomyopathy, or unstable valvular heart disease)
* Participants with myasthenia gravis
Minimum Eligible Age

50 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Otsuka Pharmaceutical Development & Commercialization, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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MD First Research #767

Chandler, Arizona, United States

Site Status

Liv Generations of Agritopia / CCT #573

Gilbert, Arizona, United States

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Liv Generations of Ahwatukee / CCT #784

Phoenix, Arizona, United States

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Perseverance Research Center

Scottsdale, Arizona, United States

Site Status

Medical Advancement Center of Arizona #820

Tempe, Arizona, United States

Site Status

Clinical Trials Inc.

Little Rock, Arkansas, United States

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Advanced Research Center, Inc #835

Anaheim, California, United States

Site Status

ATP Clinical Research, Inc #763

Costa Mesa, California, United States

Site Status

Paradigm Clinical Research Centers, Inc.

La Mesa, California, United States

Site Status

Sunwise Clinical Research #831

Lafayette, California, United States

Site Status

Torrance Clinical Research Institute, Inc. #826

Lomita, California, United States

Site Status

Rohun Medical Corporation Site #770

Long Beach, California, United States

Site Status

Alliance for Wellness, Inc dba Alliance for Research #789

Long Beach, California, United States

Site Status

Havana Research Institute

Pasadena, California, United States

Site Status

Neurology of Central Florida Rsch Ctr # 803

Altamonte Springs, Florida, United States

Site Status

Negron Research Services / Humanity Clinical Research #766

Aventura, Florida, United States

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SFM Clinical Research, LLC #563

Boca Raton, Florida, United States

Site Status

Helix Biomedics LLC

Boynton Beach, Florida, United States

Site Status

Bradenton Research Center #834

Bradenton, Florida, United States

Site Status

Clinical Research of Brandon #838

Brandon, Florida, United States

Site Status

ASCLEPES Research Center #806

Brooksville, Florida, United States

Site Status

Beautiful Minds Clinical Research Center #808

Cutler Bay, Florida, United States

Site Status

Science Connections, LLC #814

Doral, Florida, United States

Site Status

ConSalud Medical Research #773

Hialeah, Florida, United States

Site Status

Direct Helpers Research Center # 801

Hialeah, Florida, United States

Site Status

New Med Research Inc #812

Hollywood, Florida, United States

Site Status

Alphab Global Research #793

Jupiter, Florida, United States

Site Status

Alzheimer's Research and Treatment Center

Lake Worth, Florida, United States

Site Status

Meridien Research - Lakeland Site Site #558

Lakeland, Florida, United States

Site Status

Zynak Clinical Services

Lauderdale Lakes, Florida, United States

Site Status

Adaptive Clinical Research, Inc. Site# 815

Lauderhill, Florida, United States

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Innovative Clinical Research, Inc Site #819

Lauderhill, Florida, United States

Site Status

Homestead Associates in Research #797

Miami, Florida, United States

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Premier Clinical Research Institute, Inc. #817

Miami, Florida, United States

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Central Miami Medical Institute # 798

Miami, Florida, United States

Site Status

Project4Research #774

Miami, Florida, United States

Site Status

City Medical Group RC

Miami, Florida, United States

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Finlay Medical Research Corp #552

Miami, Florida, United States

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First Class Medical Services #807

Miami, Florida, United States

Site Status

Miami Jewish Health Systems, Inc. #786

Miami, Florida, United States

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New Horizon Research Center Site #795

Miami, Florida, United States

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Reliant Medical Research, LLC #811

Miami, Florida, United States

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Clinical Research Associates of South Florida

Miami, Florida, United States

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P&S Research, LLC #805

Miami, Florida, United States

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Pharmax Research of South Florida

Miami, Florida, United States

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Research Institute of West Kendall

Miami, Florida, United States

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Crystal Biomedical Research, LLC

Miami Lakes, Florida, United States

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Agility Medical Research, Inc Site #816

Miami Lakes, Florida, United States

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Bayside Clinical Research

New Port Richey, Florida, United States

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Combined Research Orlando #799

Orlando, Florida, United States

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Innovation Medical Research Center #802

Palmetto, Florida, United States

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Quantum Laboratories Site #768

Pompano Beach, Florida, United States

Site Status

Neurostudies Inc. Site# 796

Port Charlotte, Florida, United States

Site Status

VICIS Clinical Research Inc. #777

Tampa, Florida, United States

Site Status

Academic Alliance in Dermatology

Tampa, Florida, United States

Site Status

JSV Clinical Research Study, Inc. #829

Tampa, Florida, United States

Site Status

NeuroStudies. Net, LLC

Decatur, Georgia, United States

Site Status

Hawaii Pacific Neuroscience #833

Honolulu, Hawaii, United States

Site Status

DelRicht Research #776

Covington, Louisiana, United States

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Alzheimer Disease Center #804

Braintree, Massachusetts, United States

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Neurobehavioral Medicine Group #828

Bloomfield, Michigan, United States

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Onyx Clinical Research, LLC

Caro, Michigan, United States

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Oakland Medical Research #762

Troy, Michigan, United States

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Precise Research Centers Site #765

Flowood, Mississippi, United States

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Galen Research Site #550

Chesterfield, Missouri, United States

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Psychiatric Care and Research Center #827

O'Fallon, Missouri, United States

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Bio Behavioral Health

Toms River, New Jersey, United States

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Mid Hudson Medical Research, PLLC #836

New Windsor, New York, United States

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Nathan S. Kline Institute for Psychiatric Research

Orangeburg, New York, United States

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Five Towns Neurology PC/Village Site #764

Woodmere, New York, United States

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The Neurological Institute #843

Charlotte, North Carolina, United States

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New Hope Clinical Research

Charlotte, North Carolina, United States

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Insight Clinical Trials LLC #570

Beachwood, Ohio, United States

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Valley Medical Research Site#788

Centerville, Ohio, United States

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Osumc #837

Columbus, Ohio, United States

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NorthStar Medical Research #778

Middleburg Heights, Ohio, United States

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Onyx Clinical Research, LLC

Youngstown, Ohio, United States

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Newton Clinical Research

Oklahoma City, Oklahoma, United States

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Orenda Research & Consulting LLC #840

Oklahoma City, Oklahoma, United States

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Keystone Clinical Studies, LLC

Norristown, Pennsylvania, United States

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Trinity Universal Research Associates Site #821

Carrollton, Texas, United States

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Texas Neurology #832

Dallas, Texas, United States

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InSite Clinical Research

DeSoto, Texas, United States

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Bio Pharma Informatic LLC Site #822

Houston, Texas, United States

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Bio Pharma Informatic Inc Site #769

Houston, Texas, United States

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Katy Neurology #823

Katy, Texas, United States

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Northpointe Psychiatry #761

Lewisville, Texas, United States

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Wellness Clinical Research #824

McKinney, Texas, United States

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PRX Research Site #825

Mesquite, Texas, United States

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Wasatch Clinical Research, LLC Site #771

Salt Lake City, Utah, United States

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Northwest Clinical Research Center

Bellevue, Washington, United States

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Core Clinical Research # 772

Everett, Washington, United States

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IPC Research

Waukesha, Wisconsin, United States

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Australian Alzheimer's Research Foundation

Nedlands, , Australia

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Neuro Trials Victoria Pty Ltd

Noble Park, , Australia

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The Alfred Hospital

Parkville, , Australia

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University Multiprofile Hospital for Active Treatment Dr. Georgi Stranski

Pleven, , Bulgaria

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Medical Center Hipokrat-N EOOD

Plovdiv, , Bulgaria

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Center for Mental Health - Ruse

Rousse, , Bulgaria

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Mental Health Centre Prof.Nikola Shipkovenski #713

Sofia, , Bulgaria

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DCC "Sv. Vrach and Sv. Sv. Kuzma and Damian" OOD #710

Sofia, , Bulgaria

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First Multiprofile Hospital for Active Treatment Sofia

Sofia, , Bulgaria

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Medical Center Stimul

Sofia, , Bulgaria

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Medical Center Sveti Naum #707

Sofia, , Bulgaria

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University Multiprofile Hospital for Active Treatment Alexandrovska

Sofia, , Bulgaria

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Diagnostic-consultative center Mladost-М Varna OOD #711

Varna, , Bulgaria

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Medica Plus Medical Center #705

Veliko Tarnovo, , Bulgaria

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Mental Health Center Site #712

Vratsa, , Bulgaria

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MUDr. Marta Holanová Site# 733

Brno, , Czechia

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Fakultni Nemocnice u sv. Anny v Brne #722

Brno, , Czechia

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Clinline Services s.r.0 Psychiatricka ambulance #732

Hostivice, , Czechia

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Fakultní Nemocnice Hradec Králové #724

Hradec Kralové, , Czechia

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NeuropsychiatrieHK #729

Hradec Králové, , Czechia

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Brain-Soultherapy #728

Kladno, , Czechia

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Supervize #723

Kutná Hora, , Czechia

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A-Shine s.r.o.

Pilsen, , Czechia

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Ad71 #727

Prague, , Czechia

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Clintrial #720

Prague, , Czechia

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INEP Medical s.r.o. Institut Neuropsychiatricke Pece #730

Prague, , Czechia

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Neurologicka Ambulance - Forbeli #721

Prague, , Czechia

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Neuropsychiatrie #726

Prague, , Czechia

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Vestra Clinics #725

Rychnov nad Kněžnou, , Czechia

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Centre Hospitalier Universitaire de Caen - Hôpital Côte de Nacre

Caen, , France

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Centre Hospitalier de Calais

Calais, , France

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Centre Hospitalier Universitaire Dijon Bourgogn #536

Dijon, , France

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Centre Hospitalier Universitaire de Nantes - Hôpital Nord Laennec #537

Nantes, , France

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Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

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Centre Hospitalier Universitaire de Saint-Étienne - Hôpital Nord #535

Saint-Etienne, , France

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Centre Hospitalier Universitaire Toulouse - Casselardit Ancely #533

Toulouse, , France

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Centre Hospitalier Universitaire de Nancy - Hôpital de Brabois

Vandœuvre-lès-Nancy, , France

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Dr. Kenessey Albert Kórház-Rendelőintézet

Balassagyarmat, , Hungary

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Semmelweis Egyetem Site #595

Budapest, , Hungary

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Semmelweis Egyetem

Budapest, , Hungary

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Szent Janos Korhaz es Eszak-budai Egyesitett Korhazak #586

Budapest, , Hungary

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Debreceni Egyetem Kenezy Gyula Egyetemi Korhaz

Debrecen, , Hungary

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Valeomed Egeszsegugyi es Szolgaltato Kft

Esztergom, , Hungary

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Petz Aladár Egyetemi Oktató Kórház Site# 594

Győr, , Hungary

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Dr. Mathe es Tarsa Beteti Tarsasa Site #593

Kalocsa, , Hungary

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CRU Hungary Egészségügyi és Szolgáltató Korlátolt Felelősségű Társaság

Miskolc, , Hungary

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Szabolcs-Szatmar-Bereg Megyei Korhazak es Egyetemi Oktatokorhaz

Nyíregyháza, , Hungary

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PsychoTech #580

Pécs, , Hungary

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Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont

Szeged, , Hungary

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Fejér Megyei Szent György Egyetemi Oktató Kórház

Székesfehérvár, , Hungary

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Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia

Brescia, , Italy

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Centro San Giovanni di Dio - Fatebenefratelli

Brescia, , Italy

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Università degli studi G.D'Annunzio Chieti Pescara

Chieti, , Italy

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Azienda Ospedaliero - Universitaria Careggi #610

Florence, , Italy

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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, , Italy

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Azienda Ospedaliera San Gerardo di Monza

Monza, , Italy

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Azienda Sanitaria Locale di Biella - Nuovo Ospedale degli Infermi

Ponderano, , Italy

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Azienda Ospedaliera Sant'Andrea #606

Roma, , Italy

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Fondazione Policlinico Tor Vergata #609

Roma, , Italy

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Fondazione Santa Lucia - Istituto di Ricovero e Cura a Carattere Scientifico

Roma, , Italy

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Śródmieście Przychodnia - Bydgoszcz

Bydgoszcz, , Poland

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Centrum Medyczne Sensemed

Chorzów, , Poland

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Care Clinic #750

Katowice, , Poland

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Wielospecjalistyczna Poradnia Lekarska Synapsis #741

Katowice, , Poland

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Krakowska Akademia Neurologii #740

Krakow, , Poland

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Pratia MCM Kraków #747

Krakow, , Poland

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Medycyna Milorzab #743

Lodz, , Poland

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Twoja Przychodnia - Centrum Medyczne Nowa Sol #757

Nowa Sól, , Poland

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Neurologiczny Niepubliczny Zakład Opieki Zdrowotnej

Plewiska, , Poland

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Centrum Medyczne HCP

Poznan, , Poland

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Solumed Centrum Medyczne #753

Poznan, , Poland

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RCMed Oddział Sochaczew #510

Sochaczew, , Poland

Site Status

Amonaria Indywidualna Specjalistyczna Praktyka Lekarska Agnieszka Remlinger-Molenda #508

Suchy Las, , Poland

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Centrum Medyczne Euromedis

Szczecin, , Poland

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Ośrodek Alzheimerowski #756

Ścinawa, , Poland

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Przychodnia Specjalistyczna Prosen Site#758

Warsaw, , Poland

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Centrum Medyczne NeuroProtect

Warsaw, , Poland

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Centrum Medyczne Pratia Warszawa

Warsaw, , Poland

Site Status

ClinHouse Centrum Medyczne #755

Zabrze, , Poland

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ACF Neurological Services

Cape Town, , South Africa

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Cape Trial Centre #621

Cape Town, , South Africa

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Flexivest Fourteen Research Centre #620

Cape Town, , South Africa

Site Status

Apollo Clinical Research #623

Johannesburg, , South Africa

Site Status

Medical and Dental Centre #625

Rosebank, , South Africa

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Dr. Chisto Carel Coetzee

Umhlanga, , South Africa

Site Status

Accellacare Alcobendas #659

Alcobendas, Aocobendas, Spain

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Fundació ACE

Barcelona, , Spain

Site Status

Fundació Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebrón

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia #647

Córdoba, , Spain

Site Status

Hospital General Universitario de Elche

Elche, , Spain

Site Status

Hospital Universitari de Santa Maria

Lleida, , Spain

Site Status

Hospital General Universitario Gregorio Marañón

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Puerta de Hierro - Majadahonda #658

Majadahonda, , Spain

Site Status

Clínica Universidad de Navarra

Pamplona, , Spain

Site Status

Hospital Universitario de Salamanca #656

Salamanca, , Spain

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Hospital Universitario Marqués de Valdecilla

Santander, , Spain

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Hospital Universitario Virgen Macarena #649

Seville, , Spain

Site Status

Hospital Universitario y Politécnico de La Fe

Valencia, , Spain

Site Status

Complejo Asistencial de Zamora Hospital Virgen de la Concha #652

Zamora, , Spain

Site Status

Hospital Viamed Montecanal #643

Zaragoza, , Spain

Site Status

MAC Clinical Research - Barnsley Site #671

Barnsley, , United Kingdom

Site Status

Research Institute for the Care of Older People

Bath, , United Kingdom

Site Status

Belfast Health and Social Care Trust

Belfast, , United Kingdom

Site Status

MAC Clinical Research - Blackpool

Blackpool, , United Kingdom

Site Status

MAC Clinical Research - Cannock #672

Cannock, , United Kingdom

Site Status

MAC Clinical Research - Leeds

Leeds, , United Kingdom

Site Status

Re:Cognition Health - London

London, , United Kingdom

Site Status

South London and Maudsley NHS Foundation Trust

London, , United Kingdom

Site Status

MAC Clinical Research - Manchester

Manchester, , United Kingdom

Site Status

Northamptonshire Healthcare NHS Foundation Trust #682

Northampton, , United Kingdom

Site Status

MAC Clinical Research - Liverpool

Prescot, , United Kingdom

Site Status

Southern Health NHS Foundation Trust #679

Southampton, , United Kingdom

Site Status

Avon and Wiltshire Mental Health Partnership NHS Trust

Swindon, , United Kingdom

Site Status

North West Boroughs Healthcare NHS Foundation Trust #685

Warrington, , United Kingdom

Site Status

Countries

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United States Australia Bulgaria Czechia France Hungary Italy Poland South Africa Spain United Kingdom

Other Identifiers

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2017-001339-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

17-AVP-786-305

Identifier Type: -

Identifier Source: org_study_id

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