Assessment of the Efficacy, Safety, and Tolerability of AVP-786 for the Treatment of Agitation in Patients With Dementia of the Alzheimer's Type

NCT ID: NCT04408755

Last Updated: 2025-05-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

184 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-13

Study Completion Date

2024-06-27

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study was conducted to evaluate the efficacy, safety, and tolerability of AVP-786 (deudextromethorphan hydrobromide \[d6-DM\]/quinidine sulfate \[Q\]) compared to placebo for the treatment of agitation in participants with dementia of the Alzheimer's type.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Eligible participants for this study had a diagnosis of probable Alzheimer's disease (AD) and had clinically significant, moderate/severe agitation secondary to AD.

This was a multicenter, randomized, double-blind, placebo-controlled study, consisting of 12 weeks of treatment. Screening occurred within 4 weeks prior to randomization. Following screening procedures for assessment of inclusion and exclusion criteria, eligible participants were randomized into the study.

184 participants were enrolled into the study.

Study medication was administered orally twice daily from Day 1 through Day 85.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Agitation in Patients With Dementia of the Alzheimer's Type

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Placebo

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786 matching placebo capsules, twice a day, for 11 weeks in Period B.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

oral capsules

AVP-786-18

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786-18 (d6-DM 18 milligrams (mg)/Q 4.9 mg) capsules, twice a day, for 11 weeks in Period B.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

AVP-786-42.63

Participants who were enrolled in 1-week double-blind placebo lead-in Period A, were then randomized to receive AVP-786-42.63 (d6-DM 42.63 mg/Q 4.9 mg) capsules, twice a day, for 11 weeks in Period B.

Group Type EXPERIMENTAL

AVP-786

Intervention Type DRUG

oral capsules

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

AVP-786

oral capsules

Intervention Type DRUG

Placebo

oral capsules

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participants with a diagnosis of probable Alzheimer's disease according to the 2011 Neuropsychiatric Inventory Agitation/Aggression (NPI-AA) working groups criteria
* Participants with clinically significant, moderate-to-severe agitation for at least 2 weeks prior to Screening that interferes with daily routine per the Investigator's judgment
* Participants who require pharmacotherapy for the treatment of agitation per the Investigator's judgment after an evaluation of reversible factors and a course of nonpharmacological interventions
* Diagnosis of agitation must meet the International Psychogeriatric Association (IPA) provisional definition of agitation.
* Participants meeting an additional predetermined blinded eligibility criterion, which will remain blinded to the clinical study site Investigators and staff
* Participants with a reliable caregiver who is able and willing to comply with all study procedures, including adherence to administering study drug and not administering any prohibited medications during the course of the study, and who spends a minimum of 2 hours per day for 4 days per week with the participant

Exclusion Criteria

* Participants with dementia predominantly of the non-Alzheimer's type (e.g., vascular dementia, frontotemporal dementia, Parkinson's disease, substance-induced dementia)
* Participants with symptoms of agitation that are not secondary to Alzheimer's dementia (e.g., secondary to pain, other psychiatric disorder, or delirium)
* Participants with co-existent clinically significant or unstable systemic diseases that could confound the interpretation of the safety results of the study (e.g., malignancy \[except skin basal-cell carcinoma\], poorly controlled diabetes, poorly controlled hypertension, unstable pulmonary, renal or hepatic disease, unstable ischemic cardiac disease, dilated cardiomyopathy, or unstable valvular heart disease)
* Participants with myasthenia gravis
Minimum Eligible Age

50 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Otsuka Pharmaceutical Development & Commercialization, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Clinical Research Site #840-081

Fort Smith, Arkansas, United States

Site Status

Clinical Research Site #840-035

La Jolla, California, United States

Site Status

Clinical Research Site #840-084

Los Angeles, California, United States

Site Status

Clinical Research Site #840-050

Oceanside, California, United States

Site Status

Clinical Research Site #840-064

Pasadena, California, United States

Site Status

Clinical Research Site #840-098

Santa Ana, California, United States

Site Status

Clinical Research Site #840-090

Basalt, Colorado, United States

Site Status

Clinical Research Site #840-009

Atlantis, Florida, United States

Site Status

Clinical Research Site #840-056

Brandon, Florida, United States

Site Status

Clinical Research Site #840-020

Coral Gables, Florida, United States

Site Status

Clinical Research Site #840-059

Doral, Florida, United States

Site Status

Clinical Research Site #840-131

Hialeah, Florida, United States

Site Status

Clinical Research Site #840-039

Jacksonville, Florida, United States

Site Status

Clinical Research Site #840-012

Kissimmee, Florida, United States

Site Status

Clinical Research Site #840-069

Maitland, Florida, United States

Site Status

Clinical Research Site #840-083

Maitland, Florida, United States

Site Status

Clinical Research Site #840-118

Miami, Florida, United States

Site Status

Clinical Research Site #840-004

Miami, Florida, United States

Site Status

Clinical Research Site #840-125

Miami, Florida, United States

Site Status

Clinical Research Site #840-104

Miami, Florida, United States

Site Status

Clinical Research Site #840-133

Miami, Florida, United States

Site Status

Clinical Research Site #840-042

Miami, Florida, United States

Site Status

Clinical Research Site #840-003

Miami, Florida, United States

Site Status

Clinical Research Site #840-036

Orlando, Florida, United States

Site Status

Clinical Research Site 840-111

Pembroke Pines, Florida, United States

Site Status

Clinical Research Site #840-096

Pensacola, Florida, United States

Site Status

Clinical Research Site

Pompano Beach, Florida, United States

Site Status

Clinical Research Site #840-079

Tampa, Florida, United States

Site Status

Clinical Research Site #840-112

Tampa, Florida, United States

Site Status

Clinical Research Site #840-046

Tampa, Florida, United States

Site Status

Clinical Research Site #840-107

West Palm Beach, Florida, United States

Site Status

Clinical Research Site #840-049

Glen Burnie, Maryland, United States

Site Status

Clinical Research Site #840-093

Rochester Hills, Michigan, United States

Site Status

Clinical Research Site #840-015

Hattiesburg, Mississippi, United States

Site Status

Clinical Research Site #840-029

West Long Branch, New Jersey, United States

Site Status

Clinical Research Site #840-072

New Windsor, New York, United States

Site Status

Clinical Research Site #840-097

The Bronx, New York, United States

Site Status

Clinical Research Site #840-095

Monroe, North Carolina, United States

Site Status

Clinical Research Site #840-060

Canton, Ohio, United States

Site Status

Clinical Research Site #840-028

Columbus, Ohio, United States

Site Status

Clinical Research Site #840-061

Edmond, Oklahoma, United States

Site Status

Clinical Research Site #840-099

Tulsa, Oklahoma, United States

Site Status

Clinical Research Site #840-115

McKinney, Texas, United States

Site Status

Clinical Research Site

The Woodlands, Texas, United States

Site Status

Clinical Research Site #840-025

Richmond, Virginia, United States

Site Status

Clinical Research Site #100-115

Pernik, , Bulgaria

Site Status

Clinical Research Site #100-112

Pleven, , Bulgaria

Site Status

Clinical Research Site #100-106

Plovdiv, , Bulgaria

Site Status

Clinical Research Site #100-102

Sofia, , Bulgaria

Site Status

Clinical Research Site #100-111

Sofia, , Bulgaria

Site Status

Clinical Research Site #100-105

Varna, , Bulgaria

Site Status

Clinical Research Site #100-108

Varna, , Bulgaria

Site Status

Clinical Research Site #100-113

Veliko Tarnovo, , Bulgaria

Site Status

Clinical Research Site # 208-001

Aalborg, North Denmark, Denmark

Site Status

Clinical Research Site #208-002

Aalborg, , Denmark

Site Status

Clinical Research Site #1 Site #233-002

Tallinn, , Estonia

Site Status

Clinical Research Site #2 Site #233-004

Tallinn, , Estonia

Site Status

Clinical Research Site #233-001

Tartu, , Estonia

Site Status

Clinical Research Site #276-017

Böblingen, Baden-Wurttemberg, Germany

Site Status

Clinical Research Site #276-005

Bad Homburg, Hesse, Germany

Site Status

Clinical Research Site #276-012

Gera, Thuringia, Germany

Site Status

Clinical Research Site 276-014

Berlin, , Germany

Site Status

Clinical Research Site# 300-005

Athens, , Greece

Site Status

Clinical Research Site #300-006

Ioannina, , Greece

Site Status

Clinical Research Site #300-003

Thessaloniki, , Greece

Site Status

Clinical Research Site #616-018

Zabrze, Katowice, Poland

Site Status

Clinical Research Site #616-009

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Clinical Research Site #616-006

Lublin, Lublin Voivodeship, Poland

Site Status

Clinical Research Site #616-015

Sochaczew, Masovian Voivodeship, Poland

Site Status

Clinical Research Site #616-013

Bydgoszcz, , Poland

Site Status

Clinical Research Site #616-004

Kielce, , Poland

Site Status

Clinical Research Site #616-008

Lublin, , Poland

Site Status

Clinical Research Site #616-010

Lublin, , Poland

Site Status

Clinical Research Site #616-012

Poznan, , Poland

Site Status

Clinical Research Site #616-005

Poznan, , Poland

Site Status

Clinical Research Site #616-001

Pruszcz Gdański, , Poland

Site Status

Clinical Research Site #616-007

Warsaw, , Poland

Site Status

Clinical Research Site #620-007

Guimarães, Braga District, Portugal

Site Status

Clinical Research Site #620-004

Braga, , Portugal

Site Status

Clinical Research Site #620-005

Coimbra, , Portugal

Site Status

Clinical Research Site #620-002

Torres Vedras, , Portugal

Site Status

Clinical Research Site #630-001

Bayamón, , Puerto Rico

Site Status

Clinical Research Site #630-003

Rio Piedras, , Puerto Rico

Site Status

Clinical Research Site #630-002

San Juan, , Puerto Rico

Site Status

Clinical Research Site #630-005

San Juan, , Puerto Rico

Site Status

Clinical Research Site #804-006

Dnipro, , Ukraine

Site Status

Clinical Research Site #804-003

Kharkiv, , Ukraine

Site Status

Clinical Research Site #804-004

Kiev, , Ukraine

Site Status

Clinical Research Site #804-005

Kyiv, , Ukraine

Site Status

Clinical Research Site #804-007

Lviv, , Ukraine

Site Status

Clinical Research Site #826-003

Blandford Forum, , United Kingdom

Site Status

Clinical Research Site #826-004

Crowborough, , United Kingdom

Site Status

Clinical Research Site #826-001

Fulwood, , United Kingdom

Site Status

Clinical Research Site# 826-006

Manchester, , United Kingdom

Site Status

Clinical Research Site #826-002

Motherwell, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Bulgaria Denmark Estonia Germany Greece Poland Portugal Puerto Rico Ukraine United Kingdom

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2020-000798-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-504990-19-00

Identifier Type: CTIS

Identifier Source: secondary_id

20-AVP-786-306

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.