Randomized Clinical Trial Of Bococizumab (PF-04950615; RN316) In Subjects With Hyperlipidemia Or Mixed Dyslipidemia At Risk Of Cardiovascular Events

NCT ID: NCT01968954

Last Updated: 2017-05-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

711 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-10-31

Study Completion Date

2016-04-30

Brief Summary

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This study is a multicenter, randomized study in subjects with high cholesterol receiving highly effective statins to assess the efficacy, safety and tolerability of Bococizumab (PF-04950615;RN316) to lower LDL-C.

Detailed Description

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Conditions

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Hyperlipidemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Bococizumab (PF-04950615;RN316)

Group Type EXPERIMENTAL

Bococizumab (PF-04950615;RN316)

Intervention Type DRUG

150 mg every 2 weeks, subcutaneous injection, 12 months

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

subcutaneous injection, every 2 weeks for 12 months

Interventions

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Bococizumab (PF-04950615;RN316)

150 mg every 2 weeks, subcutaneous injection, 12 months

Intervention Type DRUG

Placebo

subcutaneous injection, every 2 weeks for 12 months

Intervention Type OTHER

Other Intervention Names

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RN316

Eligibility Criteria

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Inclusion Criteria

* Treated with a statin.
* Fasting LDL-C \> 70 mg/dL and triglyceride \<=400 mg/dL.
* High or very high risk of incurring a cardiovascular event.

Exclusion Criteria

* Pregnant or breastfeeding females.
* Cardiovascular or cerebrovascular event of procedures during the past 30 days.
* Congestive heart failure NYHA class IV.
* Poorly controlled hypertension.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Achieve Clinical Research, LLC

Birmingham, Alabama, United States

Site Status

Cardiovascular Associates of the Southeast, LLC

Birmingham, Alabama, United States

Site Status

Southwest Heart Group

Tucson, Arizona, United States

Site Status

ARA-Arizona Research Associates

Tucson, Arizona, United States

Site Status

Diagnamics, Inc.

Encinitas, California, United States

Site Status

Encompass Clinical Research North Coast

Encinitas, California, United States

Site Status

MD Studies, Inc.

Fountain Valley, California, United States

Site Status

Alliance Research Centers

Laguna Hills, California, United States

Site Status

Prime Care Clinical Research

Laguna Hills, California, United States

Site Status

Providence Clinical Research

North Hollywood, California, United States

Site Status

San Diego Family Care

San Diego, California, United States

Site Status

St. Joseph's Medical Associates

Stockton, California, United States

Site Status

Orange County Research Center

Tustin, California, United States

Site Status

Clinical Research Advantage, Inc./Cassidy Medical Group - Vista

Vista, California, United States

Site Status

Elite Clinical Trials

Wildomar, California, United States

Site Status

Expresscare Clinical Research

Colorado Springs, Colorado, United States

Site Status

Soundview Medical Associates

Norwalk, Connecticut, United States

Site Status

Eastern Research, Inc.

Hialeah, Florida, United States

Site Status

East Coast Institute for Research, LLC at Northeast Florida Endocrine & Diabetes Associates

Jacksonville, Florida, United States

Site Status

Care Partners Clinical Research, LLC

Jacksonville, Florida, United States

Site Status

Prestige Clinical Research Center Inc

Miami, Florida, United States

Site Status

Edgewater Medical Research

New Smyrna Beach, Florida, United States

Site Status

Gulfcoast Medical Research Center, LLC

Tampa, Florida, United States

Site Status

Fellows Research Alliance, Inc.

Savannah, Georgia, United States

Site Status

SouthCoast Medical Group

Savannah, Georgia, United States

Site Status

Evanston Premier Healthcare Research LLC

Evanston, Illinois, United States

Site Status

Comunity Clinical Research Center

Anderson, Indiana, United States

Site Status

American Health Network of Indiana, LLC

Avon, Indiana, United States

Site Status

Midwest Institute for Clinical Research

Indianapolis, Indiana, United States

Site Status

Horizon Research Group of Opelousas, LLC

Eunice, Louisiana, United States

Site Status

Internal Medicine Associates

Eunice, Louisiana, United States

Site Status

Beacon Clinical Research, LLC

Quincy, Massachusetts, United States

Site Status

Allina Health System, dba Abbott Northwestern Hospital

Minneapolis, Minnesota, United States

Site Status

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, United States

Site Status

University of MN, Lillehei Clinical Trials Unit

Minneapolis, Minnesota, United States

Site Status

Montana Medical Research Inc.

Missoula, Montana, United States

Site Status

PMG Research of Raleigh, LLC d/b/a PMG Research of Cary

Cary, North Carolina, United States

Site Status

Clinical Trials of America, Inc.

Winston-Salem, North Carolina, United States

Site Status

Radiant Research, Inc

Akron, Ohio, United States

Site Status

Rapid Medical Research, Inc.

Cleveland, Ohio, United States

Site Status

The Office of Daniel G. Williams, MD

Perrysburg, Ohio, United States

Site Status

Great Lakes Medical Research, LLC

Willoughby, Ohio, United States

Site Status

South Oklahoma Heart Research LLC

Oklahoma City, Oklahoma, United States

Site Status

Integrated Medical Research, PC

Ashland, Oregon, United States

Site Status

Columbia Research Group, Inc.

Portland, Oregon, United States

Site Status

Harleysville Medical Associates

Harleysville, Pennsylvania, United States

Site Status

Perelman Center for Advanced Medicine Heart & Vascular Center

Philadelphia, Pennsylvania, United States

Site Status

Berks Cardiologists, Ltd.

Wyomissing, Pennsylvania, United States

Site Status

Medical Research South,LLC

Charleston, South Carolina, United States

Site Status

Berkeley Family Practice

Moncks Corner, South Carolina, United States

Site Status

Internal Medicine and Pediatric Associates of Bristol, PC

Bristol, Tennessee, United States

Site Status

3 rd Coast Research Associates

Corpus Christi, Texas, United States

Site Status

Texas Center For Drug Development, Inc.

Houston, Texas, United States

Site Status

Pioneer Research Solutions, Inc.

Houston, Texas, United States

Site Status

Protenium Clinical Research

Hurst, Texas, United States

Site Status

Utah Cardiology, P.C.

Layton, Utah, United States

Site Status

National Clinical Research - Norfolk, Inc.

Norfolk, Virginia, United States

Site Status

Premier Clinical Research

Spokane, Washington, United States

Site Status

Australian Clinical Research Network

Maroubra, New South Wales, Australia

Site Status

Core Research Group Pty Ltd

Milton, Queensland, Australia

Site Status

The Avenue Cardiovascular Centre

St Kilda East, Victoria, Australia

Site Status

Ecogene-21

Chicoutimi, Quebec, Canada

Site Status

Montreal Heart Institute

Montreal, Quebec, Canada

Site Status

Diex Research Montreal Inc.

Montreal, Quebec, Canada

Site Status

ALPHA Recherche Clinique

Québec, Quebec, Canada

Site Status

Centre Hospitalier Universitaire de Sherbrooke (CHUS)

Sherbrooke, Quebec, Canada

Site Status

Medexa Recherche

Victoriaville, Quebec, Canada

Site Status

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

Kardiologie a interni lekarstvi

Prague, , Czechia

Site Status

Lekarsky dum Ormiga

Zlín, , Czechia

Site Status

Klinische Forschung Berlin-Mitte GmbH

Berlin, , Germany

Site Status

Klinische Forschung Hannover - Mitte GmbH

Hanover, , Germany

Site Status

Klinikum der Stadt Ludwigshafen am Rhein gGmbH

Ludwigshafen, , Germany

Site Status

Klinische Forschung Schwerin GmbH

Schwerin, , Germany

Site Status

The Chinese University of Hong Kong

Shatin, , Hong Kong

Site Status

Department of Medicine & Therapeutics-The Chinese University of Hong Kong

Shatin, NT, , Hong Kong

Site Status

IRCCS Ospedale San Raffaele

Milan, MI, Italy

Site Status

IRCCS Centro Cardiologico Fondazione Monzino

Milan, MI, Italy

Site Status

IRCCS Istituto Auxologico Italiano

Milan, MI, Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico "Paolo Giaccone"

Palermo, PA, Italy

Site Status

Dipartimento di Medicina Interna e Specialita Mediche Policlinico Umberto I

Roma, RM, Italy

Site Status

SYNEXUS Polska Sp. z o.o. Oddzial w Katowicach

Katowice, Masovian Voivodeship, Poland

Site Status

NZOZ Terapia Optima

Katowice, Silesian Voivodeship, Poland

Site Status

Synexus Polska Sp. z o.o. Oddzial w Gdyni

Gdynia, , Poland

Site Status

Niepubliczny Zaklad Opieki Zdrowotnej CEREO-MED Sp. z o.o.

Lodz, , Poland

Site Status

Medicus w Opolu Sp z o.o.

Opole, , Poland

Site Status

Medicome Sp. z o.o.

Oświęcim, , Poland

Site Status

Synexus Polska Sp. z o.o Oddzial w Poznaniu

Poznan, , Poland

Site Status

Centrum Medyczne Ogrodowa Sp. z o.o.

Skierniewice, , Poland

Site Status

Centrum Medyczne "SOPMED" Sp. z o.o.

Sopot, , Poland

Site Status

Synexus Polska Sp. z o.o. Oddzial w Warszawie

Warsaw, , Poland

Site Status

Centrum Medyczne AMED

Warsaw, , Poland

Site Status

CSK MSW w Warszawie, Klinika Kardiologii Zachowawczej i Nadcisnienia Tetniczego

Warsaw, , Poland

Site Status

Synexus Polska Sp. z o.o. Oddzial we Wroclawiu

Wroclaw, , Poland

Site Status

The Catholic University of Korea, Uijeongbu St. Mary's Hospital

Uijeongbu-si, Gyeonggi-do, South Korea

Site Status

Yonsei University Wonju Severance Christian Hospital

Gangwon-Do, , South Korea

Site Status

Chonnam National University Hospital

Gwangju, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Gangnam Sevrance Hospital, Yeonsei University Health System

Seoul, , South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Ulsan University Hospital

Ulsan, , South Korea

Site Status

Countries

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United States Australia Canada Czechia Germany Hong Kong Italy Poland South Korea

References

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Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

Reference Type DERIVED
PMID: 37994400 (View on PubMed)

McCush F, Wang E, Yunis C, Schwartz P, Baltrukonis D. Anti-drug Antibody Magnitude and Clinical Relevance Using Signal to Noise (S/N): Bococizumab Case Study. AAPS J. 2023 Sep 2;25(5):85. doi: 10.1208/s12248-023-00846-x.

Reference Type DERIVED
PMID: 37658997 (View on PubMed)

Chasman DI, Hyde CL, Giulianini F, Danning RD, Wang EQ, Hickling T, Ridker PM, Loomis AK. Genome-wide pharmacogenetics of anti-drug antibody response to bococizumab highlights key residues in HLA DRB1 and DQB1. Sci Rep. 2022 Mar 11;12(1):4266. doi: 10.1038/s41598-022-07997-5.

Reference Type DERIVED
PMID: 35277540 (View on PubMed)

Wang EQ, Bukowski JF, Yunis C, Shear CL, Ridker PM, Schwartz PF, Baltrukonis D. Assessing the Potential Risk of Cross-Reactivity Between Anti-Bococizumab Antibodies and Other Anti-PCSK9 Monoclonal Antibodies. BioDrugs. 2019 Oct;33(5):571-579. doi: 10.1007/s40259-019-00375-0.

Reference Type DERIVED
PMID: 31529318 (View on PubMed)

Ridker PM, Rose LM, Kastelein JJP, Santos RD, Wei C, Revkin J, Yunis C, Tardif JC, Shear CL; Studies of PCSK9 Inhibition and the Reduction of vascular Events (SPIRE) Investigators. Cardiovascular event reduction with PCSK9 inhibition among 1578 patients with familial hypercholesterolemia: Results from the SPIRE randomized trials of bococizumab. J Clin Lipidol. 2018 Jul-Aug;12(4):958-965. doi: 10.1016/j.jacl.2018.03.088. Epub 2018 Apr 3.

Reference Type DERIVED
PMID: 29685591 (View on PubMed)

Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Reference Type DERIVED
PMID: 28304227 (View on PubMed)

Related Links

Other Identifiers

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2013-002642-37

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

SPIRE-HR

Identifier Type: OTHER

Identifier Source: secondary_id

B1481019

Identifier Type: -

Identifier Source: org_study_id

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