Monthly And Twice Monthly Subcutaneous Dosing Of PF-04950615 (RN316) In Hypercholesterolemic Subjects On A Statin

NCT ID: NCT01592240

Last Updated: 2017-12-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

354 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-07-31

Study Completion Date

2013-05-31

Brief Summary

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To evaluate the Low Density Lipoprotein-Cholesterol (LDL-C) lowering effect of PF-04950615 administered subcutaneously at monthly intervals, or twice monthly intervals in subjects with high cholesterol whose LDL-cholesterol is \>/=80 mg/dL on background treatment with a statin.

Detailed Description

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Conditions

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Hypercholesterolemia

Keywords

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PF-04950615 RN316

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Q28d Dosing Arm

A total of 7 dose groups in two dosing schedules, 50 subjects per dose group are planned. Q28d dose group will receive subcutaneous administration of PF-04950615 or Placebo once a month.

Group Type EXPERIMENTAL

PBO

Intervention Type DRUG

Placebo Q28d

200mg PF-04950615 (RN316)

Intervention Type DRUG

PF-04950615 200 mg, Q28d

300mg PF-04950615 (RN316)

Intervention Type DRUG

PF-04950615 300 mg, Q28d

Q14d Dosing Arm

A total of 7 dose groups in two dosing schedules, 50 subjects per dose group are planned. Q14d dose group will receive subcutaneous administration of PF-04950615 or Placebo every 2 weeks.

Group Type EXPERIMENTAL

PBO

Intervention Type DRUG

Placebo, Q14d

PF-04950615

Intervention Type DRUG

PF-04950615 50mg, Q14d

PF-04950615

Intervention Type DRUG

PF-04950615 100 mg, Q14d

PF-04950615

Intervention Type DRUG

PF-04950615 150mg, Q14d

Interventions

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PBO

Placebo Q28d

Intervention Type DRUG

200mg PF-04950615 (RN316)

PF-04950615 200 mg, Q28d

Intervention Type DRUG

300mg PF-04950615 (RN316)

PF-04950615 300 mg, Q28d

Intervention Type DRUG

PBO

Placebo, Q14d

Intervention Type DRUG

PF-04950615

PF-04950615 50mg, Q14d

Intervention Type DRUG

PF-04950615

PF-04950615 100 mg, Q14d

Intervention Type DRUG

PF-04950615

PF-04950615 150mg, Q14d

Intervention Type DRUG

Other Intervention Names

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PF-04950615 (RN316) PF-04950615 (RN316) PF-04950615 (RN316) PF-04950615 (RN316) PF-04950615 (RN316)

Eligibility Criteria

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Inclusion Criteria

* Subjects should be receiving a stable dose (at least 6 weeks) of any statin and continue on same dose of statin for the duration of this trial.
* Lipids should meet the following criteria on a background treatment with a statin at 2 screening visits that occur at screening and at least 7 days prior to randomization on Day 1:
* Fasting LDL-C greater than or equal to 80 mg/dL (2.31 mmol/L);
* Fasting TG less than or equal to 400 mg/dL (4.52 mmol/L).
* Subject's fasting LDL-cholesterol must greater than or equal to 80 mg/dL (2.31 mmol/L at the initial screening visit, and the value at the second visit within 7 days of randomization must be not lower than 20% of this initial value to meet eligibility criterion for this trial.

Exclusion Criteria

* Participation in other studies within 3 months before the current study begins and/or during study participation.
* Severe acute or chronic medical or psychiatric condition or laboratory abnormality that may increase the risk associated with study participation or investigational product administration or may interfere with the interpretation of study results and, in the judgment of the investigator, would make the subject inappropriate for entry into this study.
* Pregnant females; breastfeeding females; males and females of childbearing potential not using highly effective contraception or not agreeing to continue highly effective contraception for at least 63 days after last dose of investigational product.
* History of a cardiovascular or cerebrovascular event or procedure (eg, MI, stroke, TIA, angioplasty) during the past 6 months. Congestive heart failure (CHF), NYHA functional classes III or IV.
* Poorly controlled type 1 or type 2 diabetes mellitus (defined as HbA1c \>9%).
* Poorly controlled hypertension.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Protenium Clinical Research, LLC

Hurst, Texas, United States

Site Status

Paragon Research Center, LLC

San Antonio, Texas, United States

Site Status

Innovative Clinical Trials

San Antonio, Texas, United States

Site Status

National Clinical Research- Norfolk, Inc

Norfolk, Virginia, United States

Site Status

Achieve Clinical Research, LLC

Birmingham, Alabama, United States

Site Status

Medical Affiliated Research Center, Inc.

Huntsville, Alabama, United States

Site Status

The Office of James G. McMurray, MD

Huntsville, Alabama, United States

Site Status

Southwest Heart Group

Tucson, Arizona, United States

Site Status

Aureus Research Inc.

Little Rock, Arkansas, United States

Site Status

Universal Biopharma Research Institute Inc. - Alta Family Health Clinic

Dinuba, California, United States

Site Status

Clinical Trials Research

Lincoln, California, United States

Site Status

The Office of Lucita M. Cruz, MD, Inc.

Norwalk, California, United States

Site Status

Radiant Research

Santa Rosa, California, United States

Site Status

St. Joseph's Medical Associates

Stockton, California, United States

Site Status

Orange County Research Center

Tustin, California, United States

Site Status

Diablo Clinical Research, Inc.

Walnut Creek, California, United States

Site Status

Chase Medical Research, LLC

Waterbury, Connecticut, United States

Site Status

Zasa Clinical Research

Boynton Beach, Florida, United States

Site Status

Florida Health Center

Davie, Florida, United States

Site Status

Avail Clinical Research, LLC

DeLand, Florida, United States

Site Status

Florida Research Network, LLC

Gainesville, Florida, United States

Site Status

In Vivo Clinical Research, Inc.

Hialeah, Florida, United States

Site Status

Health Care Family Rehab and Research Center

Hialeah, Florida, United States

Site Status

Jacksonville Center for Clinical Research

Jacksonville, Florida, United States

Site Status

Community Research Foundation, Inc.

Miami, Florida, United States

Site Status

Kendall South Medical Center, Inc.

Miami, Florida, United States

Site Status

Omega Research Consultants, LLC

Orlando, Florida, United States

Site Status

DMI Research

Pinellas Park, Florida, United States

Site Status

St Johns Center for Clinical Research

Ponte Vedra, Florida, United States

Site Status

The Office of Bridget Bellingar, DO

Seminole, Florida, United States

Site Status

Miami Research Associates

South Miami, Florida, United States

Site Status

Atlanta Center for Medical Research

Atlanta, Georgia, United States

Site Status

Radiant Research, Inc.

Atlanta, Georgia, United States

Site Status

North Georgia Clinical Research

Woodstock, Georgia, United States

Site Status

East-West Medical Research Institute

Honolulu, Hawaii, United States

Site Status

Northwest Clinical Trials

Boise, Idaho, United States

Site Status

Fox Valley Clinical Research Center, LLC

Aurora, Illinois, United States

Site Status

Radiant Research, Inc.

Chicago, Illinois, United States

Site Status

Midwest Institute for Clinical Research

Indianapolis, Indiana, United States

Site Status

Midwest Heart & Vascular Specialists

Overland Park, Kansas, United States

Site Status

L-MARC Research Center

Louisville, Kentucky, United States

Site Status

Crescent City Clinical Research Center

Metairie, Louisiana, United States

Site Status

Maine Research Associates

Auburn, Maine, United States

Site Status

Maine Research Associates

Lewiston, Maine, United States

Site Status

ActivMed Practices and Research

Haverhill, Massachusetts, United States

Site Status

Radiant Research, Inc.

Edina, Minnesota, United States

Site Status

Dybedal Clinical Research Center

Kansas City, Missouri, United States

Site Status

Montana Medical Research, Inc.

Missoula, Montana, United States

Site Status

Meridian Clinical Research

Omaha, Nebraska, United States

Site Status

New Mexico Clinical Research and Osteoporosis Center, Inc.

Albuquerque, New Mexico, United States

Site Status

Central New York Clinical Research

Manlius, New York, United States

Site Status

Clinical Trials of America, Inc.

Hickory, North Carolina, United States

Site Status

North Carolina Clinical Research

Raleigh, North Carolina, United States

Site Status

PMG Research of Raleigh

Raleigh, North Carolina, United States

Site Status

Wake Internal Medicine Consultants

Raleigh, North Carolina, United States

Site Status

PMG Research of Salisbury

Salisbury, North Carolina, United States

Site Status

Ardmore Family Practice

Winston-Salem, North Carolina, United States

Site Status

Clinical Trials of America, Inc.

Winston-Salem, North Carolina, United States

Site Status

Sterling Research Group, Ltd.

Cincinnati, Ohio, United States

Site Status

Sentral Clinical Research Services

Cincinnati, Ohio, United States

Site Status

Sterling Research Group, LTD.

Cincinnati, Ohio, United States

Site Status

Albert J. Weisbrot, M.D., Inc.

Mason, Ohio, United States

Site Status

Lynn Institute of Norman

Norman, Oklahoma, United States

Site Status

Lynn Health Science Institute

Oklahoma City, Oklahoma, United States

Site Status

Altoona Center for Clinical Research

Duncansville, Pennsylvania, United States

Site Status

Upstate Pharmaceutical Research

Greenville, South Carolina, United States

Site Status

Coastal Carolina Research Center

Mt. Pleasant, South Carolina, United States

Site Status

Palmetto Clinical Research

Summerville, South Carolina, United States

Site Status

New Orleans Center for Clinical Research

Knoxville, Tennessee, United States

Site Status

Volunteer Research Group

Knoxville, Tennessee, United States

Site Status

Baylor College of Medicine - Center for Cardiovascular Disease Prevention

Houston, Texas, United States

Site Status

Texas Center for Drug Development, Inc.

Houston, Texas, United States

Site Status

National Clinical Research - Richmond, Inc.

Richmond, Virginia, United States

Site Status

Premier Clinical Research

Spokane, Washington, United States

Site Status

Countries

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United States

References

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Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

Reference Type DERIVED
PMID: 37994400 (View on PubMed)

Ballantyne CM, Neutel J, Cropp A, Duggan W, Wang EQ, Plowchalk D, Sweeney K, Kaila N, Vincent J, Bays H. Results of bococizumab, a monoclonal antibody against proprotein convertase subtilisin/kexin type 9, from a randomized, placebo-controlled, dose-ranging study in statin-treated subjects with hypercholesterolemia. Am J Cardiol. 2015 May 1;115(9):1212-21. doi: 10.1016/j.amjcard.2015.02.006. Epub 2015 Feb 12.

Reference Type DERIVED
PMID: 25784512 (View on PubMed)

Related Links

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Other Identifiers

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2012-001226-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B1481015

Identifier Type: -

Identifier Source: org_study_id