Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects Who Are Intolerant to Statins

NCT ID: NCT02135029

Last Updated: 2017-12-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

184 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-06-30

Study Completion Date

2015-11-30

Brief Summary

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This study is a multicenter, double blinded, active and placebo controlled randomized clinical trial to demonstrate a superior lipid lowering effect of Bococizumab (PF-04950615; RN316) compared to placebo in subjects who are statin intolerant.

Detailed Description

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Conditions

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Hyperlipidemia

Keywords

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Hyperlipidemia statin intolerance

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Bococizumab (PF-04950615;RN316)

Bococizumab (PF-04950615;RN316)

Group Type EXPERIMENTAL

Bococizumab (PF-04950615;RN316)

Intervention Type DRUG

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Atorvastatin

Group Type ACTIVE_COMPARATOR

Atorvastatin

Intervention Type DRUG

Atorvastatin PO QD

Placebo

Group Type PLACEBO_COMPARATOR

Placebo for Bococizumab (PF-04950615;RN316)

Intervention Type OTHER

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Placebo for atorvastatin

Intervention Type OTHER

PO QD

Interventions

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Bococizumab (PF-04950615;RN316)

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Intervention Type DRUG

Atorvastatin

Atorvastatin PO QD

Intervention Type DRUG

Placebo for Bococizumab (PF-04950615;RN316)

150 mg every 2 weeks by subcutaneous injection for 24 weeks

Intervention Type OTHER

Placebo for atorvastatin

PO QD

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Hyperlipidemia
* Statin Intolerant
* Fasting LDL-C \> = 70 mg/dL Fasting TG \< = 400 mg/dL

Exclusion Criteria

* Pregnant or breastfeeding females
* Cardiovascular or cerebrovascular event or procedure within 90 days
* Severe or life-threatening adverse events with past use of statins
* Poorly controlled hypertension
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Creekside Endocrine Associates, PC

Denver, Colorado, United States

Site Status

Bridgeport Hospital

Bridgeport, Connecticut, United States

Site Status

Watson Clinic Center for Research, Inc. (for Drug Shipment only)

Lakeland, Florida, United States

Site Status

Cardiovascular Research Center Of South Florida

Miami, Florida, United States

Site Status

St. Johns Center for Clinical Research

Ponte Vedra, Florida, United States

Site Status

Progressive Medical Research

Port Orange, Florida, United States

Site Status

East-West Medical Research Institute

Honolulu, Hawaii, United States

Site Status

NorthShore University HealthSystem - Evanston Hospital

Evanston, Illinois, United States

Site Status

Health Care Centers of Illinois Mokena Medical Commons

Mokena, Illinois, United States

Site Status

Advocate Medical Group Cardiology

Normal, Illinois, United States

Site Status

Advocate Medical Group Midwest Heart Specialists

Park Ridge, Illinois, United States

Site Status

Prairie Education & Research Cooperative (Administrative)

Springfield, Illinois, United States

Site Status

Prairie Heart Institute

Springfield, Illinois, United States

Site Status

St. John's Hospital

Springfield, Illinois, United States

Site Status

The University of Iowa - College of Public Health - Preventive Intervention Center

Iowa City, Iowa, United States

Site Status

The Iowa Clinic, PC

West Des Moines, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Crescent City Clinical Research Center

Metairie, Louisiana, United States

Site Status

Allina Health System, dba Abbott Northwestern Hospital

Minneapolis, Minnesota, United States

Site Status

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, United States

Site Status

PMG Research of Wilmington, LLC

Wilmington, North Carolina, United States

Site Status

Dayton Heart Center

Dayton, Ohio, United States

Site Status

Clinical and Translational Research Center, Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

Site Status

Berks Cardiologists, Ltd.

Wyomissing, Pennsylvania, United States

Site Status

PMG Research of Bristol

Bristol, Tennessee, United States

Site Status

PMG Research of Knoxville, LLC

Knoxville, Tennessee, United States

Site Status

San Antonio Military Medical Center

Fort Sam Houston, Texas, United States

Site Status

Office of Michelle Zaniewski MD., PA.

Houston, Texas, United States

Site Status

Utah Cardiology, P.C.

Layton, Utah, United States

Site Status

Aspen Clinical Research LLC

Orem, Utah, United States

Site Status

The Medical Arts Health Research Group

Kelowna, British Columbia, Canada

Site Status

Corunna Medical Research Centre

Corunna, Ontario, Canada

Site Status

The Office of Dr. James Cha

Oshawa, Ontario, Canada

Site Status

Kawartha Cardiology Clinical Trials

Peterborough, Ontario, Canada

Site Status

Devonshire Clinical Research Inc.

Woodstock, Ontario, Canada

Site Status

Ecogene-21

Chicoutimi, Quebec, Canada

Site Status

Omnispec clinical research inc.

Mirabel, Quebec, Canada

Site Status

Clinique des maladies lipidiques de Quebec

Québec, Quebec, Canada

Site Status

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, Canada

Site Status

Countries

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United States Canada

References

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Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

Reference Type DERIVED
PMID: 37994400 (View on PubMed)

Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Reference Type DERIVED
PMID: 28304227 (View on PubMed)

Related Links

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Other Identifiers

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STATIN INTOLERANT

Identifier Type: -

Identifier Source: secondary_id

SPIRE-SI

Identifier Type: OTHER

Identifier Source: secondary_id

B1481030

Identifier Type: -

Identifier Source: org_study_id