Trial Evaluating PCSK9 Antibody in Subjects With LDL Receptor Abnormalities

NCT ID: NCT01588496

Last Updated: 2018-11-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

58 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-04-05

Study Completion Date

2014-01-31

Brief Summary

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A study to determine the safety, tolerability, and efficacy of evolocumab (AMG 145) in patients with homozygous familial hypercholesterolemia (HoFH).

Detailed Description

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Study Masking:

Part A: Open Label Part B: Double Blind

Conditions

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Homozygous Familial Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Part A: Evolocumab

Participants received open-label evolocumab 420 mg subcutaneously once a month for 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Part B: Evolocumab

Participants received double-blind evolocumab 420 mg subcutaneously once a month for 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Part B: Placebo

Participants received double-blind placebo subcutaneously once a month for 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered by subcutaneous injection

Interventions

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Evolocumab

Administered by subcutaneous injection

Intervention Type BIOLOGICAL

Placebo

Administered by subcutaneous injection

Intervention Type DRUG

Other Intervention Names

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AMG 145 Repatha

Eligibility Criteria

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Inclusion Criteria

* Males and females ≥ 12 to ≤ 80 years of age
* Diagnosis of homozygous familial hypercholesterolemia
* Stable lipid-lowering therapies for at least 4 weeks
* LDL cholesterol ≥ 130 mg/dl (3.4 mmol/L)
* Triglyceride ≤ 400 mg/dL (4.5 mmol/L)
* Bodyweight of ≥ 40 kg at screening.

Exclusion Criteria

* LDL or plasma apheresis within 8 weeks prior to randomization
* New York Heart Association (NYHA) class III or IV or last known left ventricular ejection fraction \< 30%
* Myocardial infarction, unstable angina, percutaneous coronary intervention (PCI), coronary artery bypass graft (CABG) or stroke within 3 months of randomization
* Planned cardiac surgery or revascularization
* Uncontrolled cardiac arrhythmia
* Uncontrolled hypertension
Minimum Eligible Age

12 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Research Site

New York, New York, United States

Site Status

Research Site

Cincinnati, Ohio, United States

Site Status

Research Site

Brussels, , Belgium

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La Louvière, , Belgium

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London, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Brno, , Czechia

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Hradec Králové, , Czechia

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Uherské Hradiště, , Czechia

Site Status

Research Site

Dijon, , France

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Paris, , France

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New Territories, , Hong Kong

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Pisa, , Italy

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Beirut, , Lebanon

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Amsterdam, , Netherlands

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Christchurch, , New Zealand

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Johannesburg, Gauteng, South Africa

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Research Site

Observatory, Western Cape, South Africa

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Research Site

Córdoba, Andalusia, Spain

Site Status

Research Site

Lugo, Galicia, Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Countries

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United States Belgium Canada Czechia France Hong Kong Italy Lebanon Netherlands New Zealand South Africa Spain

References

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Kasichayanula S, Grover A, Emery MG, Gibbs MA, Somaratne R, Wasserman SM, Gibbs JP. Clinical Pharmacokinetics and Pharmacodynamics of Evolocumab, a PCSK9 Inhibitor. Clin Pharmacokinet. 2018 Jul;57(7):769-779. doi: 10.1007/s40262-017-0620-7.

Reference Type BACKGROUND
PMID: 29353350 (View on PubMed)

Raal FJ, Honarpour N, Blom DJ, Hovingh GK, Xu F, Scott R, Wasserman SM, Stein EA; TESLA Investigators. Inhibition of PCSK9 with evolocumab in homozygous familial hypercholesterolaemia (TESLA Part B): a randomised, double-blind, placebo-controlled trial. Lancet. 2015 Jan 24;385(9965):341-50. doi: 10.1016/S0140-6736(14)61374-X. Epub 2014 Oct 1.

Reference Type DERIVED
PMID: 25282520 (View on PubMed)

Stein EA, Honarpour N, Wasserman SM, Xu F, Scott R, Raal FJ. Effect of the proprotein convertase subtilisin/kexin 9 monoclonal antibody, AMG 145, in homozygous familial hypercholesterolemia. Circulation. 2013 Nov 5;128(19):2113-20. doi: 10.1161/CIRCULATIONAHA.113.004678. Epub 2013 Sep 6.

Reference Type DERIVED
PMID: 24014831 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2011-005399-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20110233

Identifier Type: -

Identifier Source: org_study_id

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