Phase 3 Study to Evaluate the Efficacy and Safety of LIB003 With Evolocumab in HoFH

NCT ID: NCT04034485

Last Updated: 2023-03-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

65 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-07

Study Completion Date

2023-01-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

To compare the safety, tolerability and LDL-C response after 24 Weeks of monthly (every 4 weeks \[Q4W\]) subcutaneous (SC) dosing of LIB003 300 mg with monthly (Q4W) SC dosing of 420 mg evolocumab (Repatha®) in patients with HoFH on stable diet and oral LDL-C-lowering drug therapy

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Patients with verified HoFH on stable and continuing doses of oral lipid lowering therapy will be randomized to either evolocumab 420 mg Q4W or LIB003 300 mg Q4W for 24 weeks (Period A). At Week 24, subjects will be crossed over to LIB003 if they were on evolocumab and vice versa for the next 24 weeks (Period B).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Homozygous Familial Hypercholesterolemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

open label, randomized, cross-over
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

treatment is open label but lipid results are masked to participant, investigator and sponsor

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

LIB003 (lerodalcibep)

300 mg SC Q4W

Group Type EXPERIMENTAL

lerodalcibep

Intervention Type DRUG

PCSK9 inhibitor

evolocumab

420 mg SC Q4W

Group Type ACTIVE_COMPARATOR

evolocumab

Intervention Type DRUG

PCSK9 inhibitor

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

lerodalcibep

PCSK9 inhibitor

Intervention Type DRUG

evolocumab

PCSK9 inhibitor

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

LIB003 Repatha

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* HoFH diagnosed clinically and confirmed by genotyping
* Weight of \>30 kg and body mass index (BMI) \>17 and \<40 kg/m2
* stable diet and lipid-lowering oral therapies for at least 4 weeks

Exclusion Criteria

* mipomersen within 6 months of screening;
* LDL or plasma apheresis \<2 months prior to randomization
* history of non-response to PCSK9 mAb or presence of receptor negative/null LDLR activity expected to result in non-response to PCSK9 inhibition
* prior or active clinical condition or acute and/or unstable systemic disease compromising subject inclusion
Minimum Eligible Age

10 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

LIB Therapeutics LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Evan A Stein, MD PhD

Role: STUDY_DIRECTOR

LIB Therapeutics

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

NorthShore University Health System

Evanston, Illinois, United States

Site Status

Metabolic & Atherosclerosis Research Center (MARC)

Cincinnati, Ohio, United States

Site Status

VMMC & Safdarjung Hospital

Delhi, National Capital Territory of Delhi, India

Site Status

CIMS Hospital Pvt. Ltd

Ahmedabad, , India

Site Status

G.B. Pant Institute of Postgraduate Medical Education & Research

New Delhi, , India

Site Status

Department of Medicine, Hadassah University Hospital

Jerusalem, , Israel

Site Status

Rabin Medical Center, Beilinson Hospital,

Petah Tikva, , Israel

Site Status

Lipid Clinic, Oslo University Hospital

Oslo, , Norway

Site Status

Carbohydrate and Lipid Metabolism Research Unit

Johannesburg, Gauteng, South Africa

Site Status

Division of Lipidology, Department of Medicine University of Cape Town

Cape Town, Western Province, South Africa

Site Status

Ege University Medical School

Izmir, Bornova, Turkey (Türkiye)

Site Status

Afyonkarahisar Health Sciences University

Afyonkarahisar, , Turkey (Türkiye)

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States India Israel Norway South Africa Turkey (Türkiye)

References

Explore related publications, articles, or registry entries linked to this study.

Raal FJ, Mehta V, Kayikcioglu M, Blom D, Gupta P, Elis A, Turner T, Daniels C, Vest J, Mitchell T, Caldwell K, Bahassi EM, Kallend D, Stein EA. Lerodalcibep and evolocumab for the treatment of homozygous familial hypercholesterolaemia with PCSK9 inhibition (LIBerate-HoFH): a phase 3, randomised, open-label, crossover, non-inferiority trial. Lancet Diabetes Endocrinol. 2025 Mar;13(3):178-187. doi: 10.1016/S2213-8587(24)00313-9. Epub 2025 Jan 24.

Reference Type DERIVED
PMID: 39870096 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

LIB003-003

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.