Evaluate the Effect of Obicetrapib in Patients With HeFH on Top of Maximum Tolerated Lipid-Modifying Therapies.

NCT ID: NCT05425745

Last Updated: 2025-06-11

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

354 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-25

Study Completion Date

2024-05-28

Brief Summary

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This study will be a placebo-controlled, double-blind, randomized, phase 3 study to Evaluate the Efficacy, Safety, and Tolerability of Obicetrapib in Participants with a History of Heterozygous Familial Hypercholesterolemia (HeFH).

Detailed Description

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This study will be a placebo-controlled, double-blind, randomized, phase 3 study in participants with HeFH to evaluate the efficacy, safety, and tolerability of obicetrapib as an adjunct to diet and maximally tolerated lipid-lowering therapy. The screening period for this study will take up to 14 days. Afterwards, patients will be randomized to placebo or 10 mg obicetrapib for an 365-day treatment period. After the treatment period, participants will have an end-of-study follow-up visit.

Conditions

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Dyslipidemias High Cholesterol Hypercholesterolemia Familial Hypercholesterolemia Lipid Metabolism Disorder Metabolic Disease Lipid Metabolism, Inborn Errors Genetic Disease, Inborn Hyperlipoproteinemias

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Placebo-Controlled, double-blind, randomized
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
placebo tablet made to resemble active

Study Groups

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Placebo

one placebo tablet once daily

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

placebo tablet made to resemble active

Obicetrapib 10 mg

one 10 mg Obicetrapib tablet once daily

Group Type EXPERIMENTAL

Obicetrapib

Intervention Type DRUG

10 mg Obicetrapib tablet

Interventions

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Obicetrapib

10 mg Obicetrapib tablet

Intervention Type DRUG

Placebo

placebo tablet made to resemble active

Intervention Type DRUG

Other Intervention Names

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CETP-inhibitor

Eligibility Criteria

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Inclusion Criteria

* Have a history of heterozygous familial hypercholesterolemia (HeFH) by 1) Genotyping (not a screening assessment), WHO Criteria/Dutch Lipid Clinical Network Criteria with a score of \> 8 points; and/or Simon Broome Register Diagnostic Criteria for definite or possible Familial Hypercholesterolemia (FH)
* Maximally tolerated lipid Modifying therapy for at least 8 weeks prior to screening such as: ATV (40 or 80), or (ROS 20 or 40 mg), Ezetimide, Bempedoic Acid, PCSK9 targeted therapy for at least 4 doses
* Fasting serum LDL-C ≥70 mg/dL (≥1.80 mmol/L)

Exclusion Criteria

* New York Heart Association class II or IV heart failure or last known left ventricular ejection fraction \< 30%;
* Hospitalized for heart failure within 5 years prior to Screening
* Major adverse cardiac event (MACE) within 3 months prior to Screening;
* HbA1c ≥10%, or fasting glucose
* Formal diagnosis of homozygous familial hypercholesterolemia (HoFH)
* Uncontrolled severe hypertension, defined as either systolic blood pressure ≥ 160 mmHg or diastolic blood pressure ≥100 mmHg prior to Randomization
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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NewAmsterdam Pharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marc Ditmarsch

Role: STUDY_DIRECTOR

NewAmsterdam Pharma

Locations

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Site 01022

Jonesboro, Arkansas, United States

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Site 01015

Toluca Lake, California, United States

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Site 01009

Sarasota, Florida, United States

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Site 01023

Boise, Idaho, United States

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Site 01018

Chicago, Illinois, United States

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Site 01012

Iowa City, Iowa, United States

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Site 01007

Baton Rouge, Louisiana, United States

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Site 01005

Port Gibson, Mississippi, United States

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Site 01006

St Louis, Missouri, United States

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Site 01011

Lincoln, Nebraska, United States

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Site 01004

Norfolk, Nebraska, United States

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Site 01002

Morristown, New Jersey, United States

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Site 01010

New Providence, New Jersey, United States

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Site 01001

North Massapequa, New York, United States

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Site 01020

Morganton, North Carolina, United States

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Site 01019

Winston-Salem, North Carolina, United States

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Site 01008

Chattanooga, Tennessee, United States

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Site 01016

El Paso, Texas, United States

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Site 01013

Houston, Texas, United States

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Site 01014

Suffolk, Virginia, United States

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Site 06007

Brampton, , Canada

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Site 06008

Chicoutimi, , Canada

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Site 06005

Halifax, , Canada

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Site 06003

Montreal, , Canada

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Site 06009

Montreal, , Canada

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Site 06004

Québec, , Canada

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Site 06006

Sherbrooke, , Canada

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Site 06001

Vancouver, , Canada

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Site 06002

Victoria, , Canada

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Site 02006

Brno, , Czechia

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Site 02002

Hradec Králové, , Czechia

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Site 02003

Prague, , Czechia

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Site 02005

Prague, , Czechia

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Site 02004

Prague, , Czechia

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Site 02001

Uherské Hradiště, , Czechia

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Site 022001

Batumi, , Georgia

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Site 022003

Tbilisi, , Georgia

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Site 022004

Tbilisi, , Georgia

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Site 022010

Tbilisi, , Georgia

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Site 022006

Tbilisi, , Georgia

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Site 022007

Tbilisi, , Georgia

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Site 022008

Tbilisi, , Georgia

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Site 022002

Tbilisi, , Georgia

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Site 022005

Tbilisi, , Georgia

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Site 022009

Tbilisi, , Georgia

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Site 04001

Amsterdam, , Netherlands

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Arnhem, , Netherlands

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Site 04002

Deventer, , Netherlands

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Site 04004

Eindhoven, , Netherlands

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Roosendaal, , Netherlands

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Site 04006

Rotterdam, , Netherlands

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Site 023003

Bodø, , Norway

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Site 023002

Oslo, , Norway

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Site 05002

Bialystok, , Poland

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Site 05003

Lodz, , Poland

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Site 05004

Lodz, , Poland

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Site 05005

Zabrze, , Poland

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Site 05001

Zamość, , Poland

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Site 018001

Bloemfontein, , South Africa

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Site 018002

Cape Town, , South Africa

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Site 018009

Centurion, , South Africa

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Site 018006

Centurion, , South Africa

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Site 018004

Parow, , South Africa

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Site 018003

Somerset West, , South Africa

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Site 018005

Somerset West, , South Africa

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Site 018007

Tongaat, , South Africa

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Site 018008

Umhlanga, , South Africa

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Site 17004

A Coruña, , Spain

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Site 017001

Barcelona, , Spain

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Site 17002

Barcelona, , Spain

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Site 17003

Córdoba, , Spain

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Site 17018

Figueras, , Spain

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Site 17011

Granada, , Spain

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Site 17017

Huelva, , Spain

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Site 17012

Huesca, , Spain

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Site 17008

Las Palmas de Gran Canaria, , Spain

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Site 17010

Madrid, , Spain

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Site 17016

Madrid, , Spain

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Site 17007

Málaga, , Spain

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Site 17013

Sabadell, , Spain

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Site 17015

Santiago de Compostela, , Spain

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Site 17009

Seville, , Spain

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Site 17006

Seville, , Spain

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Site 17014

Valencia, , Spain

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Site 17005

Zaragoza, , Spain

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Site 014006

Birmingham, , United Kingdom

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Site 014012

Bristol, , United Kingdom

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Site 014009

Cardiff, , United Kingdom

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Site 014010

Chichester, , United Kingdom

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Site 014001

Dundee, , United Kingdom

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Site 014002

London, , United Kingdom

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Site 014003

Manchester, , United Kingdom

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Site 014008

Metropolitan Borough of Wirral, , United Kingdom

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Site 014011

Penzance, , United Kingdom

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Site 014005

Stevenage, , United Kingdom

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Site 014004

West Bromwich, , United Kingdom

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Countries

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United States Canada Czechia Georgia Netherlands Norway Poland South Africa Spain United Kingdom

References

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Nicholls SJ, Nelson AJ, Ditmarsch M, Kastelein JJP, Ballantyne CM, Ray KK, Navar AM, Nissen SE, Goldberg AC, Brunham LR, Curcio D, Wuerdeman E, Neild A, Kling D, Hsieh A, Dicklin MR, Ference BA, Laufs U, Banach M, Mehran R, Catapano AL, Davidson MH. Obicetrapib on top of maximally tolerated lipid-modifying therapies in participants with or at high risk for atherosclerotic cardiovascular disease: rationale and designs of BROADWAY and BROOKLYN. Am Heart J. 2024 Aug;274:32-45. doi: 10.1016/j.ahj.2024.05.002. Epub 2024 May 4.

Reference Type DERIVED
PMID: 38705341 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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TA-8995-301

Identifier Type: -

Identifier Source: org_study_id

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