Trial Outcomes & Findings for Evaluate the Effect of Obicetrapib in Patients With HeFH on Top of Maximum Tolerated Lipid-Modifying Therapies. (NCT NCT05425745)

NCT ID: NCT05425745

Last Updated: 2025-06-11

Results Overview

LS mean percent change from baseline to Day 84 in Low-Density Lipoprotein Cholesterol (LDL-C) in the obicetrapib group compared to the placebo group \[PUC\]. LDL-C level was measured by preparative ultracentrifugation (PUC).

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

354 participants

Primary outcome timeframe

84 Days

Results posted on

2025-06-11

Participant Flow

513 patients were screened: out of 513, 354 participants were randomized: 236 participants to the obicetrapib 10 mg group and 118 participants to the placebo group

Participant milestones

Participant milestones
Measure
Placebo
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Overall Study
STARTED
118
236
Overall Study
COMPLETED
110
226
Overall Study
NOT COMPLETED
8
10

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Overall Study
Withdrawal of Consent
3
3
Overall Study
Death
2
3
Overall Study
Lost to Follow-up
1
2
Overall Study
Adverse Event
0
1
Overall Study
Did not return for end of study visit
0
1
Overall Study
End of study visit completed by phone
1
0
Overall Study
Subject decision
1
0

Baseline Characteristics

4 participants were missing baseline LDL-C (measured by PUC). 2 pts baseline LDL-C results were not available due to low volume or hemolysis. 2 pts were randomized but did not receive study drug. Therefore, baseline values (baseline defined as the last measurement prior to the first dose of study drug) were not available.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=236 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Total
n=354 Participants
Total of all reporting groups
Age, Continuous
56.6 years
STANDARD_DEVIATION 11.06 • n=118 Participants
57 years
STANDARD_DEVIATION 12.70 • n=236 Participants
56.9 years
STANDARD_DEVIATION 12.16 • n=354 Participants
Sex: Female, Male
Female
65 Participants
n=118 Participants
125 Participants
n=236 Participants
190 Participants
n=354 Participants
Sex: Female, Male
Male
53 Participants
n=118 Participants
111 Participants
n=236 Participants
164 Participants
n=354 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=118 Participants
8 Participants
n=236 Participants
10 Participants
n=354 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
114 Participants
n=118 Participants
226 Participants
n=236 Participants
340 Participants
n=354 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
2 Participants
n=118 Participants
2 Participants
n=236 Participants
4 Participants
n=354 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=118 Participants
0 Participants
n=236 Participants
0 Participants
n=354 Participants
Race (NIH/OMB)
Asian
1 Participants
n=118 Participants
6 Participants
n=236 Participants
7 Participants
n=354 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=118 Participants
0 Participants
n=236 Participants
0 Participants
n=354 Participants
Race (NIH/OMB)
Black or African American
3 Participants
n=118 Participants
3 Participants
n=236 Participants
6 Participants
n=354 Participants
Race (NIH/OMB)
White
110 Participants
n=118 Participants
219 Participants
n=236 Participants
329 Participants
n=354 Participants
Race (NIH/OMB)
More than one race
3 Participants
n=118 Participants
4 Participants
n=236 Participants
7 Participants
n=354 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=118 Participants
4 Participants
n=236 Participants
5 Participants
n=354 Participants
Baseline Low-Density Lipoprotein Cholesterol (LDL-C)
119.9 mg/dL
STANDARD_DEVIATION 54.47 • n=118 Participants • 4 participants were missing baseline LDL-C (measured by PUC). 2 pts baseline LDL-C results were not available due to low volume or hemolysis. 2 pts were randomized but did not receive study drug. Therefore, baseline values (baseline defined as the last measurement prior to the first dose of study drug) were not available.
123.4 mg/dL
STANDARD_DEVIATION 49.23 • n=232 Participants • 4 participants were missing baseline LDL-C (measured by PUC). 2 pts baseline LDL-C results were not available due to low volume or hemolysis. 2 pts were randomized but did not receive study drug. Therefore, baseline values (baseline defined as the last measurement prior to the first dose of study drug) were not available.
121.65 mg/dL
STANDARD_DEVIATION 51.85 • n=350 Participants • 4 participants were missing baseline LDL-C (measured by PUC). 2 pts baseline LDL-C results were not available due to low volume or hemolysis. 2 pts were randomized but did not receive study drug. Therefore, baseline values (baseline defined as the last measurement prior to the first dose of study drug) were not available.

PRIMARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in Low-Density Lipoprotein Cholesterol (LDL-C) in the obicetrapib group compared to the placebo group \[PUC\]. LDL-C level was measured by preparative ultracentrifugation (PUC).

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=232 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Low-Density Lipoprotein Cholesterol (LDL-C) From Baseline to Day 84 [PUC]
.25 percent change from baseline
Standard Error 2.480
-36.05 percent change from baseline
Standard Error 1.769

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in Low-Density Lipoprotein Cholesterol (LDL-C) in the obicetrapib group compared to the placebo group \[Martin/Hopkins\]. LDL-C value was calculated using the Martin/Hopkins equation unless TG \>= 400 mg/dL or LDL-C \<= 50 mg/dL; where, LDL-C value was measured directly by preparative ultracentrifugation (PUC).

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Low Density Lipoprotein-Cholesterol (LDL-C) From Baseline to Day 180 [Martin/Hopkins]
5.98 percent change from baseline
Standard Error 2.925
-31.80 percent change from baseline
Standard Error 2.054

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in Low-Density Lipoprotein Cholesterol (LDL-C) in the obicetrapib group compared to the placebo group \[PUC\]. LDL-C level was measured by preparative ultracentrifugation (PUC).

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=232 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Low Density Lipoprotein-Cholesterol (LDL-C) From Baseline to Day 365 [PUC]
10.30 percent change from baseline
Standard Error 4.222
-31.14 percent change from baseline
Standard Error 2.544

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in apolipoprotein B (ApoB) in obicetrapib group compared to the placebo group.

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Apolipoprotein B (ApoB) From Baseline to Day 84
2.93 percent change from baseline
Standard Error 1.758
-21.45 percent change from baseline
Standard Error 1.219

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in apolipoprotein B (ApoB) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Apolipoprotein B (ApoB) From Baseline to Day 180
6.02 percent change from baseline
Standard Error 2.127
-18.30 percent change from baseline
Standard Error 1.472

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in apolipoprotein B (ApoB) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Apolipoprotein B (ApoB) From Baseline to Day 365
8.15 percent change from baseline
Standard Error 2.633
-17.62 percent change from baseline
Standard Error 1.663

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in Non-high-density Lipoprotein Cholesterol (Non-HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Non-HDL-C From Baseline to Day 84
2.83 percent change from baseline
Standard Error 2.188
-31.62 percent change from baseline
Standard Error 1.520

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in Non-high-density Lipoprotein Cholesterol (non-HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Non-HDL-C From Baseline to Day 180
5.92 percent change from baseline
Standard Error 2.658
-27.08 percent change from baseline
Standard Error 1.855

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in Non-high-density Lipoprotein Cholesterol (non-HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Non-HDL-C From Baseline to Day 365
11.64 percent change from baseline
Standard Error 3.905
-25.84 percent change from baseline
Standard Error 2.305

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in High-density Lipoprotein Cholesterol (HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in HDL-C From Baseline to Day 84
1.26 percent change from baseline
Standard Error 5.078
139.92 percent change from baseline
Standard Error 3.614

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in High-density Lipoprotein Cholesterol (HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in HDL-C From Baseline to Day 180
2.63 percent change from baseline
Standard Error 5.484
133.83 percent change from baseline
Standard Error 3.730

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in High-density Lipoprotein Cholesterol (HDL-C) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in HDL-C From Baseline to Day 365
6.28 percent change from baseline
Standard Error 5.994
127.67 percent change from baseline
Standard Error 4.222

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in Lipoprotein (a) \[Lp(a)\] in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Lp(a) From Baseline to Day 84
10.52 percent change from baseline
Standard Error 9.413
-35.42 percent change from baseline
Standard Error 4.527

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in Lipoprotein (a) \[Lp(a)\] in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Lp(a) From Baseline to Day 365
24.37 percent change from baseline
Standard Error 37.111
-29.93 percent change from baseline
Standard Error 11.224

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in Total Cholesterol (TC) in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Total Cholesterol From Baseline to Day 84
2.34 percent change from baseline
Standard Error 1.796
12.09 percent change from baseline
Standard Error 1.268

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in Total Cholesterol in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Total Cholesterol From Baseline to Day 180
4.44 percent change from baseline
Standard Error 2.043
14.43 percent change from baseline
Standard Error 1.438

SECONDARY outcome

Timeframe: 365 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in Total Cholesterol in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Total Cholesterol From Baseline to Day 365
9.32 percent change from baseline
Standard Error 2.801
13.92 percent change from baseline
Standard Error 1.684

SECONDARY outcome

Timeframe: 84 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 84.

LS mean percent change from baseline to Day 84 in Triglycerides in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Triglycerides From Baseline to Day 84
10.16 percent change from baseline
Standard Error 4.207
-1.57 percent change from baseline
Standard Error 2.580

SECONDARY outcome

Timeframe: 180 Days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 180.

LS mean percent change from baseline to Day 180 in Triglycerides in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Percent Change in Triglycerides From Baseline to Day 180
12.43 percent change from baseline
Standard Error 4.178
4.49 percent change from baseline
Standard Error 2.885

SECONDARY outcome

Timeframe: 365 days

Population: Baseline Population is defined as all participants who were randomized in the study. Baseline values were defined as last measurement prior to the first dose of study drug. 2 participants in the obi arm were randomized but did not receive study drug, therefore the "n" for the obi arm baseline values did not exceed n=234. In addition, participants needed available labs at both baseline and Day 365.

LS mean percent change from baseline to Day 365 in Triglycerides in obicetrapib group compared to the placebo group

Outcome measures

Outcome measures
Measure
Placebo
n=118 Participants
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 Participants
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Precent Change in Triglycerides From Baseline to Day 365
7.39 percent change from baseline
Standard Error 5.642
2.27 percent change from baseline
Standard Error 3.219

Adverse Events

Placebo

Serious events: 8 serious events
Other events: 52 other events
Deaths: 2 deaths

Obicetrapib 10 mg

Serious events: 13 serious events
Other events: 95 other events
Deaths: 3 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=118 participants at risk
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 participants at risk
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
General disorders
Death
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Gastrointestinal disorders
Enteritis
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Cardiac disorders
Angina unstable
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.85%
2/234 • Number of events 2 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Cardiac disorders
Angina pectoris
1.7%
2/118 • Number of events 2 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Gastrointestinal disorders
Gastrointestinal fistula
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Vascular disorders
Deep vein thrombosis
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Diabetic gangrene
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Hepatobiliary disorders
Cholecystitis
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Cardiac disorders
Sudden cardiac death
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Cardiac disorders
Acute myocardial infarction
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Respiratory, thoracic and mediastinal disorders
Pneumothorax
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Injury, poisoning and procedural complications
Rib fracture
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.00%
0/234 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Spinal stenosis
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Influenza
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Respiratory, thoracic and mediastinal disorders
Acute respiratory failure
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.85%
2/234 • Number of events 3 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Injury, poisoning and procedural complications
Accident
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Salivary gland adenoma
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Osteoarthritis
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Gastrointestinal disorders
Crohn's disease
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Nervous system disorders
Ischaemic stroke
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Pneumonia
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Cardiac disorders
Myocardial infarction
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Nervous system disorders
Cerebrovascular accident
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Vascular disorders
Angiopathy
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Adenocarcinoma of colon
0.00%
0/118 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.43%
1/234 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.

Other adverse events

Other adverse events
Measure
Placebo
n=118 participants at risk
one placebo tablet once daily Placebo: placebo tablet made to resemble active
Obicetrapib 10 mg
n=234 participants at risk
one 10 mg Obicetrapib tablet once daily Obicetrapib: 10 mg Obicetrapib tablet
Infections and infestations
Influenza
5.9%
7/118 • Number of events 7 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
9.0%
21/234 • Number of events 22 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
COVID-19
6.8%
8/118 • Number of events 8 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
6.4%
15/234 • Number of events 16 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Nasopharyngitis
4.2%
5/118 • Number of events 5 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
6.4%
15/234 • Number of events 17 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Upper respiratory tract infection
3.4%
4/118 • Number of events 4 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
5.1%
12/234 • Number of events 15 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Infections and infestations
Urinary tract infection
4.2%
5/118 • Number of events 5 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
3.0%
7/234 • Number of events 7 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Back pain
5.1%
6/118 • Number of events 6 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
3.0%
7/234 • Number of events 7 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Arthralgia
2.5%
3/118 • Number of events 4 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
3.8%
9/234 • Number of events 9 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Myalgia
0.85%
1/118 • Number of events 1 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
4.3%
10/234 • Number of events 10 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Musculoskeletal and connective tissue disorders
Pain in extremity
3.4%
4/118 • Number of events 4 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
2.6%
6/234 • Number of events 8 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Gastrointestinal disorders
Diarrhea
6.8%
8/118 • Number of events 9 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
3.8%
9/234 • Number of events 10 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Investigations
Blood creatine phosphokinase increased
4.2%
5/118 • Number of events 6 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
1.3%
3/234 • Number of events 4 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Vascular disorders
Hypertension
6.8%
8/118 • Number of events 10 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
6.0%
14/234 • Number of events 14 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
General disorders
Fatigue
5.9%
7/118 • Number of events 7 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
0.85%
2/234 • Number of events 2 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Nervous system disorders
Headache
5.1%
6/118 • Number of events 8 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
3.0%
7/234 • Number of events 9 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
Respiratory, thoracic and mediastinal disorders
Cough
2.5%
3/118 • Number of events 3 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.
2.1%
5/234 • Number of events 5 • From first dose of study drug up to Week 54
Safety Population included all participants who received at least 1 dose of any study drug.

Additional Information

Study Director

NewAmsterdam Pharma

Phone: +1(305) 627-3081

Results disclosure agreements

  • Principal investigator is a sponsor employee After the multicenter publication or 12 months after completion of the study, whichever occurs first, Institution may publish the results of its study data. Institution and PI shall provide sponsor with an advance copy of any proposed communications at least 60 days prior and Sponsor shall have 60 days to review. Sponsor may request (a) the deletion of any Confidential Information, (b) reasonable changes, or (c) a delay for an additional period, not to exceed 90 days.
  • Publication restrictions are in place

Restriction type: OTHER