LDL-C Assessment With PCSK9 Monoclonal Antibody Inhibition Combined With Statin Therapy-2

NCT ID: NCT01763866

Last Updated: 2022-11-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

2067 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-01-15

Study Completion Date

2013-12-04

Brief Summary

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The primary objective was to evaluate the effect of 12 weeks of evolocumab administered subcutaneously every 2 weeks (Q2W) and monthly (QM) when used in combination with a statin, compared with placebo, on percent change from baseline in low-density lipoprotein cholesterol (LDL-C) in patients with primary hypercholesterolemia and mixed dyslipidemia.

Detailed Description

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Prior to the first randomization, participants entered a screening period to determine eligibility. During screening, all participants received subcutaneous placebo corresponding to the once monthly dose volume. Participants who completed the screening period and met eligibility criteria were randomized to 1 of 5 open-label statin cohorts (atorvastatin 10 mg or 80 mg, rosuvastatin 5 mg or 40 mg, or simvastatin 40 mg) for a 4 week lipid stabilization period based on statin therapy at the time of study entry (no statin use vs non-intensive statin use vs intensive statin use).

After the 4-week lipid-stabilization period, eligible patients taking rosuvastatin or simvastatin during the lipid-stabilization phase were then randomized to 1 of 4 treatment groups: evolocumab (140 mg, subcutaneous, every 2 weeks) or matching placebo (subcutaneous, every 2 weeks), or evolocumab (420 mg, subcutaneous, monthly) or matching placebo (subcutaneous, monthly). Patients taking atorvastatin during the lipid-stabilization phase were then randomized to 1 of 6 treatment groups: evolocumab (140 mg, subcutaneous, every 2 weeks) and placebo (oral, daily), evolocumab (420 mg, subcutaneous, monthly) and placebo (oral, daily), placebo (subcutaneous, every 2 weeks) and placebo (oral, daily) or ezetimibe (10 mg, oral, daily), or placebo (subcutaneous, monthly) and placebo (oral, daily) or ezetimibe (10 mg, oral, daily).

A participant was considered randomized into the study after successfully completing the screening period, meeting all inclusion/exclusion criteria, and undergoing both randomization procedures.

Participants randomized to simvastatin who were taking verapamil or diltiazem prior to randomization received simvastatin 10 mg once daily (QD) while participants who were taking amlodipine, amiodarone or ranolazine prior to randomization received simvastatin 20 mg QD. All other participants randomized to simvastatin received simvastatin 40 mg QD.

Conditions

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Hyperlipidemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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A10 PBO Q2W

Participants received atorvastatin 10 mg once daily during the 4 week lipid stabilization period and then in combination with placebo (PBO) subcutaneous injection once every 2 weeks (Q2W) and placebo tablets once daily for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A10 PBO QM

Participants received atorvastatin 10 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every month (QM) and placebo tablets once a day for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A10 EZE (Q2W)

Participants received atorvastatin 10 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks and 10 mg ezetimibe (EZE) orally once a day for up to 12 weeks.

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

Administered orally once a day

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A10 EZE (QM)

Participants received atorvastatin 10 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once a month and 10 mg ezetimibe orally once a day for up to 12 weeks.

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

Administered orally once a day

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A10 EvoMab Q2W

Participants received atorvastatin 10 mg a day during the 4-week lipid stabilization period and then with 140 mg evolocumab (EvoMab) by subcutaneous injection once every 2 weeks and placebo tablets once a day for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A10 EvoMab QM

Participants received atorvastatin 10 mg a day during the 4-week lipid stabilization period and then with 420 mg evolocumab by subcutaneous injection once a month and placebo tablets once a day for up to 12 weeks

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 PBO Q2W

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks and placebo tablets once a day for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 PBO QM

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every month and placebo tablets once a day for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 EZE (Q2W)

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks and 10 mg ezetimibe orally once a day for up to 12 weeks.

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

Administered orally once a day

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 EZE (QM)

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once a month and 10 mg ezetimibe orally once a day for up to 12 weeks.

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

Administered orally once a day

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 EvoMab Q2W

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with 140 mg evolocumab by subcutaneous injection once every 2 weeks and placebo tablets once a day for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

A80 EvoMab QM

Participants received atorvastatin 80 mg a day during the 4-week lipid stabilization period and then with 420 mg evolocumab by subcutaneous injection once a month and placebo tablets once a day for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Placebo to Ezetimibe

Intervention Type DRUG

Administered orally once a day

Atorvastatin

Intervention Type DRUG

Administered orally once a day

R5 PBO Q2W

Participants received rosuvastatin 5 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R5 PBO QM

Participants received rosuvastatin 5 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every month for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R5 EvoMab Q2W

Participants received rosuvastatin 5 mg a day during the 4-week lipid stabilization period and then with 140 mg evolocumab by subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R5 EvoMab QM

Participants received rosuvastatin 5 mg a day during the 4-week lipid stabilization period and then with 420 mg evolocumab by subcutaneous injection once a month for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R40 PBO Q2W

Participants received rosuvastatin 40 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R40 PBO QM

Participants received rosuvastatin 40 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every month for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R40 EvoMab Q2W

Participants received rosuvastatin 40 mg a day during the 4-week lipid stabilization period and then with 140 mg evolocumab by subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

R40 EvoMab QM

Participants received rosuvastatin 40 mg a day during the 4-week lipid stabilization period and then with 420 mg evolocumab by subcutaneous injection once a month for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Rosuvastatin

Intervention Type DRUG

Administered orally once a day

S40 PBO Q2W

Participants received simvastatin 40 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Simvastatin

Intervention Type DRUG

Administered orally once a day

S40 PBO QM

Participants received simvastatin 40 mg a day during the 4-week lipid stabilization period and then with placebo subcutaneous injection once every month for up to 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to Evolocumab

Intervention Type DRUG

Administered by subcutaneous injection

Simvastatin

Intervention Type DRUG

Administered orally once a day

S40 EvoMab Q2W

Participants received simvastatin 40 mg a day during the 4-week lipid stabilization period and then with 140 mg evolocumab by subcutaneous injection once every 2 weeks for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Simvastatin

Intervention Type DRUG

Administered orally once a day

S40 EvoMab QM

Participants received simvastatin 40 mg a day during the 4-week lipid stabilization period and then with 420 mg evolocumab by subcutaneous injection once a month for up to 12 weeks.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Simvastatin

Intervention Type DRUG

Administered orally once a day

Interventions

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Evolocumab

Administered by subcutaneous injection

Intervention Type BIOLOGICAL

Ezetimibe

Administered orally once a day

Intervention Type DRUG

Placebo to Evolocumab

Administered by subcutaneous injection

Intervention Type DRUG

Placebo to Ezetimibe

Administered orally once a day

Intervention Type DRUG

Atorvastatin

Administered orally once a day

Intervention Type DRUG

Rosuvastatin

Administered orally once a day

Intervention Type DRUG

Simvastatin

Administered orally once a day

Intervention Type DRUG

Other Intervention Names

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AMG 145 Repatha Zetia Lipitor Crestor Zocor

Eligibility Criteria

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Inclusion Criteria

* Male or female ≥ 18 to ≤ 80 years of age
* Subjects not taking a statin must have fasting LDL-C of at least 150 mg/dL (4.0 mmol/L)
* Subjects already on a non-intensive statin must have fasting LDL-C at screening ≥ 100 mg/dL (2.6 mmol/L)
* Subjects already on a intensive statin must have fasting LDL-C at screening ≥ 80 mg/dL (2.1 mmol/L)
* Fasting triglycerides ≤ 400 mg/dL (4.5 mmol/L)

Exclusion Criteria

* Statin intolerance
* New York Heart association (NYHA) III or IV heart failure
* Uncontrolled hypertension
* Uncontrolled cardiac arrhythmia
* Type 1 diabetes, poorly controlled type 2 diabetes
* Uncontrolled hypothyroidism or hyperthyroidism
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Reading, , United Kingdom

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Reading, , United Kingdom

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Scunthorpe, , United Kingdom

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Wakefield, , United Kingdom

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Whitby, , United Kingdom

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Chesterfield, , United Kingdom

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Chorley, , United Kingdom

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Doncaster, , United Kingdom

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Glasgow, , United Kingdom

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Glasgow, , United Kingdom

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Harrow, , United Kingdom

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Liverpool, , United Kingdom

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Liverpool, , United Kingdom

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Manchester, , United Kingdom

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Manchester, , United Kingdom

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Birmingham, Alabama, United States

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Glendale, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Carmichael, California, United States

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Encino, California, United States

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Long Beach, California, United States

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Newport Beach, California, United States

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San Diego, California, United States

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Santa Ana, California, United States

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Santa Rosa, California, United States

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Thousand Oaks, California, United States

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Torrance, California, United States

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Tustin, California, United States

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Westlake Village, California, United States

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Littleton, Colorado, United States

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Daytona Beach, Florida, United States

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Jacksonville, Florida, United States

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Melbourne, Florida, United States

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Miami, Florida, United States

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Port Charlotte, Florida, United States

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Atlanta, Georgia, United States

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Atlanta, Georgia, United States

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Boise, Idaho, United States

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Hammond, Indiana, United States

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Indianapolis, Indiana, United States

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Valparaiso, Indiana, United States

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Iowa City, Iowa, United States

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Crestview Hills, Kentucky, United States

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Monroe, Louisiana, United States

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Auburn, Maine, United States

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Bangor, Maine, United States

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Portland, Maine, United States

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Baltimore, Maryland, United States

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Ypsilanti, Michigan, United States

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Tupelo, Mississippi, United States

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Billings, Montana, United States

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Voorhees Township, New Jersey, United States

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Manlius, New York, United States

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Rochester, New York, United States

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Syracuse, New York, United States

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Williamsville, New York, United States

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Winston-Salem, North Carolina, United States

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Cadiz, Ohio, United States

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Canton, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Dayton, Ohio, United States

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Mansfield, Ohio, United States

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Marion, Ohio, United States

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Sandusky, Ohio, United States

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Norman, Oklahoma, United States

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Duncansville, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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York, Pennsylvania, United States

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Florence, South Carolina, United States

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Rapid City, South Dakota, United States

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Jackson, Tennessee, United States

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Jackson, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Suffolk, Virginia, United States

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Winchester, Virginia, United States

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Tacoma, Washington, United States

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Sydney, New South Wales, Australia

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Ashford, South Australia, Australia

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Fullarton, South Australia, Australia

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Fitzroy, Victoria, Australia

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Heidelberg Heights, Victoria, Australia

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Richmond, Victoria, Australia

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Blankenberge, , Belgium

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Chênée, , Belgium

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Hasselt, , Belgium

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Ostend, , Belgium

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Tremelo, , Belgium

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Vilvoorde, , Belgium

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Burnaby, British Columbia, Canada

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Kelowna, British Columbia, Canada

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Kelowna, British Columbia, Canada

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Surrey, British Columbia, Canada

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Saint John’s, Newfoundland and Labrador, Canada

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Cambridge, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Newmarket, Ontario, Canada

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Oshawa, Ontario, Canada

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Sarnia, Ontario, Canada

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Scarborough Village, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Woodstock, Ontario, Canada

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Brossard, Quebec, Canada

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Greenfield Park, Quebec, Canada

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Lachine, Quebec, Canada

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Longueuil, Quebec, Canada

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Montreal, Quebec, Canada

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Pointe-Claire, Quebec, Canada

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Brno, , Czechia

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Brno, , Czechia

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Kladno, , Czechia

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Litoměřice, , Czechia

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Moravské Budějovice, , Czechia

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Olomouc, , Czechia

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Pardubice, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Slaný, , Czechia

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Svitavy, , Czechia

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Ústí nad Orlicí, , Czechia

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Aalborg, , Denmark

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Ballerup Municipality, , Denmark

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Vejle, , Denmark

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Brest, , France

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Caen, , France

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Dijon, , France

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Le Creusot, , France

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Montpellier, , France

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Nantes, , France

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Paris, , France

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Paris, , France

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Poitiers, , France

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Strasbourg, , France

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Bad Krozingen, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Freiburg im Breisgau, , Germany

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Heidelberg, , Germany

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Hellersdorf, , Germany

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Homburg, , Germany

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Leipzig, , Germany

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Magdeburg, , Germany

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Messkirch, , Germany

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Witten, , Germany

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Hong Kong, , Hong Kong

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New Territories, , Hong Kong

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Baja, , Hungary

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Berettyóújfalu, , Hungary

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Dunaújváros, , Hungary

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Eger, , Hungary

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Gyöngyös, , Hungary

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Hódmezővásárhely, , Hungary

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Jászberény, , Hungary

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Komárom, , Hungary

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Marcali, , Hungary

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Mosonmagyaróvár, , Hungary

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Pécs, , Hungary

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Bologna, , Italy

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Cagliari, , Italy

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Chieti, , Italy

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Ferrara, , Italy

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Milan, , Italy

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Napoli, , Italy

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Padua, , Italy

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Perugia, , Italy

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Pisa, , Italy

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Trieste, , Italy

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León, Guanajuato, Mexico

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Guadalajara, Jalisco, Mexico

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Guadalajara, Jalisco, Mexico

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Mexico City, Mexico City, Mexico

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Mexico City, Mexico City, Mexico

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Monterrey, Nuevo León, Mexico

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San Luis Potosí City, San Luis PotosÃ-, Mexico

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Tampico, Tamaulipas, Mexico

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Durango, , Mexico

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Den Helder, , Netherlands

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Groningen, , Netherlands

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Hoogeveen, , Netherlands

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Nieuwegein, , Netherlands

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Nijmegen, , Netherlands

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Rotterdam, , Netherlands

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Waalwijk, , Netherlands

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Zwijndrecht, , Netherlands

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Barnaul, , Russia

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Kemerovo, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saratov, , Russia

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Alberton, Gauteng, South Africa

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Johannesburg, Gauteng, South Africa

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Lyttelton, Gauteng, South Africa

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Pretoria, Gauteng, South Africa

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Kuils River, Western Cape, South Africa

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Somerset West, Western Cape, South Africa

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Bloemfontein, , South Africa

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Cape Town, , South Africa

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Suwon, , South Korea

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Suwon, , South Korea

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AlmerÃ-a, AndalucÃ-a, Spain

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Almería, AndalucÃ-a, Spain

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Barcelona, Cataluña, Spain

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Barcelona, Cataluña, Spain

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L'Hospitalet de Llobregat, Cataluña, Spain

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Pozuelo de Alarcón, Madrid, Spain

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Pozuelo de Alarcón, Madrid, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Ã-rebro, , Sweden

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Göteborg, , Sweden

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Lund, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Uddevalla, , Sweden

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Bellinzona, , Switzerland

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Geneva, , Switzerland

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Lausanne, , Switzerland

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Muensterlingen, , Switzerland

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Sankt Gallen, , Switzerland

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Zurich, , Switzerland

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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Taipei, , Taiwan

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Birmingham, , United Kingdom

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Blackpool, , United Kingdom

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Cardiff, , United Kingdom

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Countries

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United States Australia Belgium Canada Czechia Denmark France Germany Hong Kong Hungary Italy Mexico Netherlands Russia South Africa South Korea Spain Sweden Switzerland Taiwan United Kingdom

References

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Robinson JG, Nedergaard BS, Rogers WJ, Fialkow J, Neutel JM, Ramstad D, Somaratne R, Legg JC, Nelson P, Scott R, Wasserman SM, Weiss R; LAPLACE-2 Investigators. Effect of evolocumab or ezetimibe added to moderate- or high-intensity statin therapy on LDL-C lowering in patients with hypercholesterolemia: the LAPLACE-2 randomized clinical trial. JAMA. 2014 May 14;311(18):1870-82. doi: 10.1001/jama.2014.4030.

Reference Type BACKGROUND
PMID: 24825642 (View on PubMed)

Robinson JG, Rogers WJ, Nedergaard BS, Fialkow J, Neutel JM, Ramstad D, Somaratne R, Legg JC, Nelson P, Scott R, Wasserman SM, Weiss R. Rationale and design of LAPLACE-2: a phase 3, randomized, double-blind, placebo- and ezetimibe-controlled trial evaluating the efficacy and safety of evolocumab in subjects with hypercholesterolemia on background statin therapy. Clin Cardiol. 2014 Apr;37(4):195-203. doi: 10.1002/clc.22252. Epub 2014 Jan 30.

Reference Type BACKGROUND
PMID: 24481874 (View on PubMed)

Daviglus ML, Ferdinand KC, Lopez JAG, Wu Y, Monsalvo ML, Rodriguez CJ. Effects of Evolocumab on Low-Density Lipoprotein Cholesterol, Non-High Density Lipoprotein Cholesterol, Apolipoprotein B, and Lipoprotein(a) by Race and Ethnicity: A Meta-Analysis of Individual Participant Data From Double-Blind and Open-Label Extension Studies. J Am Heart Assoc. 2021 Jan 5;10(1):e016839. doi: 10.1161/JAHA.120.016839. Epub 2020 Dec 16.

Reference Type BACKGROUND
PMID: 33325247 (View on PubMed)

Koren MJ, Jones PH, Robinson JG, Sullivan D, Cho L, Hucko T, Lopez JAG, Fleishman AN, Somaratne R, Stroes E. A Comparison of Ezetimibe and Evolocumab for Atherogenic Lipid Reduction in Four Patient Populations: A Pooled Efficacy and Safety Analysis of Three Phase 3 Studies. Cardiol Ther. 2020 Dec;9(2):447-465. doi: 10.1007/s40119-020-00181-8. Epub 2020 Jun 20.

Reference Type BACKGROUND
PMID: 32564340 (View on PubMed)

Kuchimanchi M, Grover A, Emery MG, Somaratne R, Wasserman SM, Gibbs JP, Doshi S. Population pharmacokinetics and exposure-response modeling and simulation for evolocumab in healthy volunteers and patients with hypercholesterolemia. J Pharmacokinet Pharmacodyn. 2018 Jun;45(3):505-522. doi: 10.1007/s10928-018-9592-y. Epub 2018 May 7.

Reference Type BACKGROUND
PMID: 29736889 (View on PubMed)

Kasichayanula S, Grover A, Emery MG, Gibbs MA, Somaratne R, Wasserman SM, Gibbs JP. Clinical Pharmacokinetics and Pharmacodynamics of Evolocumab, a PCSK9 Inhibitor. Clin Pharmacokinet. 2018 Jul;57(7):769-779. doi: 10.1007/s40262-017-0620-7.

Reference Type BACKGROUND
PMID: 29353350 (View on PubMed)

Shapiro MD, Minnier J, Tavori H, Kassahun H, Flower A, Somaratne R, Fazio S. Relationship Between Low-Density Lipoprotein Cholesterol and Lipoprotein(a) Lowering in Response to PCSK9 Inhibition With Evolocumab. J Am Heart Assoc. 2019 Feb 19;8(4):e010932. doi: 10.1161/JAHA.118.010932.

Reference Type BACKGROUND
PMID: 30755061 (View on PubMed)

Stroes E, Robinson JG, Raal FJ, Dufour R, Sullivan D, Kassahun H, Ma Y, Wasserman SM, Koren MJ. Consistent LDL-C response with evolocumab among patient subgroups in PROFICIO: A pooled analysis of 3146 patients from phase 3 studies. Clin Cardiol. 2018 Oct;41(10):1328-1335. doi: 10.1002/clc.23049. Epub 2018 Oct 21.

Reference Type BACKGROUND
PMID: 30120772 (View on PubMed)

Toth PP, Descamps O, Genest J, Sattar N, Preiss D, Dent R, Djedjos C, Wu Y, Geller M, Uhart M, Somaratne R, Wasserman SM; PROFICIO Investigators. Pooled Safety Analysis of Evolocumab in Over 6000 Patients From Double-Blind and Open-Label Extension Studies. Circulation. 2017 May 9;135(19):1819-1831. doi: 10.1161/CIRCULATIONAHA.116.025233. Epub 2017 Mar 1.

Reference Type BACKGROUND
PMID: 28249876 (View on PubMed)

Toth PP, Jones SR, Monsalvo ML, Elliott-Davey M, Lopez JAG, Banach M. Effect of Evolocumab on Non-High-Density Lipoprotein Cholesterol, Apolipoprotein B, and Lipoprotein(a): A Pooled Analysis of Phase 2 and Phase 3 Studies. J Am Heart Assoc. 2020 Mar 3;9(5):e014129. doi: 10.1161/JAHA.119.014129. Epub 2020 Mar 2.

Reference Type BACKGROUND
PMID: 32114889 (View on PubMed)

Wasserman SM, Sabatine MS, Koren MJ, Giugliano RP, Legg JC, Emery MG, Doshi S, Liu T, Somaratne R, Gibbs JP. Comparison of LDL-C Reduction Using Different Evolocumab Doses and Intervals: Biological Insights and Treatment Implications. J Cardiovasc Pharmacol Ther. 2018 Sep;23(5):423-432. doi: 10.1177/1074248418774043. Epub 2018 May 16.

Reference Type BACKGROUND
PMID: 29768954 (View on PubMed)

May HT, Muhlestein JB, Ma Y, Lopez JAG, Coll B, Nelson J. Effects of Evolocumab on the ApoA1 Remnant Ratio: A Pooled Analysis of Phase 3 Studies. Cardiol Ther. 2019 Jun;8(1):91-102. doi: 10.1007/s40119-019-0133-6. Epub 2019 Mar 9.

Reference Type BACKGROUND
PMID: 30852766 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2012-001363-70

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20110115

Identifier Type: -

Identifier Source: org_study_id

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