Open Label Study of Long Term Evaluation Against LDL-C Trial

NCT ID: NCT01439880

Last Updated: 2022-09-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

1324 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-10-07

Study Completion Date

2018-06-20

Brief Summary

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The primary clinical hypothesis is that long-term exposure of evolocumab (AMG 145) will be safe and well tolerated in adults with hypercholesterolemia.

Detailed Description

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Conditions

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Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Standard of Care

Participants received standard of care (SOC) treatment for the first year of the study (SOC-controlled period). At week 52 participants began treatment with evolocumab 420 mg once a month (QM) for 4 years during the all-investigational product \[all-IP\] period.

Group Type ACTIVE_COMPARATOR

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Standard of care

Intervention Type OTHER

Standard of care therapy as per local practices. This could include prescribed therapies and/or dietary/exercise regimes

Evolocumab + SOC

Participants received evolocumab 420 mg once a month plus standard of care for the first year of the study (SOC-controlled period). At week 52 participants continued treatment with evolocumab 420 mg QM for another 4 years during the all-IP period.

Group Type EXPERIMENTAL

Evolocumab

Intervention Type BIOLOGICAL

Administered by subcutaneous injection

Interventions

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Evolocumab

Administered by subcutaneous injection

Intervention Type BIOLOGICAL

Standard of care

Standard of care therapy as per local practices. This could include prescribed therapies and/or dietary/exercise regimes

Intervention Type OTHER

Other Intervention Names

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AMG 145 Repatha

Eligibility Criteria

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Inclusion Criteria

* Complete a qualifying evolocumab (AMG 145) parent study protocol, including: 20101154 (NCT01375777), 20101155 (NCT01380730), 20090158 (NCT01375751), 20090159 (NCT01375764), and 20110231 (NCT01652703)

Exclusion Criteria

* Experienced a treatment-related serious adverse event that led to investigational product (IP) discontinuation in the parent study
* Have an unstable medical condition, in the judgment of the investigator
* Known sensitivity to any of the products to be administered during dosing
* Currently enrolled in another investigational device or drug study (excluding evolocumab (AMG 145) parent study), or less than 30 days since ending another investigational device or drug study(s),or receiving other investigational agent(s)
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Research Site

Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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Malvern, Arkansas, United States

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Anaheim, California, United States

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Carmichael, California, United States

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Inglewood, California, United States

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Mission Viejo, California, United States

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Newport Beach, California, United States

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Thousand Oaks, California, United States

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Tustin, California, United States

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Colorado Springs, Colorado, United States

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Littleton, Colorado, United States

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Daytona Beach, Florida, United States

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DeLand, Florida, United States

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Green Cove Springs, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Melbourne, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Ponte Vedra, Florida, United States

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Port Charlotte, Florida, United States

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Sanford, Florida, United States

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Atlanta, Georgia, United States

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Savannah, Georgia, United States

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Chicago, Illinois, United States

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Indianapolis, Indiana, United States

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Munster, Indiana, United States

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Iowa City, Iowa, United States

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Louisville, Kentucky, United States

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Auburn, Maine, United States

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Portland, Maine, United States

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Bethesda, Maryland, United States

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Chevy Chase, Maryland, United States

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Brockton, Massachusetts, United States

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Marquette, Michigan, United States

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Brooklyn Center, Minnesota, United States

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Tupelo, Mississippi, United States

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Great Falls, Montana, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Cortlandt Manor, New York, United States

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Endwell, New York, United States

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New York, New York, United States

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Williamsville, New York, United States

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Raleigh, North Carolina, United States

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Raleigh, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Akron, Ohio, United States

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Cadiz, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Dayton, Ohio, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Camp Hill, Pennsylvania, United States

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Duncansville, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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York, Pennsylvania, United States

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Mt. Pleasant, South Carolina, United States

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Rapid City, South Dakota, United States

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Rapid City, South Dakota, United States

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Bristol, Tennessee, United States

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Arlington, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Norfolk, Virginia, United States

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Richmond, Virginia, United States

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Renton, Washington, United States

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Seattle, Washington, United States

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Tacoma, Washington, United States

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Camperdown, New South Wales, Australia

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Maroubra, New South Wales, Australia

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Sydney, New South Wales, Australia

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Perth, Western Australia, Australia

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Anthée, , Belgium

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Brussels, , Belgium

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Gozée, , Belgium

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Gribomont, , Belgium

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Halen, , Belgium

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Ham, , Belgium

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Linkebeek, , Belgium

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Uccle, , Belgium

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Kelowna, British Columbia, Canada

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Bay Roberts, Newfoundland and Labrador, Canada

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Mount Pearl, Newfoundland and Labrador, Canada

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St. John's, Newfoundland and Labrador, Canada

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Cambridge, Ontario, Canada

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Greater Sudbury, Ontario, Canada

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London, Ontario, Canada

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London, Ontario, Canada

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Newmarket, Ontario, Canada

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Sarnia, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Woodstock, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Gatineau, Quebec, Canada

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Granby, Quebec, Canada

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Lachine, Quebec, Canada

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Pointe-Claire, Quebec, Canada

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Québec, Quebec, Canada

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Brno, , Czechia

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Brno, , Czechia

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Brno, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Slaný, , Czechia

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Svitavy, , Czechia

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Ústí nad Orlicí, , Czechia

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Znojmo, , Czechia

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Aalborg, , Denmark

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Ballerup Municipality, , Denmark

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Vejle, , Denmark

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Helsinki, , Finland

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OYS, , Finland

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Berlin, , Germany

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Cologne, , Germany

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New Territories, , Hong Kong

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Budapest, , Hungary

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Debrecen, , Hungary

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Dunaújváros, , Hungary

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Gyula, , Hungary

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Kecskemét, , Hungary

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Komárom, , Hungary

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Szolnok, , Hungary

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Zalaegerszeg, , Hungary

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Nagoya, Aichi-ken, Japan

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Nagoya, Aichi-ken, Japan

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Nagoya, Aichi-ken, Japan

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Fukui-shi, Fukui, Japan

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Kasuga-shi, Fukuoka, Japan

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Fujioka-shi, Gunma, Japan

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Maebashi, Gunma, Japan

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Maebashi, Gunma, Japan

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Takasaki-shi, Gunma, Japan

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Kawanishi-shi, Hyōgo, Japan

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Kobe, Hyōgo, Japan

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Hitachi-shi, Ibaraki, Japan

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Koga-shi, Ibaraki, Japan

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Mito, Ibaraki, Japan

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Komatsu-shi, Ishikawa-ken, Japan

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Takamatsu, Kagawa-ken, Japan

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Kochi, Kochi, Japan

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Kyoto, Kyoto, Japan

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Kyoto, Kyoto, Japan

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Ina-shi, Nagano, Japan

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Matsumoto-shi, Nagano, Japan

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Suwa-shi, Nagano, Japan

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Ibaraki-shi, Osaka, Japan

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Toyonaka-shi, Osaka, Japan

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Hanyu-shi, Saitama, Japan

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Sayama-shi, Saitama, Japan

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Toda-shi, Saitama, Japan

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Chiyoda-ku, Tokyo, Japan

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Hachioji-shi, Tokyo, Japan

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Itabashi-ku, Tokyo, Japan

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Shinagawa-ku, Tokyo, Japan

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Toshima-ku, Tokyo, Japan

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Amsterdam, , Netherlands

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Hoorn, , Netherlands

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Utrecht, , Netherlands

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Oslo, , Norway

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Singapore, , Singapore

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Johannesburg, Gauteng, South Africa

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Midrand, Gauteng, South Africa

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Observatory, Western Cape, South Africa

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Parow, Western Cape, South Africa

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Córdoba, Andalusia, Spain

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Zaragoza, Aragon, Spain

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Barcelona, Catalonia, Spain

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Reus, Catalonia, Spain

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Madrid, , Spain

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Gothenburg, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Stockholm, , Sweden

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London, , United Kingdom

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Countries

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United States Australia Belgium Canada Czechia Denmark Finland Germany Hong Kong Hungary Japan Netherlands Norway Singapore South Africa Spain Sweden United Kingdom

References

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Koren MJ, Sabatine MS, Giugliano RP, Langslet G, Wiviott SD, Kassahun H, Ruzza A, Ma Y, Somaratne R, Raal FJ. Long-term Low-Density Lipoprotein Cholesterol-Lowering Efficacy, Persistence, and Safety of Evolocumab in Treatment of Hypercholesterolemia: Results Up to 4 Years From the Open-Label OSLER-1 Extension Study. JAMA Cardiol. 2017 Jun 1;2(6):598-607. doi: 10.1001/jamacardio.2017.0747.

Reference Type BACKGROUND
PMID: 28291870 (View on PubMed)

Koren MJ, Giugliano RP, Raal FJ, Sullivan D, Bolognese M, Langslet G, Civeira F, Somaratne R, Nelson P, Liu T, Scott R, Wasserman SM, Sabatine MS; OSLER Investigators. Efficacy and safety of longer-term administration of evolocumab (AMG 145) in patients with hypercholesterolemia: 52-week results from the Open-Label Study of Long-Term Evaluation Against LDL-C (OSLER) randomized trial. Circulation. 2014 Jan 14;129(2):234-43. doi: 10.1161/CIRCULATIONAHA.113.007012. Epub 2013 Nov 19.

Reference Type BACKGROUND
PMID: 24255061 (View on PubMed)

Daviglus ML, Ferdinand KC, Lopez JAG, Wu Y, Monsalvo ML, Rodriguez CJ. Effects of Evolocumab on Low-Density Lipoprotein Cholesterol, Non-High Density Lipoprotein Cholesterol, Apolipoprotein B, and Lipoprotein(a) by Race and Ethnicity: A Meta-Analysis of Individual Participant Data From Double-Blind and Open-Label Extension Studies. J Am Heart Assoc. 2021 Jan 5;10(1):e016839. doi: 10.1161/JAHA.120.016839. Epub 2020 Dec 16.

Reference Type BACKGROUND
PMID: 33325247 (View on PubMed)

Hovingh GK, Raal FJ, Dent R, Stefanutti C, Descamps O, Masana L, Lira A, Bridges I, Coll B, Sullivan D. Long-term safety, tolerability, and efficacy of evolocumab in patients with heterozygous familial hypercholesterolemia. J Clin Lipidol. 2017 Nov-Dec;11(6):1448-1457. doi: 10.1016/j.jacl.2017.09.003. Epub 2017 Sep 22.

Reference Type BACKGROUND
PMID: 29066265 (View on PubMed)

Koren MJ, Sabatine MS, Giugliano RP, Langslet G, Wiviott SD, Ruzza A, Ma Y, Hamer AW, Wasserman SM, Raal FJ. Long-Term Efficacy and Safety of Evolocumab in Patients With Hypercholesterolemia. J Am Coll Cardiol. 2019 Oct 29;74(17):2132-2146. doi: 10.1016/j.jacc.2019.08.1024.

Reference Type BACKGROUND
PMID: 31648705 (View on PubMed)

Kasichayanula S, Grover A, Emery MG, Gibbs MA, Somaratne R, Wasserman SM, Gibbs JP. Clinical Pharmacokinetics and Pharmacodynamics of Evolocumab, a PCSK9 Inhibitor. Clin Pharmacokinet. 2018 Jul;57(7):769-779. doi: 10.1007/s40262-017-0620-7.

Reference Type BACKGROUND
PMID: 29353350 (View on PubMed)

Sattar N, Toth PP, Blom DJ, Koren MJ, Soran H, Uhart M, Elliott M, Cyrille M, Somaratne R, Preiss D. Effect of the Proprotein Convertase Subtilisin/Kexin Type 9 Inhibitor Evolocumab on Glycemia, Body Weight, and New-Onset Diabetes Mellitus. Am J Cardiol. 2017 Nov 1;120(9):1521-1527. doi: 10.1016/j.amjcard.2017.07.047. Epub 2017 Jul 31.

Reference Type BACKGROUND
PMID: 28844508 (View on PubMed)

Toth PP, Jones SR, Monsalvo ML, Elliott-Davey M, Lopez JAG, Banach M. Effect of Evolocumab on Non-High-Density Lipoprotein Cholesterol, Apolipoprotein B, and Lipoprotein(a): A Pooled Analysis of Phase 2 and Phase 3 Studies. J Am Heart Assoc. 2020 Mar 3;9(5):e014129. doi: 10.1161/JAHA.119.014129. Epub 2020 Mar 2.

Reference Type BACKGROUND
PMID: 32114889 (View on PubMed)

Schludi B, Giugliano RP, Sabatine MS, Raal FJ, Teramoto T, Koren MJ, Stein EA, Wang H, Monsalvo ML. Time-averaged low-density lipoprotein cholesterol lowering with evolocumab: Pooled analysis of phase 2 trials. J Clin Lipidol. 2022 Jul-Aug;16(4):538-543. doi: 10.1016/j.jacl.2022.05.069. Epub 2022 Jun 6.

Reference Type BACKGROUND
PMID: 35760720 (View on PubMed)

Hirayama A, Yamashita S, Ruzza A, Inomata H, Cyrille M, Lu C, Hamer AW, Yoshida M, Kiyosue A, Teramoto T. Long-Term Treatment With Evolocumab Among Japanese Patients - Final Report of the OSLER Open-Label Extension Studies. Circ J. 2019 Apr 25;83(5):971-977. doi: 10.1253/circj.CJ-19-0139. Epub 2019 Mar 29.

Reference Type BACKGROUND
PMID: 30930429 (View on PubMed)

Sabatine MS, Giugliano RP, Wiviott SD, Raal FJ, Blom DJ, Robinson J, Ballantyne CM, Somaratne R, Legg J, Wasserman SM, Scott R, Koren MJ, Stein EA; Open-Label Study of Long-Term Evaluation against LDL Cholesterol (OSLER) Investigators. Efficacy and safety of evolocumab in reducing lipids and cardiovascular events. N Engl J Med. 2015 Apr 16;372(16):1500-9. doi: 10.1056/NEJMoa1500858. Epub 2015 Mar 15.

Reference Type DERIVED
PMID: 25773607 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2011-001915-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20110110

Identifier Type: -

Identifier Source: org_study_id

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