Evaluation of the Efficacy and Safety of Bempedoic Acid (ETC-1002) in Patients With Hyperlipidemia and Statin Intolerant

NCT ID: NCT02988115

Last Updated: 2020-04-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

345 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-11-16

Study Completion Date

2018-03-16

Brief Summary

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The purpose of this study is to determine if bempedoic acid (ETC-1002) is effective and safe versus placebo in patients with elevated LDL cholesterol and who are statin-intolerant.

Detailed Description

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Conditions

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Hypercholesterolemia Atherosclerotic Cardiovascular Disease Statin Adverse Reaction

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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bempedoic acid

bempedoic acid 180 mg tablet taken orally, daily. Patients remain on ongoing lipid-modifying therapy (not study provided)

Group Type EXPERIMENTAL

bempedoic acid

Intervention Type DRUG

bempedoic acid 180 mg tablet

placebo

Matching placebo tablet taken orally, daily. Patients remain on ongoing lipid-modifying therapy (not study provided)

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type OTHER

Matching placebo tablet

Interventions

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bempedoic acid

bempedoic acid 180 mg tablet

Intervention Type DRUG

placebo

Matching placebo tablet

Intervention Type OTHER

Other Intervention Names

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ETC-1002 placebo control

Eligibility Criteria

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Inclusion Criteria

* Require lipid-modifying therapy for primary or secondary prevention of cardiovascular disease
* Fasting LDL-C ≥130 mg/dL for primary prevention or LDL-C ≥100 mg/dL for secondary prevention (history of HeFH and/or ASCVD)
* Be statin-intolerant (unable to tolerate 2 or more statins)

Exclusion Criteria

* Total fasting triglyceride ≥500 mg/dL
* Renal dysfunction or nephrotic syndrome or history of nephritis
* Body Mass Index (BMI) ≥50 kg/m2
* Significant cardiovascular disease or cardiovascular event in the past 3 months
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Esperion Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ron Haberman, MD

Role: STUDY_DIRECTOR

Esperion Therapeutics, Inc.

Locations

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Gilbert, Arizona, United States

Site Status

Anaheim, California, United States

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Long Beach, California, United States

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Sacramento, California, United States

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Santa Ana, California, United States

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Torrance, California, United States

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Ventura, California, United States

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Hamden, Connecticut, United States

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Daytona Beach, Florida, United States

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Fort Lauderdale, Florida, United States

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Site 1

Miami, Florida, United States

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Site 2

Miami, Florida, United States

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Orlando, Florida, United States

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West Palm Beach, Florida, United States

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Atlanta, Georgia, United States

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Savannah, Georgia, United States

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Meridian, Idaho, United States

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Evanston, Illinois, United States

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Evansville, Indiana, United States

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Iowa City, Iowa, United States

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Waterloo, Iowa, United States

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Monroe, Louisiana, United States

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Slidell, Louisiana, United States

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Tupelo, Mississippi, United States

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Lincoln, Nebraska, United States

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Somerset, New Jersey, United States

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Binghamton, New York, United States

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Endwell, New York, United States

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New Windsor, New York, United States

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Greensboro, North Carolina, United States

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Morganton, North Carolina, United States

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Mount Airy, North Carolina, United States

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Columbus, Ohio, United States

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Marion, Ohio, United States

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Maumee, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Beaver, Pennsylvania, United States

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Langhorne, Pennsylvania, United States

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Cumberland, Rhode Island, United States

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Anderson, South Carolina, United States

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Summerville, South Carolina, United States

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Jackson, Tennessee, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Amarillo, Texas, United States

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Site 1

Dallas, Texas, United States

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Site 2

Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Clinton, Utah, United States

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Hampton, Virginia, United States

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Kenosha, Wisconsin, United States

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Brossard, , Canada

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Chicoutimi, , Canada

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Gatineau, , Canada

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London, , Canada

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Longueuil, , Canada

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Mirabel, , Canada

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Montreal, , Canada

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Newmarket, , Canada

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Oakville, , Canada

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Peterborough, , Canada

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Pointe-Claire, , Canada

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Saint-Jérôme, , Canada

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Sarnia, , Canada

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Toronto, , Canada

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Victoriaville, , Canada

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Countries

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United States Canada

References

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Pinkosky SL, Newton RS, Day EA, Ford RJ, Lhotak S, Austin RC, Birch CM, Smith BK, Filippov S, Groot PHE, Steinberg GR, Lalwani ND. Liver-specific ATP-citrate lyase inhibition by bempedoic acid decreases LDL-C and attenuates atherosclerosis. Nat Commun. 2016 Nov 28;7:13457. doi: 10.1038/ncomms13457.

Reference Type BACKGROUND
PMID: 27892461 (View on PubMed)

Cholesterol Treatment Trialists' (CTT) Collaboration; Baigent C, Blackwell L, Emberson J, Holland LE, Reith C, Bhala N, Peto R, Barnes EH, Keech A, Simes J, Collins R. Efficacy and safety of more intensive lowering of LDL cholesterol: a meta-analysis of data from 170,000 participants in 26 randomised trials. Lancet. 2010 Nov 13;376(9753):1670-81. doi: 10.1016/S0140-6736(10)61350-5. Epub 2010 Nov 8.

Reference Type BACKGROUND
PMID: 21067804 (View on PubMed)

Eckel RH. Approach to the patient who is intolerant of statin therapy. J Clin Endocrinol Metab. 2010 May;95(5):2015-22. doi: 10.1210/jc.2009-2689.

Reference Type BACKGROUND
PMID: 20444930 (View on PubMed)

Ridker PM, Cannon CP, Morrow D, Rifai N, Rose LM, McCabe CH, Pfeffer MA, Braunwald E; Pravastatin or Atorvastatin Evaluation and Infection Therapy-Thrombolysis in Myocardial Infarction 22 (PROVE IT-TIMI 22) Investigators. C-reactive protein levels and outcomes after statin therapy. N Engl J Med. 2005 Jan 6;352(1):20-8. doi: 10.1056/NEJMoa042378.

Reference Type BACKGROUND
PMID: 15635109 (View on PubMed)

Robinson JG, Stone NJ. The 2013 ACC/AHA guideline on the treatment of blood cholesterol to reduce atherosclerotic cardiovascular disease risk: a new paradigm supported by more evidence. Eur Heart J. 2015 Aug 14;36(31):2110-2118. doi: 10.1093/eurheartj/ehv182. Epub 2015 May 20.

Reference Type BACKGROUND
PMID: 25994746 (View on PubMed)

Ballantyne CM, Bays HE, Louie MJ, Smart J, Zhang Y, Ray KK. Factors Associated With Enhanced Low-Density Lipoprotein Cholesterol Lowering With Bempedoic Acid. J Am Heart Assoc. 2022 Aug 2;11(15):e024531. doi: 10.1161/JAHA.121.024531. Epub 2022 Aug 2.

Reference Type DERIVED
PMID: 35916348 (View on PubMed)

Banach M, Duell PB, Gotto AM Jr, Laufs U, Leiter LA, Mancini GBJ, Ray KK, Flaim J, Ye Z, Catapano AL. Association of Bempedoic Acid Administration With Atherogenic Lipid Levels in Phase 3 Randomized Clinical Trials of Patients With Hypercholesterolemia. JAMA Cardiol. 2020 Oct 1;5(10):1124-1135. doi: 10.1001/jamacardio.2020.2314.

Reference Type DERIVED
PMID: 32609313 (View on PubMed)

Laufs U, Banach M, Mancini GBJ, Gaudet D, Bloedon LT, Sterling LR, Kelly S, Stroes ESG. Efficacy and Safety of Bempedoic Acid in Patients With Hypercholesterolemia and Statin Intolerance. J Am Heart Assoc. 2019 Apr 2;8(7):e011662. doi: 10.1161/JAHA.118.011662.

Reference Type DERIVED
PMID: 30922146 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://www.who.int/mediacentre/factsheets/fs317/en/

World Health Organization Fact Sheet No. 317

Other Identifiers

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1002-046

Identifier Type: -

Identifier Source: org_study_id

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