Evaluation of ETC-1002, Ezetimibe, and the Combination in Hypercholesterolemic Patients

NCT ID: NCT01941836

Last Updated: 2019-03-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

349 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-30

Study Completion Date

2014-11-30

Brief Summary

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The purpose of this research study is to see how ETC-1002 is tolerated in the body, to measure the amount of ETC-1002 in the blood, and to determine how ETC-1002 affects the level of LDL-cholesterol (bad cholesterol) and other markers of health and disease in blood and urine in patients with elevated LDL-cholesterol with or without statin intolerance.

Detailed Description

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Hypercholesterolemic patients either with or without a history of statin intolerance (1:1 ratio) will be randomized to receive once daily by mouth capsules containing either ETC-1002, ezetimibe, or ETC-1002 + ezetimibe. This study will explore the safety and efficacy of concomitant administration of ETC-1002 and ezetimibe, while also exploring the effect of ezetimibe on ETC-1002 systemic exposure.

Conditions

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Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ETC-1002 120 mg/day

Orally, once daily in morning as capsules

Group Type EXPERIMENTAL

ETC-1002

Intervention Type DRUG

Patients receive ETC-1002

ETC-1002 180 mg/day

Orally, once daily in morning as capsules

Group Type EXPERIMENTAL

ETC-1002

Intervention Type DRUG

Patients receive ETC-1002

ezetimibe 10mg/day

Orally, once daily in morning as capsules

Group Type ACTIVE_COMPARATOR

Ezetimibe

Intervention Type DRUG

Patients receive ezetimibe

ETC-1002 120 mg/day + ezetimibe 10mg/day

Orally, once daily in morning

Group Type EXPERIMENTAL

ETC-1002

Intervention Type DRUG

Patients receive ETC-1002

Ezetimibe

Intervention Type DRUG

Patients receive ezetimibe

ETC-1002 180 mg/day + ezetimibe 10mg/day

Orally, once daily in morning

Group Type EXPERIMENTAL

ETC-1002

Intervention Type DRUG

Patients receive ETC-1002

Ezetimibe

Intervention Type DRUG

Patients receive ezetimibe

Interventions

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ETC-1002

Patients receive ETC-1002

Intervention Type DRUG

Ezetimibe

Patients receive ezetimibe

Intervention Type DRUG

Other Intervention Names

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Zetia

Eligibility Criteria

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Inclusion Criteria

* Statin intolerant and statin tolerant
* Fasting LDL-C between 130 mg/dL and 220 mg/dL
* Fasting triglyceride less than or equal to 400 mg/dL
* Body mass index (BMI) between 18 and 45 kg/m2

Exclusion Criteria

* History or current clinically significant cardiovascular disease
* History or current type 1 diabetes or uncontrolled type 2 diabetes
* Use of metformin or thiazolidinediones (TZD) within 3 months of screening
* History of joint symptoms difficult to differentiate from myalgia
* Uncontrolled hypothyroidism
* Liver disease or dysfunction
* Renal dysfunction or nephritic syndrome
* Gastrointestinal (GI) conditions or prior GI procedures
* HIV or AIDS
* History or malignancy
* History or drug or alcohol abuse within last 2 years
* Use of experimental or investigational drugs within 30 days of screening
* Use of ETC-1002 in a previous clinical study
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Medpace, Inc.

INDUSTRY

Sponsor Role collaborator

Esperion Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Diane E MacDougall, MS

Role: STUDY_DIRECTOR

Esperion Therapeutics, Inc.

Locations

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Birmingham, Alabama, United States

Site Status

Muscle Shoals, Alabama, United States

Site Status

Chandler, Arizona, United States

Site Status

Beverly Hills, California, United States

Site Status

Chino, California, United States

Site Status

Lincoln, California, United States

Site Status

Long Beach, California, United States

Site Status

Los Angeles, California, United States

Site Status

Newport Beach, California, United States

Site Status

Thousand Oaks, California, United States

Site Status

Vista, California, United States

Site Status

Denver, Colorado, United States

Site Status

Hartford, Connecticut, United States

Site Status

Atlantis, Florida, United States

Site Status

Brandon, Florida, United States

Site Status

Hialeah, Florida, United States

Site Status

Jacksonville, Florida, United States

Site Status

Oviedo, Florida, United States

Site Status

Ponte Vedra, Florida, United States

Site Status

Port Orange, Florida, United States

Site Status

St. Petersburg, Florida, United States

Site Status

West Palm Beach, Florida, United States

Site Status

Decatur, Georgia, United States

Site Status

Marietta, Georgia, United States

Site Status

Meridian, Idaho, United States

Site Status

Evansville, Indiana, United States

Site Status

Kansas City, Kansas, United States

Site Status

Auburn, Maine, United States

Site Status

Lincoln, Nebraska, United States

Site Status

Clifton, New Jersey, United States

Site Status

Albuquerque, New Mexico, United States

Site Status

New Windsor, New York, United States

Site Status

Rochester, New York, United States

Site Status

Williamsville, New York, United States

Site Status

Greensboro, North Carolina, United States

Site Status

Raleigh, North Carolina, United States

Site Status

Salisbury, North Carolina, United States

Site Status

Wilmington, North Carolina, United States

Site Status

Beachwood, Ohio, United States

Site Status

Cincinnati, Ohio, United States

Site Status

Cincinnati, Ohio, United States

Site Status

Cleveland, Ohio, United States

Site Status

Columbus, Ohio, United States

Site Status

Franklin, Ohio, United States

Site Status

Lyndhurst, Ohio, United States

Site Status

Marion, Ohio, United States

Site Status

Willoughby Hills, Ohio, United States

Site Status

Oklahoma City, Oklahoma, United States

Site Status

Tulsa, Oklahoma, United States

Site Status

Eugene, Oregon, United States

Site Status

Mt. Pleasant, South Carolina, United States

Site Status

Kingsport, Tennessee, United States

Site Status

Austin, Texas, United States

Site Status

Dallas, Texas, United States

Site Status

Dallas, Texas, United States

Site Status

Fort Worth, Texas, United States

Site Status

Houston, Texas, United States

Site Status

Houston, Texas, United States

Site Status

Houston, Texas, United States

Site Status

Round Rock, Texas, United States

Site Status

Orem, Utah, United States

Site Status

Salt Lake City, Utah, United States

Site Status

Norfolk, Virginia, United States

Site Status

Richmond, Virginia, United States

Site Status

Olympia, Washington, United States

Site Status

Renton, Washington, United States

Site Status

Seattle, Washington, United States

Site Status

Spokane, Washington, United States

Site Status

Countries

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United States

References

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Ballantyne CM, Davidson MH, Macdougall DE, Bays HE, Dicarlo LA, Rosenberg NL, Margulies J, Newton RS. Efficacy and safety of a novel dual modulator of adenosine triphosphate-citrate lyase and adenosine monophosphate-activated protein kinase in patients with hypercholesterolemia: results of a multicenter, randomized, double-blind, placebo-controlled, parallel-group trial. J Am Coll Cardiol. 2013 Sep 24;62(13):1154-62. doi: 10.1016/j.jacc.2013.05.050. Epub 2013 Jun 13.

Reference Type BACKGROUND
PMID: 23770179 (View on PubMed)

Filippov S, Pinkosky SL, Lister RJ, Pawloski C, Hanselman JC, Cramer CT, Srivastava RAK, Hurley TR, Bradshaw CD, Spahr MA, Newton RS. ETC-1002 regulates immune response, leukocyte homing, and adipose tissue inflammation via LKB1-dependent activation of macrophage AMPK. J Lipid Res. 2013 Aug;54(8):2095-2108. doi: 10.1194/jlr.M035212. Epub 2013 May 24.

Reference Type BACKGROUND
PMID: 23709692 (View on PubMed)

Pinkosky SL, Filippov S, Srivastava RA, Hanselman JC, Bradshaw CD, Hurley TR, Cramer CT, Spahr MA, Brant AF, Houghton JL, Baker C, Naples M, Adeli K, Newton RS. AMP-activated protein kinase and ATP-citrate lyase are two distinct molecular targets for ETC-1002, a novel small molecule regulator of lipid and carbohydrate metabolism. J Lipid Res. 2013 Jan;54(1):134-51. doi: 10.1194/jlr.M030528. Epub 2012 Nov 1.

Reference Type BACKGROUND
PMID: 23118444 (View on PubMed)

Gutierrez MJ, Rosenberg NL, Macdougall DE, Hanselman JC, Margulies JR, Strange P, Milad MA, McBride SJ, Newton RS. Efficacy and safety of ETC-1002, a novel investigational low-density lipoprotein-cholesterol-lowering therapy for the treatment of patients with hypercholesterolemia and type 2 diabetes mellitus. Arterioscler Thromb Vasc Biol. 2014 Mar;34(3):676-83. doi: 10.1161/ATVBAHA.113.302677. Epub 2014 Jan 2.

Reference Type BACKGROUND
PMID: 24385236 (View on PubMed)

Thompson PD, MacDougall DE, Newton RS, Margulies JR, Hanselman JC, Orloff DG, McKenney JM, Ballantyne CM. Treatment with ETC-1002 alone and in combination with ezetimibe lowers LDL cholesterol in hypercholesterolemic patients with or without statin intolerance. J Clin Lipidol. 2016 May-Jun;10(3):556-67. doi: 10.1016/j.jacl.2015.12.025. Epub 2016 Jan 6.

Reference Type DERIVED
PMID: 27206943 (View on PubMed)

Other Identifiers

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1002-008

Identifier Type: -

Identifier Source: org_study_id

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