Evaluation of Long-Term Safety and Tolerability of ETC-1002 in High-Risk Patients With Hyperlipidemia and High CV Risk (CLEAR Harmony)

NCT ID: NCT02666664

Last Updated: 2020-05-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

2230 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-01-21

Study Completion Date

2018-03-28

Brief Summary

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The purpose of this study is to see if ETC-1002 (bempedoic acid) is safe and well-tolerated versus placebo in patients with high cardiovascular risk and elevated LDL cholesterol that is not adequately controlled by their current therapy.

Detailed Description

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Conditions

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Hypercholesterolemia Atherosclerotic Cardiovascular Diseases

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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ETC-1002

ETC-1002 180 mg/day

Group Type EXPERIMENTAL

ETC-1002

Intervention Type DRUG

ETC-1002 180 mg tablets taken orally, once per day. Patients remain on ongoing statin therapy (not study provided)

Placebo

Placebo control

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo tablets taken orally, once per day. Patients remain on ongoing statin therapy (not study provided)

Interventions

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ETC-1002

ETC-1002 180 mg tablets taken orally, once per day. Patients remain on ongoing statin therapy (not study provided)

Intervention Type DRUG

Placebo

Matching placebo tablets taken orally, once per day. Patients remain on ongoing statin therapy (not study provided)

Intervention Type DRUG

Other Intervention Names

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bempedoic acid

Eligibility Criteria

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Inclusion Criteria

* Fasting LDL-C ≥ 70 mg/dL
* High cardiovascular risk (diagnosis of HeFH or ASCVD)
* Be on maximally tolerated lipid-modifying therapy

Exclusion Criteria

* Total fasting triglyceride ≥500 mg/dL
* Renal dysfunction or nephrotic syndrome or history of nephritis
* Body Mass Index (BMI) ≥50kg/m2
* Significant cardiovascular disease or cardiovascular event in the past 3 months
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Esperion Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ron Haberman, MD

Role: STUDY_DIRECTOR

Esperion Therapeutics, Inc.

Locations

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Huntsville, Alabama, United States

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Cottonwood, Arizona, United States

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Phoenix, Arizona, United States

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Canoga Park, California, United States

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Santa Rosa, California, United States

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Bridgeport, Connecticut, United States

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Hartford, Connecticut, United States

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Atlantis, Florida, United States

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Boca Raton, Florida, United States

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Crestview, Florida, United States

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Crystal River, Florida, United States

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Daytona Beach, Florida, United States

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Lake Worth, Florida, United States

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Miami Lakes, Florida, United States

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Tampa, Florida, United States

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Park Ridge, Illinois, United States

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Iowa City, Iowa, United States

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Overland Park, Kansas, United States

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Covington, Kentucky, United States

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Louisville, Kentucky, United States

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Minden, Louisiana, United States

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Monroe, Louisiana, United States

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Shreveport, Louisiana, United States

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Auburn, Maine, United States

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Midland, Michigan, United States

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Saginaw, Michigan, United States

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Saint Cloud, Minnesota, United States

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Tupelo, Mississippi, United States

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Jefferson City, Missouri, United States

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Nashua, New Hampshire, United States

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Bridgewater, New Jersey, United States

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Cary, North Carolina, United States

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Mount Airy, North Carolina, United States

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Raleigh, North Carolina, United States

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Rocky Mount, North Carolina, United States

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Wilmington, North Carolina, United States

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Cincinnati, Ohio, United States

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Sandusky, Ohio, United States

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Willoughby, Ohio, United States

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Hillsboro, Oregon, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Katy, Texas, United States

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Kingwood, Texas, United States

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Orem, Utah, United States

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Richmond, Virginia, United States

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Puyallup, Washington, United States

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Tacoma, Washington, United States

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Vancouver, British Columbia, Canada

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Victoria, British Columbia, Canada

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Gatineau, Ontario, Canada

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Mississauga, Ontario, Canada

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Oshawa, Ontario, Canada

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Peterborough, Ontario, Canada

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Scarborough Village, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Gatineau, Quebec, Canada

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Longueuil, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Saint-Charles-Borromée, Quebec, Canada

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Saint-Jean-sur-Richelieu, Quebec, Canada

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Berlin, , Germany

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Bochum, , Germany

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Dresden, , Germany

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Essen, , Germany

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Frankfurt, , Germany

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Leipzig, , Germany

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München, , Germany

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Amsterdam, , Netherlands

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Arnhem, , Netherlands

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Eindhoven, , Netherlands

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Goes, , Netherlands

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Groningen, , Netherlands

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Hardenberg, , Netherlands

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Leiden, , Netherlands

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Rotterdam, , Netherlands

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Tilburg, , Netherlands

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Venlo, , Netherlands

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Zutphen, , Netherlands

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Gdansk, , Poland

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Gdynia, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lowicz, , Poland

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Poznan, , Poland

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Puławy, , Poland

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Torun, , Poland

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Wroclaw, , Poland

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Bexhill-on-Sea, , United Kingdom

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Birmingham, , United Kingdom

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Cardiff, , United Kingdom

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Chesterfield, , United Kingdom

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Chichester, , United Kingdom

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Chippenham, , United Kingdom

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Chorley, , United Kingdom

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Glasgow, , United Kingdom

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Hexham, , United Kingdom

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Hull, , United Kingdom

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Ipswich, , United Kingdom

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Liverpool, , United Kingdom

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Manchester, , United Kingdom

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Reading, , United Kingdom

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Countries

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United States Canada Germany Netherlands Poland United Kingdom

References

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Pinkosky SL, Newton RS, Day EA, Ford RJ, Lhotak S, Austin RC, Birch CM, Smith BK, Filippov S, Groot PHE, Steinberg GR, Lalwani ND. Liver-specific ATP-citrate lyase inhibition by bempedoic acid decreases LDL-C and attenuates atherosclerosis. Nat Commun. 2016 Nov 28;7:13457. doi: 10.1038/ncomms13457.

Reference Type BACKGROUND
PMID: 27892461 (View on PubMed)

Stone NJ, Robinson JG, Lichtenstein AH, Bairey Merz CN, Blum CB, Eckel RH, Goldberg AC, Gordon D, Levy D, Lloyd-Jones DM, McBride P, Schwartz JS, Shero ST, Smith SC Jr, Watson K, Wilson PW, Eddleman KM, Jarrett NM, LaBresh K, Nevo L, Wnek J, Anderson JL, Halperin JL, Albert NM, Bozkurt B, Brindis RG, Curtis LH, DeMets D, Hochman JS, Kovacs RJ, Ohman EM, Pressler SJ, Sellke FW, Shen WK, Smith SC Jr, Tomaselli GF; American College of Cardiology/American Heart Association Task Force on Practice Guidelines. 2013 ACC/AHA guideline on the treatment of blood cholesterol to reduce atherosclerotic cardiovascular risk in adults: a report of the American College of Cardiology/American Heart Association Task Force on Practice Guidelines. Circulation. 2014 Jun 24;129(25 Suppl 2):S1-45. doi: 10.1161/01.cir.0000437738.63853.7a. Epub 2013 Nov 12. No abstract available.

Reference Type BACKGROUND
PMID: 24222016 (View on PubMed)

Goldberg AC, Hopkins PN, Toth PP, Ballantyne CM, Rader DJ, Robinson JG, Daniels SR, Gidding SS, de Ferranti SD, Ito MK, McGowan MP, Moriarty PM, Cromwell WC, Ross JL, Ziajka PE; National Lipid Association Expert Panel on Familial Hypercholesterolemia. Familial hypercholesterolemia: screening, diagnosis and management of pediatric and adult patients: clinical guidance from the National Lipid Association Expert Panel on Familial Hypercholesterolemia. J Clin Lipidol. 2011 Jun;5(3 Suppl):S1-8. doi: 10.1016/j.jacl.2011.04.003. Epub 2011 Apr 12.

Reference Type BACKGROUND
PMID: 21600525 (View on PubMed)

Pollex RL, Joy TR, Hegele RA. Emerging antidyslipidemic drugs. Expert Opin Emerg Drugs. 2008 Jun;13(2):363-81. doi: 10.1517/14728214.13.2.363.

Reference Type BACKGROUND
PMID: 18537526 (View on PubMed)

Sharrett AR, Ballantyne CM, Coady SA, Heiss G, Sorlie PD, Catellier D, Patsch W; Atherosclerosis Risk in Communities Study Group. Coronary heart disease prediction from lipoprotein cholesterol levels, triglycerides, lipoprotein(a), apolipoproteins A-I and B, and HDL density subfractions: The Atherosclerosis Risk in Communities (ARIC) Study. Circulation. 2001 Sep 4;104(10):1108-13. doi: 10.1161/hc3501.095214.

Reference Type BACKGROUND
PMID: 11535564 (View on PubMed)

Ray KK, Bays HE, Catapano AL, Lalwani ND, Bloedon LT, Sterling LR, Robinson PL, Ballantyne CM; CLEAR Harmony Trial. Safety and Efficacy of Bempedoic Acid to Reduce LDL Cholesterol. N Engl J Med. 2019 Mar 14;380(11):1022-1032. doi: 10.1056/NEJMoa1803917.

Reference Type RESULT
PMID: 30865796 (View on PubMed)

Ridker PM, Lei L, Ray KK, Ballantyne CM, Bradwin G, Rifai N. Effects of bempedoic acid on CRP, IL-6, fibrinogen and lipoprotein(a) in patients with residual inflammatory risk: A secondary analysis of the CLEAR harmony trial. J Clin Lipidol. 2023 Mar-Apr;17(2):297-302. doi: 10.1016/j.jacl.2023.02.002. Epub 2023 Feb 14.

Reference Type DERIVED
PMID: 36813656 (View on PubMed)

Ballantyne CM, Bays HE, Louie MJ, Smart J, Zhang Y, Ray KK. Factors Associated With Enhanced Low-Density Lipoprotein Cholesterol Lowering With Bempedoic Acid. J Am Heart Assoc. 2022 Aug 2;11(15):e024531. doi: 10.1161/JAHA.121.024531. Epub 2022 Aug 2.

Reference Type DERIVED
PMID: 35916348 (View on PubMed)

Banach M, Duell PB, Gotto AM Jr, Laufs U, Leiter LA, Mancini GBJ, Ray KK, Flaim J, Ye Z, Catapano AL. Association of Bempedoic Acid Administration With Atherogenic Lipid Levels in Phase 3 Randomized Clinical Trials of Patients With Hypercholesterolemia. JAMA Cardiol. 2020 Oct 1;5(10):1124-1135. doi: 10.1001/jamacardio.2020.2314.

Reference Type DERIVED
PMID: 32609313 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Related Links

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http://www.who.int/mediacentre/factsheets/fs317/en/

World Health Organization Fact Sheet No. 317

https://rarediseases.org/rare-diseases/familial-hypercholesterolemia/

National Organization for Rare Disorders - Familial Hypercholesterolemia

Other Identifiers

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2015-004136-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

1002-040

Identifier Type: -

Identifier Source: org_study_id

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