Efficacy and Safety Study of ELND005 as a Treatment for Agitation and Aggression in Alzheimer's Disease

NCT ID: NCT01735630

Last Updated: 2019-10-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

350 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-11-30

Study Completion Date

2015-05-31

Brief Summary

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The primary purpose of this study is to determine whether ELND005 is effective in treating symptoms of agitation and aggression in patients with Alzheimer's disease

Detailed Description

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Conditions

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Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ELND005

ELND005 film coated tablets, BID for 12 weeks

Group Type EXPERIMENTAL

ELND005

Intervention Type DRUG

Placebo

Matched placebo BID for 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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ELND005

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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Scyllo-inositol

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of Probable AD according to the National Institute on Aging- Alzheimer's Association (NIA-AA) guidelines (McKhann et al 2011).
* MMSE score of 5 to 24 (inclusive) at the Screening Visit.
* Has clinically significant agitation/aggression defined as Neuropsychiatric Inventory (NPI)-agitation/aggression subscore of ≥4.
* No response or suboptimal response to standard nonpharmacological interventions.

Exclusion Criteria

* The agitation/aggression is attributable to concomitant medications, environmental conditions, or active medical or psychiatric condition.
* Current diagnosis of major depressive disorder according to the criteria of the Diagnostic and Statistical Manual of Mental Disorders Fourth Edition Text Revision (DSM IV TR).
* Has persistent and distressing psychotic symptoms (delusion and/or hallucinations) that require psychiatric hospitalization.
Minimum Eligible Age

50 Years

Maximum Eligible Age

95 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Elan Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

OPKO Health, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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TransitionTIL Investigational Site

Birmingham, Alabama, United States

Site Status

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Encino, California, United States

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Escondido, California, United States

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Fresno, California, United States

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Irvine, California, United States

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Long Beach, California, United States

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Los Alamitos, California, United States

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Los Angeles, California, United States

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Newport Beach, California, United States

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Santa Ana, California, United States

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Norwalk, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Atlantis, Florida, United States

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Deerfield Beach, Florida, United States

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Delray Beach, Florida, United States

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Lake Worth, Florida, United States

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Miami, Florida, United States

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Oakland Park, Florida, United States

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Orlando, Florida, United States

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Ormond Beach, Florida, United States

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Port Charlotte, Florida, United States

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Sarasota, Florida, United States

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Sunrise, Florida, United States

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Columbus, Georgia, United States

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Savannah, Georgia, United States

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Springfield, Illinois, United States

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Bangor, Maine, United States

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Easton, Maryland, United States

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Winchester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Paw Paw, Michigan, United States

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Saint Paul, Minnesota, United States

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Hattiesburg, Mississippi, United States

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Stratford, New Jersey, United States

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Rochester, New York, United States

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Rochester, New York, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Abington, Pennsylvania, United States

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Jenkintown, Pennsylvania, United States

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Norristown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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North Charleston, South Carolina, United States

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Port Royal, South Carolina, United States

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Nashville, Tennessee, United States

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DeSoto, Texas, United States

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Richmond, Virginia, United States

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Bellevue, Washington, United States

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Calgary, Alberta, Canada

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Kelowna, British Columbia, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Regina, Saskatchewan, Canada

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Elche, Alicante, Spain

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Getxo, Biscay, Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Burgos, , Spain

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Madrid, , Spain

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Bath, , United Kingdom

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Swindon, , United Kingdom

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Countries

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United States Canada Spain United Kingdom

Other Identifiers

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2012-004299-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ELND005-AG201

Identifier Type: -

Identifier Source: org_study_id

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