A Phase 2 Study to Evaluate Efficacy and Safety of AL002 in Participants With Early Alzheimer's Disease

NCT ID: NCT04592874

Last Updated: 2025-10-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

356 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-22

Study Completion Date

2024-09-12

Brief Summary

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A phase 2 randomized, double blind, placebo controlled study evaluating the efficacy and safety of AL002 in participants with Early Alzheimer's Disease.

Detailed Description

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This is a phase 2 randomized, double blind, placebo controlled study evaluating the efficacy and safety of AL002 administered intravenously in participants with Early Alzheimer's Disease.

Conditions

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Alzheimer Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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AL002 Dose 1

AL002 every 4 weeks

Group Type EXPERIMENTAL

AL002

Intervention Type DRUG

Administered via intravenous (IV) infusion

AL002 Dose 2

AL002 every 4 weeks

Group Type EXPERIMENTAL

AL002

Intervention Type DRUG

Administered via intravenous (IV) infusion

AL002 Dose 3

AL002 every 4 weeks

Group Type EXPERIMENTAL

AL002

Intervention Type DRUG

Administered via intravenous (IV) infusion

Placebo

Placebo every 4 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered via intravenous (IV) infusion

Interventions

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AL002

Administered via intravenous (IV) infusion

Intervention Type DRUG

Placebo

Administered via intravenous (IV) infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of Early AD including evidence of brain amyloidosis by CSF or PET
* MMSE score ≥ 20 points, CDR Global Score of 0.5 - 1.0, and RBANS score on the DMI ≤95.
* Study partner who consents to study participation and who cares for/visits the participant at least 10 hours a week
* Written informed consent must be obtained and documented (from the participant or, where jurisdictions allow it, from their legal decision maker).

Exclusion Criteria

* Dementia due to a condition other than AD including, but not limited to, FTD, Parkinson's disease, dementia with Lewy bodies, Huntington disease, or vascular dementia.
* Known history of severe allergic, anaphylactic, or other hypersensitivity reactions to chimeric, human, or humanized antibodies or fusion proteins.
* Current uncontrolled hypertension, diabetes mellitus or thyroid disease. Clinically significant heart disease, liver disease or kidney disease.
* History or evidence of clinically significant brain disease other than AD.
* Females who are pregnant or breastfeeding, or planning to conceive within the study period.
* Any experimental vaccine or gene therapy.
* History of unresolved cancer.
* Current use of anticoagulant medications.
* Residence in a skilled nursing facility, convalescent home, or long term care facility at screening; or requires continuous nursing care.
* Participant is positive for presence of APOE e4/e4 genotype.
Minimum Eligible Age

50 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alector Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Catherine Mummery

Role: PRINCIPAL_INVESTIGATOR

Locations

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Banner Alzheimer's Institute

Phoenix, Arizona, United States

Site Status

Woodlands Research Network, LLC - ERG

Rogers, Arkansas, United States

Site Status

ATP Clinical Research

Costa Mesa, California, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

South Florida Neurology Associates

Boca Raton, Florida, United States

Site Status

Brain Matters Research - ERG

Delray Beach, Florida, United States

Site Status

Charter Research

Lady Lake, Florida, United States

Site Status

ClinCloud, LLC

Maitland, Florida, United States

Site Status

K2 Medical Research

Maitland, Florida, United States

Site Status

K2 Winter Garden Ocoee

Ocoee, Florida, United States

Site Status

Progressive Medical Research

Port Orange, Florida, United States

Site Status

Axiom Clinical Research FL

Tampa, Florida, United States

Site Status

K2 The Villages

The Villages, Florida, United States

Site Status

Alzheimers Research and Treatment Center

Wellington, Florida, United States

Site Status

Conquest Clinical Research (Winter Park)

Winter Park, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

AMITA Health Clinical Research Institute

Elk Grove Village, Illinois, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Boston Center for Memory

Newton, Massachusetts, United States

Site Status

Hattiesburg Clinic

Hattiesburg, Mississippi, United States

Site Status

Advanced Clinical Institute

Neptune City, New Jersey, United States

Site Status

Feinstein Institute For MR

Manhasset, New York, United States

Site Status

Columbia University College of Physicians and Surgeons

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

SUNY Upstate Medical Center

Syracuse, New York, United States

Site Status

University of Cincinnati MC

Cincinnati, Ohio, United States

Site Status

Summit Research Network

Portland, Oregon, United States

Site Status

Abington Neurologic Associates

Abington, Pennsylvania, United States

Site Status

Clinical Trial Network

Houston, Texas, United States

Site Status

Instituto Kremer

Córdoba, , Argentina

Site Status

Centro de Psiquiatría Biológica Instituto Senecta

Mendoza, , Argentina

Site Status

KaRa Institute of Neurological Disease

Macquarie Park, New South Wales, Australia

Site Status

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status

The Alfred Hospital

Parkville, Victoria, Australia

Site Status

SMarT Minds WA

Nedlands, Western Australia, Australia

Site Status

Okanagan Clinical Trials

Kelowna, British Columbia, Canada

Site Status

True North Clinical Research - Halifax

Halifax, Nova Scotia, Canada

Site Status

True North Clinical Research - New Minas

New Minas, Nova Scotia, Canada

Site Status

Parkwood Institute

London, Ontario, Canada

Site Status

Bruyère Research Institute

Ottawa, Ontario, Canada

Site Status

Kawartha Regional Memory Clinic

Peterborough, Ontario, Canada

Site Status

Toronto Memory Clinic

Toronto, Ontario, Canada

Site Status

Baycrest Health Sciences

Toronto, Ontario, Canada

Site Status

Hôpital Roger Salengro

Lille, Nord, France

Site Status

Hopital Lariboisiere

Paris, , France

Site Status

Hôpital de la Pitié Salpétrière

Paris, , France

Site Status

Centre Hospitalier Universitaire de Toulouse

Toulouse, , France

Site Status

Gerontopole

Toulouse, , France

Site Status

Charité - Universitätsmedizin Berlin (CBF)

Berlin, , Germany

Site Status

Charite Campus Buch

Berlin, , Germany

Site Status

University Clinic Heidelberg

Mannheim, , Germany

Site Status

LMU Klinikum der Universität München

München, , Germany

Site Status

Klinikum rechts der Isa der Technischen Universitaet Muenchen

München, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Fondazione Policlinico Universitario A Gemelli

Rome, Lazio, Italy

Site Status

Azienda Policlinico Umberto I

Rome, Lazio, Italy

Site Status

Ospedale S Giovanni Calibita Fatebenefratelli

Rome, Lazio, Italy

Site Status

IRCCS - Centro S. Giovanni di Dio Fatebenefratelli

Brescia, Lombardy, Italy

Site Status

ASST degli Spedali Civili di Brescia - Spedali Civili di Brescia

Brescia, , Italy

Site Status

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta

Milan, , Italy

Site Status

Ospedale Civile di Baggiovara

Modena, , Italy

Site Status

Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

Site Status

Ospedale degli Infermi

Ponderano, , Italy

Site Status

Brain Research Center Den Bosch

's-Hertogenbosch, North Brabant, Netherlands

Site Status

Brain Research Center Amsterdam

Amsterdam, , Netherlands

Site Status

CGM Research Trust

Christchurch, , New Zealand

Site Status

NZOZ Wroclawskie Centrum Alzheimerowskie

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Centrum Medyczne NeuroProtect

Warsaw, Masovian Voivodeship, Poland

Site Status

EUROMEDIS Sp. z o.o.

Szczecin, West Pomeranian Voivodeship, Poland

Site Status

SOMED CR

Warsaw, , Poland

Site Status

Centro de Atencion Especializada Oroitu

Getxo, Basque Country, Spain

Site Status

Hospital de La Santa Creu i Sant Pau

Barcelona, Catalonia, Spain

Site Status

Fundacion CITA Alzheimer Fundazioa

Donostia / San Sebastian, Guipuzcoa, Spain

Site Status

Fundacion ACE Instituto Catalan de Neurociencias

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario Doctor Peset

Valencia, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Hospital Viamed Montecanal

Zaragoza, , Spain

Site Status

Re: Cognition Health - Guildford

Guildford, Surrey, United Kingdom

Site Status

Re:Cognition Health Bristol

Bristol, , United Kingdom

Site Status

Re:Cognition Health London

London, , United Kingdom

Site Status

The National Hospital for Neurology and Neurosurgery

London, , United Kingdom

Site Status

Greater Manchester Mental Health NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Glasgow Memory Clinic

Motherwell, , United Kingdom

Site Status

Re:Cognition Health Plymouth

Plymouth, , United Kingdom

Site Status

Countries

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United States Argentina Australia Canada France Germany Italy Netherlands New Zealand Poland Spain United Kingdom

References

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Shao Q, Chen S, Zheng Y, Xu W, Chen J, Shao W, Wang Q, Li C, Wang X. Crucial role of microglia-mediated myelin sheath damage in vascular dementia: Antecedents and consequences. Neural Regen Res. 2026 Mar 1;21(3):1000-1012. doi: 10.4103/NRR.NRR-D-24-01109. Epub 2025 Mar 25.

Reference Type DERIVED
PMID: 40145953 (View on PubMed)

Brodtmann A, Darby D, Oboudiyat C, Mahoney CJ, Le Heron C, Panegyres PK, Brew B. Assessing preparedness for Alzheimer disease-modifying therapies in Australasian health care systems. Med J Aust. 2023 Apr 3;218(6):247-249. doi: 10.5694/mja2.51880. Epub 2023 Mar 19. No abstract available.

Reference Type DERIVED
PMID: 36934371 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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AL002-2

Identifier Type: -

Identifier Source: org_study_id

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