An Open-Label, Long-Term Study of Oral Treprostinil in Subjects With Pulmonary Arterial Hypertension

NCT ID: NCT01560637

Last Updated: 2022-06-02

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

471 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-11

Study Completion Date

2021-08-12

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study is an international, multi-center, open-label study designed to provide oral treprostinil (UT-15C) to eligible subjects with pulmonary arterial hypertension who have completed the TDE-PH-310 study. The purpose of this study is to assess the long-term safety of UT-15C and to assess the effects of long-term treatment with UT-15C on exercise capacity.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Pulmonary Arterial Hypertension

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

UT-15C

Open label access

Group Type EXPERIMENTAL

UT-15C (treprostinil diolamine)

Intervention Type DRUG

UT-15C extended release oral tablet three times daily

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

UT-15C (treprostinil diolamine)

UT-15C extended release oral tablet three times daily

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participated in United Therapeutics Study TDE-PH-310
* All women of childbearing potential (WOCBP) must have practiced true abstinence from intercourse when it was in line with their preferred and usual lifestyle or used 2 different forms of highly effective contraception for the duration of the study and for at least 30 days after discontinuing study medication.
* Males who participated in the study must have used a condom during the length of the study and for at least 48 hours after their last dose of study medication.

Exclusion Criteria

* The subject was pregnant or lactating.
* The subject had received infused or inhaled prostacyclin therapy for 29 days or more.
* The subject was prematurely discontinued from TDE-PH-310 for reasons other than a clinical worsening event.
* The subject developed a concurrent illness or condition during the conduct of TDE-PH-310 which, in the opinion of the Investigator, would represent a risk to their overall health if they enrolled in this study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Arizona Pulmonary Specialists, Ltd.

Phoenix, Arizona, United States

Site Status

University of Arizona

Tucson, Arizona, United States

Site Status

University of California, San Francisco-Fresno

Fresno, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

University of California-Davis Medical Group, Advanced Lung Disease/Transplant Program

Sacramento, California, United States

Site Status

David Geffen School of Medicine

Torrance, California, United States

Site Status

University of Colorado Hospital

Aurora, Colorado, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

University of Florida College of Medicine Jacksonville- Division of Pulmonary & Critical Medicine

Jacksonville, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

Augusta University

Augusta, Georgia, United States

Site Status

Piedmont - Georgia Lung Associates

Austell, Georgia, United States

Site Status

HeartCare Midwest

Peoria, Illinois, United States

Site Status

Indiana University Hospital

Carmel, Indiana, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Beaumont Health

Troy, Michigan, United States

Site Status

Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Newark Beth Israel Medical Center

Newark, New Jersey, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

Asheville Cardiology Associates

Asheville, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

University Hospital

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Legacy Research Institute

Portland, Oregon, United States

Site Status

Perelman Center for Advanced Medicine, University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center - Presbyterian Cardiovascular Institute

Pittsburgh, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

Sentara Cardiovascular Research Institute

Norfolk, Virginia, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Aurora Saint Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Sanatorio San José

CABA, Buenos Aires, Argentina

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, Distrito Federal, Argentina

Site Status

Hospital Italiano Garibaldi

Rosario, Santa Fe Province, Argentina

Site Status

Sanatorio de la Trinidad Mitre

Buenos Aires, , Argentina

Site Status

Hospital Dr. José María Cullen

Santa Fe, , Argentina

Site Status

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

Nepean Hospital

Kingswood, New South Wales, Australia

Site Status

Saint Vincents Hospital

Sydney, New South Wales, Australia

Site Status

Macquarie University

Sydney, New South Wales, Australia

Site Status

Prince Charles Hospital

Chermside, Queensland, Australia

Site Status

Royal Hobart Hospital

Hobart, Tasmania, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Krankenhaus Elisabethinen Linz

Linz, Upper Austria, Austria

Site Status

Medizinische Universität Wien

Vienna, , Austria

Site Status

Hospital das Clinicas da Universidade Federal de Goias

Goiânia, Goiás, Brazil

Site Status

Hospital das Clínicas da Universidade Federal de Minas Gerais

Belo Horizonte, Minas Gerais, Brazil

Site Status

Hospital Madre Teresa

Belo Horizonte, Minas Gerais, Brazil

Site Status

Complexo Hospitalar Santa Casa de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital das Clínicas da Faculdade de Medicina de Botucatu- UNESP

Botucatu, São Paulo, Brazil

Site Status

Hospital da Clínicas da Faculdade de Medicina da Universidade de São Paulo

São Paulo, São Paulo, Brazil

Site Status

Escola Paulista de Medicina, Universidade Federal de São Paulo

São Paulo, São Paulo, Brazil

Site Status

Hospital Alemão Oswaldo Cruz

São Paulo, , Brazil

Site Status

Respiratory Research Foundation

Calgary, Alberta, Canada

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

Vancouver Coastal Health

Vancouver, British Columbia, Canada

Site Status

Lawson Health Research Institute

London, Ontario, Canada

Site Status

Centro de Investigaciones TASOL

Santiago, Santiago Metropolitan, Chile

Site Status

Clínica Tabancura

Vitacura, Santiago Metropolitan, Chile

Site Status

Beijing Chao-Yang Hospital

Beijing, Beijing Municipality, China

Site Status

Guangdong General Hospital

Guangzhou, Guangdong, China

Site Status

Wuhan Asia Heart Hospital

Wuhan, Hubei, China

Site Status

Xiangya Hospital

Changsha, Hunan, China

Site Status

The First Affiliated Hospital of Nanjing Medical University

Nanjing, Jiangsu, China

Site Status

The Second Affiliated Hospital of Nanchang Medical University

Nanchang, Jiangxi, China

Site Status

Zhongshan Hospital Fudan University

Shanghai, Shanghai Municipality, China

Site Status

Renji Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, Shanghai Municipality, China

Site Status

West China Hospital

Chengdu, Sichuan, China

Site Status

Peking Union Medical College Hospital

Beijing, , China

Site Status

Beijing Shijitan Hospital

Beijing, , China

Site Status

Chinese PLA General Hospital

Beijing, , China

Site Status

The Affiliated Hospital of Qingdao University

Qingdao, , China

Site Status

Renji Hospital of Shanghai Jiaotong University

Shanghai, , China

Site Status

Shanghai Pulmonary Hospital of Tongji University

Shanghai, , China

Site Status

Shenyang General Hospital of Shenyang Military Command

Shenyang, , China

Site Status

Aarhus Universitetshospital, Skejby

Aarhus, , Denmark

Site Status

Rigshospitalet-Copenhagen University Hospital

Copenhagen, , Denmark

Site Status

Hopital Haut-Leveque, CHU Bordeaux

Pessac, Aquitaine, France

Site Status

Hopital Jean Minjoz Centre Hospitalier Universitaire Besancon

Besançon, Franche-comte, France

Site Status

Centre Hospitalier Régional Universitaire de Lille - Hôpital Claude Huriez

Lille, Hauts-de-France, France

Site Status

CHU de Montpellier

Montpellier, Languedoc-roussillon, France

Site Status

Hopital Brabois

Vandœuvre-lès-Nancy, Limousin, Lorraine, France

Site Status

Centre Hospitalier Universitaire Hopital Nord

Marseille, Provence-Alpes-Côte d'Azur Region, France

Site Status

Thoraxklinik am Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Ludwig-Maximilians-Universitat Munchen

München, Bavaria, Germany

Site Status

Universitätsklinikum Regensburg

Regensburg, Bavaria, Germany

Site Status

Missionsarztliche Klinik Wurzburg gGmbH

Würzburg, Bavaria, Germany

Site Status

Universitätsmedizin Greifswald

Greifswald, Mecklenburg-Vorpommern, Germany

Site Status

Bergmannsheil Berufsgenossenschaftliche Universitätsklinik GmbH

Bochum, North Rhine-Westphalia, Germany

Site Status

Universitätsklinikum Köln

Cologne, North Rhine-Westphalia, Germany

Site Status

Herzzentrum Duisburg

Duisburg, North Rhine-Westphalia, Germany

Site Status

Universitätsmedizin der Johannes Gutenberg Universität

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitätsklinikum des Saarlandes

Homburg, Saarland, Germany

Site Status

Technische Universität Dresden

Dresden, Saxony, Germany

Site Status

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status

Universitätskrankenhaus Hamburg-Eppendorf

Hamburg, , Germany

Site Status

University General Hospital of Attikon

Athens, Attica, Greece

Site Status

General Hospital of Thessaloniki, "G.Papanikolaou"

Thessaloniki, Macedoni, Greece

Site Status

CARE Hospital

Hyderabad, Andhra Pradesh, India

Site Status

Mediciti Hospital

Hyderabad, Andhra Pradesh, India

Site Status

Care Institute Medical Sciences

Ahmedabad, Gujarat, India

Site Status

Apollo Hospitals International, Ltd.

Gandhinagar, Gujarat, India

Site Status

Medanta - The Medicity

Gurgaon, Haryana, India

Site Status

Narayana Institute of Cardiac Sciences

Bangalore, Karnataka, India

Site Status

KEM Hospital

Mumbai, Maharashtra, India

Site Status

King Edward Memorial Hospital & Seth Gordhandas Sunderdas Medical College

Mumbai, Maharashtra, India

Site Status

Ruby Hall Clinic

Pune, Maharashtra, India

Site Status

Sir Ganga Ram Hospital

New Delhi, National Capital Territory of Delhi, India

Site Status

Indraprastha Apollo Hospital

New Delhi, National Capital Territory of Delhi, India

Site Status

Apollo Hospital

Chennai, Tamil Nadu, India

Site Status

G. Kuppuswamy Naidu Memorial Hospital

Coimbatore, Tamil Nadu, India

Site Status

Rabin Medical Center

Petach Tikvah, Petah Tiqwa, Israel

Site Status

The Chaim Sheba Medical Center at Tel Hashomer

Tel Litwinsky, Tel Aviv, Israel

Site Status

Rambam Health Corp.

Haifa, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Hadassah Medical Center

Jerusalem, , Israel

Site Status

Azienda Ospedaliera Universitaria

Napoli, , Italy

Site Status

Istituto Mediterraneo Trapianti e Terapia Alta Specializzazione (ISMETT)

Palermo, , Italy

Site Status

Fondazione IRCCS Policlinico S. Matteo

Pavia, , Italy

Site Status

Azienda Policlinico Umberto I di Roma

Roma, , Italy

Site Status

Instituto Nacional de Cardiologia Ignacio Chavez

Tlalpan, Mexico City, Mexico

Site Status

Unidad de Investigacion Clinica en Medicina S.C.

Monterrey, Nuevo León, Mexico

Site Status

Universitair Medisch Centrum Sint Radboud

Nijmegen, Gelderland, Netherlands

Site Status

Vrije Universiteit Medisch Centrum

Amsterdam, North Holland, Netherlands

Site Status

Uniwersytecki Szpital Kliniczny w Bialymstoku

Bialystok, , Poland

Site Status

Szpital Kliniczny Przemienienia Panskiego Uniwersytetu Medycznego im K. Marcinkowskiego w Poznaniu

Krakow, , Poland

Site Status

Krakowski Szpital Specjalistyczny im. Jana Pawla II

Małogoskie, , Poland

Site Status

Europejskie Centrum Zdrowia Otwock, Szpital im. Fryderyka Chopina

Otwock, , Poland

Site Status

National University Hospital

Singapore, , Singapore

Site Status

National Heart Centre Singapore

Singapore, , Singapore

Site Status

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Sahlgrenska University Hospital

Gothenburg, Västra Götaland County, Sweden

Site Status

Karolinska University Hospital Solna

Stockholm, , Sweden

Site Status

National Cheng Kung University Hospital

Tainan City, Tainan CITY, Taiwan

Site Status

Veterans General Hospital-Kaohsiung

Kaohsiung City, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Papworth Hospital

Papworth Everard, Cambridgshire, United Kingdom

Site Status

Royal Free Hospital

London, England, United Kingdom

Site Status

Freeman Hospital

Newcastle upon Tyne, England, United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, England, United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Austria Brazil Canada Chile China Denmark France Germany Greece India Israel Italy Mexico Netherlands Poland Singapore South Korea Sweden Taiwan United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Grunig E, Rahaghi F, Elwing J, Vizza CD, Pepke-Zaba J, Shen J, Yao H, Hage A, Rosenkranz S, Vonk M, Balasubramanian V, Yuanhua Y, Yu Z, Lordan J, Cadaret L, Grover R, Ousmanou A, Seaman S, Deng C, Broderick M, White RJ; FREEDOM-EV Investigators. Oral Treprostinil is Associated with Improved Survival in FREEDOM-EV and its Open-Label Extension. Adv Ther. 2024 Feb;41(2):618-637. doi: 10.1007/s12325-023-02711-x. Epub 2023 Dec 6.

Reference Type DERIVED
PMID: 38055186 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Document Type: Informed Consent Form

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

TDE-PH-311

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.