An Open Label Extension Study to Evaluate Inhaled Treprostinil in Adult PH With ILD Including CPFE

NCT ID: NCT02633293

Last Updated: 2022-12-02

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

243 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-09-15

Study Completion Date

2021-08-01

Brief Summary

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This is a multicenter, open-label trial to evaluate the safety and efficacy of inhaled treprostinil in subjects with pre-capillary pulmonary hypertension (PH) associated with interstitial lung disease (ILD) including combined pulmonary fibrosis and emphysema (CPFE). The study will include about 266 patients who completed all required assessments in the RIN-PH-201 study at approximately 100 clinical trial centers. The study will continue Your participation in this study is voluntary and will last until you discontinue from the study or the study ends. The study will continue until each subject reaches the Week 108 visit or until inhaled treprostinil become commercially available for patients with PH associated with ILD including CPFE (whichever is sooner).

Detailed Description

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Conditions

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Pulmonary Hypertension Interstitial Lung Disease Combined Pulmonary Fibrosis and Emphysema

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Inhaled Treprostinil

Open-label access

Group Type EXPERIMENTAL

Inhaled Treprostinil

Intervention Type DRUG

Inhaled treprostinil up to 15 breaths (90 mcg) four times daily

Interventions

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Inhaled Treprostinil

Inhaled treprostinil up to 15 breaths (90 mcg) four times daily

Intervention Type DRUG

Other Intervention Names

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Tyvaso

Eligibility Criteria

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Inclusion Criteria

1. Subject voluntarily gives informed consent to participate in the study.
2. The subject participated in study RIN-PH-201, remained on study drug, was compliant with RIN-PH-201 study procedures or was enrolled in study RIN-PH-201 at the time that the study was discontinued by the sponsor.
3. Females of reproductive potential must be non-pregnant (as confirmed by a urine pregnancy test at Baseline) and non-lactating, and will:

* Either abstain from intercourse (when it is in line with their preferred and usual lifestyle), or
* Use two medically acceptable, highly-effective forms of contraception for the duration of study, and at least 30 days after discontinuing study drug.
4. Males must use a condom for the duration of treatment and for at least 48 hours after discontinuing study drug.

Exclusion Criteria

1. The subject is pregnant or lactating.
2. The subject was prematurely discontinued from study RIN-PH-201.
3. The subject developed a concurrent illness or condition during the conduct of RIN-PH-201 which, in the opinion of the Investigator, would represent a risk to overall health if they enrolled in this study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

IMC-Diagnostic & Medical Clinic

Mobile, Alabama, United States

Site Status

Arizona Pulmonary Specialists, Ltd.

Phoenix, Arizona, United States

Site Status

University of Arizona

Tucson, Arizona, United States

Site Status

Cedars-Sinai Medical Center

Beverly Hills, California, United States

Site Status

University of California, San Francisco-Fresno

Fresno, California, United States

Site Status

University of California San Diego

La Jolla, California, United States

Site Status

VA Long Beach Healthcare System

Long Beach, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Department of Veterans Affairs Greater Los Angeles Healthcare System

Los Angeles, California, United States

Site Status

Pacific Pulmonary Medical Group

Riverside, California, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

Kaiser Permanente

San Francisco, California, United States

Site Status

University of Colorado Hospital - Cardiac and Vascular Center

Aurora, Colorado, United States

Site Status

National Jewish Health

Denver, Colorado, United States

Site Status

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

MedStar Heart & Vascular Institute

Washington D.C., District of Columbia, United States

Site Status

Florida Lung, Asthma & Sleep Specialists, P.A.

Celebration, Florida, United States

Site Status

St. Francis Sleep, Allergy and Lung Institute

Clearwater, Florida, United States

Site Status

University of Florida Clinical Research Center

Gainesville, Florida, United States

Site Status

University of Florida College of Medicine, Jacksonville

Jacksonville, Florida, United States

Site Status

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status

St. Vincent's Lung, Sleep, and Critical Care Specialists

Jacksonville, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Florida Hospital

Orlando, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

The Emory Clinic

Atlanta, Georgia, United States

Site Status

Piedmont - Georgia Lung Associates

Austell, Georgia, United States

Site Status

Wellstar Medical Group

Marietta, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Illinois at Chicago Hospital

Chicago, Illinois, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Indiana University Hospital

Indianapolis, Indiana, United States

Site Status

Community Heart and Vascular Hospital

Indianapolis, Indiana, United States

Site Status

St. Vincent Medical Group, Inc.

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospitals & Clinics

Iowa City, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Louisville Physicians Outpatient Center

Louisville, Kentucky, United States

Site Status

Louisiana State University Health Sciences Center New Orleans

New Orleans, Louisiana, United States

Site Status

Maine Medical Center

South Portland, Maine, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Johns Hopkins University

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Spectrum Health Medical Center

Grand Rapids, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, United States

Site Status

Washington University Hospital

St Louis, Missouri, United States

Site Status

The University of New Mexico

Albuquerque, New Mexico, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

New York Methodist Hospital

Brooklyn, New York, United States

Site Status

Northwell Health

New Hyde Park, New York, United States

Site Status

NYU Langone Medical Center

New York, New York, United States

Site Status

The Mount Sinai Hospital

New York, New York, United States

Site Status

Weill Cornell Medical Center

New York, New York, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Pinehurst Medical Clinic, Inc.

Pinehurst, North Carolina, United States

Site Status

The Carl and Edyth Lindner Research Center at The Christ Hospital

Cincinnati, Ohio, United States

Site Status

University of Cincinnati Health

Cincinnati, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The Ohio State University Medical Center

Columbus, Ohio, United States

Site Status

Integris Baptist Medical Center

Oklahoma City, Oklahoma, United States

Site Status

Hospital of University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

AnMed Health Pulmonary and Sleep Medicine

Anderson, South Carolina, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Statcare Pulmonary Consultants

Knoxville, Tennessee, United States

Site Status

Baylor University Medical Center at Dallas

Dallas, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Texas Tech University Health Sciences Center

El Paso, Texas, United States

Site Status

Houston Methodist

Houston, Texas, United States

Site Status

Michael E. DeBakey VA Medical Center

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

University of Vermont, Vermont Lung Center

Colchester, Vermont, United States

Site Status

Inova Fairfax Hospital

Fairfax, Virginia, United States

Site Status

Sentara Cardiovascular Research Institute

Norfolk, Virginia, United States

Site Status

Pulmonary Associates of Richmond

Richmond, Virginia, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

University of Wisconsin School of Medicine and Public Health

Madison, Wisconsin, United States

Site Status

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Medical College of Wisconsin/Froedtert Hospital

Milwaukee, Wisconsin, United States

Site Status

Alliance Cardio Pulmonary Research Group, Inc.

Guaynabo, , Puerto Rico

Site Status

Countries

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United States Puerto Rico

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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RIN-PH-202

Identifier Type: -

Identifier Source: org_study_id

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