Open-label Extension of Oral Treprostinil in Subjects With PH Associated With HFpEF

NCT ID: NCT03043651

Last Updated: 2020-10-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-30

Study Completion Date

2020-03-02

Brief Summary

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This was an open-label study to evaluate the safety of continued therapy with oral treprostinil in subjects who completed Study TDE-HF-301. This study provided long-term, open-label data regarding the effect of continued long-term oral treprostinil therapy for the treatment of pulmonary hypertension (PH) associated with heart failure with preserved ejection fraction (HFpEF). Subject visits occurred at Baseline, Weeks 6, 12, 18, 24, and every 12 weeks thereafter until either oral treprostinil was commercially available to treat PH associated with HFpEF or the study was discontinued by the Sponsor.

The Sponsor terminated Studies TDE-HF-301 and TDE-HF-302 on 14 October 2019 due to slow enrollment. Safety data from the final subject in Study TDE-HF-302 were recorded on 02 March 2020. Due to the lower than expected number of subjects enrolled, the planned secondary efficacy-related endpoints were not analyzed.

Detailed Description

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Study TDE-HF-302 was a multicenter, open-label study in subjects participating and completing all required visits for Study TDE-HF-301. This study assessed the long-term safety of oral treprostinil in subjects with PH associated with HFpEF.

Subjects received oral treprostinil as 0.125-, 0.25-, 1-, and 2.5-mg sustained-release tablets. For subjects who were randomly allocated to receive oral treprostinil in Study TDE-HF-301, the initial dose of oral treprostinil was the same as the final dose in Study TDE-HF-301. Subjects randomly allocated to receive placebo in Study TDE-HF-301 were administered the initial dose of oral treprostinil at 0.125 mg 3 times daily (TID). Dose increases could occur in 0.125-mg increments every 72 hours at the discretion of the Investigator up to 6 mg TID, the maximum allowable dose determined by the Data Monitoring Committee during Study TDE-HF-301. Doses of study drug were to be increased in the absence of dose-limiting drug-related adverse events (AEs) to ensure that each subject received the optimal dose throughout the study. Subjects returned for visits at Weeks 6, 12, 18, and 24, and every 12 weeks thereafter. Subjects who terminated the study early were asked to return to the study center for a final evaluation.

Safety assessments consisted of AEs, clinical laboratory parameters, and clinical assessment of heart failure signs and symptoms.

Due to the lower than expected number of subjects enrolled, the planned secondary efficacy-related endpoints were not analyzed.

Conditions

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Pulmonary Hypertension Associated With HFpEF

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Oral treprostinil

Sustained-release tablets for TID administration

Group Type EXPERIMENTAL

Oral treprostinil

Intervention Type DRUG

Sustained-release oral tablets for TID administration

Interventions

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Oral treprostinil

Sustained-release oral tablets for TID administration

Intervention Type DRUG

Other Intervention Names

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Treprostinil diethanolamine, Treprostinil diolamine

Eligibility Criteria

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Inclusion Criteria

1\. The subject participated in Study TDE-HF-301, remained on study drug, was compliant with study procedures and assessments during Study TDE-HF-301, and completed through Week 24 of that study.

Exclusion Criteria

1. The subject was pregnant or lactating.
2. The subject was prematurely discontinued from Study TDE-HF-301 for any reason.
3. The subject developed a concurrent illness or condition during Study TDE-HF-301, which, in the opinion of the Investigator, represented a risk to the subject's overall health if they enrolled in this study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mardi Gomberg-Maitland, MD

Role: PRINCIPAL_INVESTIGATOR

George Washington University

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Banner University Medical Center Phoenix

Phoenix, Arizona, United States

Site Status

University of Arizona

Tucson, Arizona, United States

Site Status

VA Healthcare System of Greater Los Angeles

Los Angeles, California, United States

Site Status

University of California Los Angeles Pulmonary Division

Los Angeles, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

University of California - Davis Medical Center

Sacramento, California, United States

Site Status

Santa Barbara Cottage Hospital

Santa Barbara, California, United States

Site Status

Aurora Denver Cardiology Associates

Aurora, Colorado, United States

Site Status

University of Colorado Denver

Aurora, Colorado, United States

Site Status

National Jewish Health

Denver, Colorado, United States

Site Status

South Denver Cardiology

Littleton, Colorado, United States

Site Status

Cleveland Clinic of Florida

Weston, Florida, United States

Site Status

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Medical Faculty Associates, George Washington University

Washington D.C., District of Columbia, United States

Site Status

Bay Area Cardiology Associates

Brandon, Florida, United States

Site Status

Mayo Clinic - Jacksonville

Jacksonville, Florida, United States

Site Status

St. Vincent's Lung, Sleep, and Critical Care Specialists

Jacksonville, Florida, United States

Site Status

Central Florida Pulmonary Group, P.A.

Orlando, Florida, United States

Site Status

Florida Hospital

Orlando, Florida, United States

Site Status

University of South Florida ; Tampa General Hospital

Tampa, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

Augusta University

Augusta, Georgia, United States

Site Status

Piedmont Physicians Georgia Lung

Austell, Georgia, United States

Site Status

WellStar Medical Group

Marietta, Georgia, United States

Site Status

University of Illinois at Chicago Hospital

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Advocate Christ Medical Center

Oak Lawn, Illinois, United States

Site Status

OSF HealthCare

Peoria, Illinois, United States

Site Status

Indiana University Health Methodist Research Institute, INC

Indianapolis, Indiana, United States

Site Status

Community Heart and Vascular Hospital

Indianapolis, Indiana, United States

Site Status

Saint Vincent Hospital and Health Services

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

Iowa Heart Center

West Des Moines, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Kentucky Medical Center

Lexington, Kentucky, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

University of Louisville Physicians Outpatient Center

Louisville, Kentucky, United States

Site Status

Chest Medicine Associates

South Portland, Maine, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

St. Elizabeth's Medical Center

Brighton, Massachusetts, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Spectrum Health Medical Group

Grand Rapids, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

St. Luke's Hospital

Chesterfield, Missouri, United States

Site Status

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Barnabas Health Lung Center

Newark, New Jersey, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Pulmonary Health Physicians, PC

Syracuse, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Asheville Cardiology Associates

Asheville, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Pinehurst Medical Clinic

Pinehurst, North Carolina, United States

Site Status

The Lindner Research Center The Christ Hospital Health Network

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Site Status

University of Toldedo Medical Center

Toledo, Ohio, United States

Site Status

The Oregon Clinic

Portland, Oregon, United States

Site Status

Lancaster General Hospital

Lancaster, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

AnMed Health Pulmonary and Sleep Medicine

Anderson, South Carolina, United States

Site Status

VitaLink Research - Anderson

Anderson, South Carolina, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Stern Cardiovascular Foundation

Germantown, Tennessee, United States

Site Status

Summit Medical Group

Knoxville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

Houston Methodist Research Institute

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

Texas Tech University Health Sciences Center

Lubbock, Texas, United States

Site Status

Intermountain Medical Center

Murray, Utah, United States

Site Status

Inova Heart and Vascular Institute

Falls Church, Virginia, United States

Site Status

Sentara Cardiovascular Research Institute

Norfolk, Virginia, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Carilion Clinic

Roanoke, Virginia, United States

Site Status

Providence Medical Research Center

Spokane, Washington, United States

Site Status

West Virginia University Hospital

Morgantown, West Virginia, United States

Site Status

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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TDE-HF-302

Identifier Type: -

Identifier Source: org_study_id

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