FREEDOM - M: Oral Treprostinil as Monotherapy for the Treatment of Pulmonary Arterial Hypertension (PAH)

NCT ID: NCT00325403

Last Updated: 2024-01-03

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

349 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-10-31

Study Completion Date

2011-04-30

Brief Summary

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This study was an international, multicenter, randomized (2:1 active:placebo), double-blind, placebo-controlled study in subjects with PAH who were NOT currently receiving approved therapy for their PAH. Study visits occurred at 4 week intervals for 12 weeks (with an additional visit at Week 11) with the key measure of efficacy being the 6-minute walk test. Study procedures included routine blood tests, medical history, physical exams, disease evaluation, and exercise tests. Two optional substudies were also a part of FREEDOM-M at select centers - a hemodynamic substudy with a right heart catheterization at Baseline and Week 12 and a genetics and biomarkers substudy with blood samples collected at Baseline and Week 12.

Patients who completed all assessments for 12 weeks were also eligible to enter an open-label, extension phase study (FREEDOM - EXT).

Detailed Description

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Conditions

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Pulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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UT-15C (oral treprositnil)

Subjects receive UT-15C (oral treprostinil) twice daily.

Group Type ACTIVE_COMPARATOR

Oral treprostinil (UT-15C) Sustained Release Tablets

Intervention Type DRUG

Sustained release oral tablet, twice daily

Placebo

Subjects receive placebo (sugar pill) twice daily.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo oral tablet twice daily

Interventions

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Oral treprostinil (UT-15C) Sustained Release Tablets

Sustained release oral tablet, twice daily

Intervention Type DRUG

Placebo

Placebo oral tablet twice daily

Intervention Type OTHER

Other Intervention Names

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treprostinil diethanolamine

Eligibility Criteria

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Inclusion Criteria

* Between 12 and 75 years of age, inclusive.
* Body weight at least 40 kg with a Body Mass Index \< 45
* PAH that is either idiopathic/heritable; associated with repaired congenital systemic-to-pulmonary shunts (repaired ≥ 5 years); associated with collagen vascular disease; associated with HIV.
* Previous testing (e.g., right heart catheterization, echocardiography) consistent with the diagnosis of PAH.
* Baseline 6-minute walk distance between 200 and 425 meters, inclusive.
* Reliable and cooperative with protocol requirements.

* History of uncontrolled sleep apnea, renal insufficiency, anemia, left sided heart disease, uncontrolled systemic hypertension, or parenchymal lung disease.
* Use of an investigational drug within 30 days of Baseline.

Exclusion Criteria

* Nursing or pregnant.
* Currently receiving an endothelin receptor antagonist, a phosphodiesterase-5 inhibitor, or prostacyclin within 30 days of Baseline.
Minimum Eligible Age

12 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kevin Laliberte, PharmD

Role: STUDY_DIRECTOR

United Therapeutics

Locations

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University of Alabama-Birmingham

Birmingham, Alabama, United States

Site Status

Arizona Pulmonary Specialist

Phoenix, Arizona, United States

Site Status

Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status

University of California, San Francisco-Fresno

Fresno, California, United States

Site Status

West Los Angeles VA Healthcare Center

Los Angeles, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

Harbor-UCLA Medical Center

Torrance, California, United States

Site Status

University of Colorado Health Science Center

Aurora, Colorado, United States

Site Status

University of Florida - Shands Hospital

Jacksonville, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

University of Chicago Hospitals

Chicago, Illinois, United States

Site Status

University of Iowa Hospital and Clinics

Iowa City, Iowa, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

Alexandria Cardiology Clinic

Alexandria, Louisiana, United States

Site Status

Maine Medical Center

Portland, Maine, United States

Site Status

University of Maryland School of Medicine

Baltimore, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Washington University Hospital

St Louis, Missouri, United States

Site Status

Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Newark Beth Israel Medical Center

Newark, New Jersey, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Columbia Presbyterian Medical Center

New York, New York, United States

Site Status

Mary M Parkes Center for Asthma, Allergy and Pulmonary Care - University of Rochester

Rochester, New York, United States

Site Status

The Lindner Center

Cincinnati, Ohio, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

University Hospitals of Cleveland

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Legacy Clinic Northwest

Portland, Oregon, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

University of Texas Southwestern

Dallas, Texas, United States

Site Status

Baylor College of Medicine, Pulmonary & Critical Care

Houston, Texas, United States

Site Status

University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Inova Fairfax Hospital

Falls Church, Virginia, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Heart Care Associates

Milwaukee, Wisconsin, United States

Site Status

Universitaet Wien

Vienna, , Austria

Site Status

Hospital Erasme

Brussels, , Belgium

Site Status

University Hospital Gasthuisberg

Leuven, , Belgium

Site Status

Peter Lougheed Centre

Calgary, Alberta, Canada

Site Status

London Health Science Centre

London, Ontario, Canada

Site Status

SMBD Jewish General Hospital

Montreal, Quebec, Canada

Site Status

Beijing Shijitan Hospital

Beijing, , China

Site Status

Peking Union Medical College Hospital

Beijing, , China

Site Status

Shanghai Pulmonary Hospital

Shanghai, , China

Site Status

Hospital Antoine Beclere

Clamart, , France

Site Status

PRIME Hospitals

Hyderbad, Andhra Pradesh, India

Site Status

Care Institute of Medical Science

Ahmedabad, Gujarat, India

Site Status

Lifecare Institute of Medical Sciences & Research

Ahmedabad, Gujarat, India

Site Status

Narayana Hrudayalaya Institute of Medical Sciences

Bangalore, Karnataka, India

Site Status

Asian Heart Institute and Research Centre

Parel Mumbai, Maharashtra, India

Site Status

Poona Hospital and Research Centre

Pune, Maharashtra, India

Site Status

Sri Ramachandra Medical College

Chennai, Tamil Nadu, India

Site Status

G. Kuppuswamy Naidu Memorial Hospital

Coimbatore, Tamil Nadu, India

Site Status

K. S. Hospital

Chennai, Tamil Nadu, , India

Site Status

Sir Ganga Ram Hospital

New Delhi, , India

Site Status

Ruby Hall Clinic

Pune, , India

Site Status

Care Hospital

Visakhapatnam, Andra Pradesh, , India

Site Status

Hadassah Ein-Kerem Medical Center

Jerusalem, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

Tel Hashomer Medical Center

Ramat Gan, , Israel

Site Status

Universita degli Studi Bologna

Bologna, , Italy

Site Status

Instituto Nacional de Cardiologia

Mexico City, Mexico City, Mexico

Site Status

Hospital Universitario UANL

Monterrey, Nuevo León, Mexico

Site Status

Unidad de Investigacion Clinica en Medicina (UDICEM)

Monterrey, , Mexico

Site Status

VU Medisch Centrum (VUCM)

Amsterdam, , Netherlands

Site Status

Krakowski Szpital Specjalistyczny im. (Kraków Specialist Hospital)

Krakow, , Poland

Site Status

National Tuberculosis and Lung Disease Research Institute

Warsaw, , Poland

Site Status

Wojewódzki Szpital Specjalistyczny we Wroclawiu (Provincial Specialist Hospital in Wrocław)

Wroclaw, , Poland

Site Status

Auxilio Mutuo Hospital

Guaynabo, , Puerto Rico

Site Status

Countries

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United States Austria Belgium Canada China France India Israel Italy Mexico Netherlands Poland Puerto Rico

References

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Jing ZC, Parikh K, Pulido T, Jerjes-Sanchez C, White RJ, Allen R, Torbicki A, Xu KF, Yehle D, Laliberte K, Arneson C, Rubin LJ. Efficacy and safety of oral treprostinil monotherapy for the treatment of pulmonary arterial hypertension: a randomized, controlled trial. Circulation. 2013 Feb 5;127(5):624-33. doi: 10.1161/CIRCULATIONAHA.112.124388. Epub 2013 Jan 10.

Reference Type DERIVED
PMID: 23307827 (View on PubMed)

Related Links

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http://www.pahstudy.com

FREEDOM Studies Website

Other Identifiers

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TDE-PH-302

Identifier Type: -

Identifier Source: org_study_id

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