FREEDOM-C: Oral Treprostinil in Combination With an Endothelin Receptor Antagonist (ERA) and/or a Phosphodiesterase-5 (PDE-5) Inhibitor for the Treatment of Pulmonary Arterial Hypertension (PAH)

NCT ID: NCT00325442

Last Updated: 2017-08-02

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

354 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-10-31

Study Completion Date

2010-12-31

Brief Summary

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This study was an international, multi-center, randomized, double-blind, placebo-controlled study in subjects with PAH who were currently receiving approved therapy for their PAH (i.e., endothelin receptor antagonist and/or phosphodiesterase-5 inhibitor). Study visits occurred at 4 week intervals for 16 weeks; the key measure of efficacy was the 6-minute walk test. Study procedures included routine blood tests, medical history, physical exams, disease evaluation, and exercise tests. One optional substudy was also a part of FREEDOM-C at select centers - a hemodynamic substudy with a right heart catheterization at Baseline and Week 16.

Patients who completed all assessments for 16-weeks were also eligible to enter an open-label, extension phase study (FREEDOM - EXT).

Detailed Description

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Conditions

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Pulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Active

Subjects assigned to active therapy with UT-15C 0.25, 0.5, 1, or 5 mg oral tablets.

Group Type ACTIVE_COMPARATOR

Oral treprostinil (UT-15C) sustained release tablets

Intervention Type DRUG

UT-15C 0.25, 0.5, 1, or 5 mg oral tablets by mouth every 12 hours

Placebo Arm

Subjects assigned to placebo 0.25, 0.5, 1, or 5 mg oral tablets.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo 0.25, 0.5, 1, or 5 mg oral tablets by mouth every 12 hours

Interventions

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Oral treprostinil (UT-15C) sustained release tablets

UT-15C 0.25, 0.5, 1, or 5 mg oral tablets by mouth every 12 hours

Intervention Type DRUG

Placebo

Placebo 0.25, 0.5, 1, or 5 mg oral tablets by mouth every 12 hours

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Between 12 and 70 years of age, inclusive.
* Body weight at least 45 kg (approximately 100 pounds).
* PAH that is either idiopathic/heritable (including PAH associated with appetite suppressant/toxin use); PAH associated with repaired congenital systemic-to-pulmonary shunts (repaired ≥ 5 years); PAH associated with collagen vascular disease; or PAH associated with HIV.
* Baseline 6-minute walk distance between 150 and 450 meters, inclusive.
* Currently receiving an approved endothelin receptor antagonist and/or an approved phosphodiesterase-5 inhibitor for at least 90 days and on a stable dose for at least the last 30 days.
* Previous testing (e.g., right heart catheterization, echocardiography) consistent with the diagnosis of PAH.
* Reliable and cooperative with protocol requirements.

* History of uncontrolled sleep apnea, renal insufficiency, anemia, left sided heart disease, uncontrolled systemic hypertension, or parenchymal lung disease.
* Use of an investigational drug within 30 days of Baseline.

Exclusion Criteria

* Nursing or pregnant.
* Received a prostacyclin within the past 30 days.
Minimum Eligible Age

12 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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United Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama-Birmingham

Birmingham, Alabama, United States

Site Status

Arizona Pulmonary Specialist

Phoenix, Arizona, United States

Site Status

University of Arizona Health Science Center

Tucson, Arizona, United States

Site Status

West Los Angeles VA Healthcare Center

Los Angeles, California, United States

Site Status

Stanford University, Pulmonary and Critical Care

Palo Alto, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

University of California-San Francisco

San Francisco, California, United States

Site Status

Harbour-UCLA Medical Center

Torrance, California, United States

Site Status

The Children's Hospital

Aurora, Colorado, United States

Site Status

Pulmonary Hypertension Clinic

Aurora, Colorado, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

University of Iowa Health Care

Iowa City, Iowa, United States

Site Status

Maine Medical Center

Portland, Maine, United States

Site Status

University of Maryland School of Medicine

Baltimore, Maryland, United States

Site Status

John's Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Washington University Hospital

St Louis, Missouri, United States

Site Status

Columbia Presbyterian Medical Center

New York, New York, United States

Site Status

Mary M Parkes Center for Asthma, Allergy and Pulmonary Care

Rochester, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

University Hospitals of Cleveland

Cleveland, Ohio, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Legacy Clinic Northwest

Portland, Oregon, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

UT Southwestern

Dallas, Texas, United States

Site Status

Baylor College of Medicine, Pulmonary & Critical Care

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Intermountain Medical Center

Murray, Utah, United States

Site Status

Inova Transplant Center

Fairfax, Virginia, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Heart Care Associates

Milwaukee, Wisconsin, United States

Site Status

St. Vincent's Hospital

Sydney, New South Wales, Australia

Site Status

The Prince Charles Hospital

Brisbane, , Australia

Site Status

The Alfred Hospital

Melbourne, , Australia

Site Status

Royal Perth Hospital

Perth, , Australia

Site Status

Medizinische Universität Innsbruck

Innsbruck, , Austria

Site Status

Universitaet Wien

Vienna, , Austria

Site Status

Hospital Erasme

Brussels, , Belgium

Site Status

University Hospital Gasthuisberg

Leuven, , Belgium

Site Status

Respiratory Research

Calgary, Alberta, Canada

Site Status

Vancouver Coastal Health Respiratory Clinic

Vancouver, British Columbia, Canada

Site Status

Lab London Health Sciences Center

London, Ontario, Canada

Site Status

Toronto General Hospital

Toronto, Ontario, Canada

Site Status

SMBD Jewish General Hospital

Montreal, Quebec, Canada

Site Status

Hospital Cavale Blanche

Brest, , France

Site Status

Hospital Antoine Beclere

Clamart, , France

Site Status

Hospital Claude Huriez

Lille, , France

Site Status

Hôpital Louis Pradel

Lyon, , France

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Mater Misericordiae University Hospital Ltd

Dublin, , Ireland

Site Status

Hadassah Ein-Kerem Medical Center

Jerusalem, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

Tel Hashomer Medical Center

Ramat Gan, , Israel

Site Status

Universita degli Studi Bologna

Bologna, , Italy

Site Status

Universita "La Sapienza" Roma

Rome, , Italy

Site Status

Hospital Vrije Universiteit

Amsterdam, , Netherlands

Site Status

National Tuberculosis and Lung Disease Research Institute

Warsaw, , Poland

Site Status

Hospital Clinic of Barcelona

Barcelona, , Spain

Site Status

Hospital Valle Hebron

Barcelona, , Spain

Site Status

Hospital 12 de Octubre

Madrid, , Spain

Site Status

Papworth Hospital

Cambridge, , United Kingdom

Site Status

Western Infirmary

Glasgow, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Freeman Hospital

Newcastle, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada France Germany Ireland Israel Italy Netherlands Poland Spain United Kingdom

References

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Tapson VF, Torres F, Kermeen F, Keogh AM, Allen RP, Frantz RP, Badesch DB, Frost AE, Shapiro SM, Laliberte K, Sigman J, Arneson C, Galie N. Oral treprostinil for the treatment of pulmonary arterial hypertension in patients on background endothelin receptor antagonist and/or phosphodiesterase type 5 inhibitor therapy (the FREEDOM-C study): a randomized controlled trial. Chest. 2012 Dec;142(6):1383-1390. doi: 10.1378/chest.11-2212.

Reference Type DERIVED
PMID: 22628490 (View on PubMed)

Other Identifiers

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TDE-PH-301

Identifier Type: -

Identifier Source: org_study_id

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