A Study of Tocilizumab (RoActemra/Actemra) in Patients With Ankylosing Spondylitis Who Have Had an Inadequate Response to Previous Tumor Necrosis Factor (TNF) Antagonist Therapy

NCT ID: NCT01209689

Last Updated: 2013-01-17

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

113 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-10-31

Study Completion Date

2011-12-31

Brief Summary

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This randomized, double-blind, placebo-controlled study evaluated the safety and efficacy of tocilizumab (RoActemra/Actemra) in patients with ankylosing spondylitis (AS) who had an inadequate response to previous tumor necrosis factor (TNF) antagonist therapy. Patients were randomized to receive tocilizumab at a dose of either 8 mg/kg or 4 mg/kg intravenously (iv) or placebo every 4 weeks for 24 weeks. The double-blind treatment period was followed by open-label treatment with tocilizumab 8 mg/kg iv every 4 weeks until Week 104 for all patients.

This study and all further clinical development of tocilizumab AS was halted after a review of 12-week data from Study NA22823, a randomized double-blind, placebo-controlled study in TNF antagonist naïve AS patients, failed to demonstrate efficacy.

Detailed Description

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Conditions

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Spondylitis, Ankylosing

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Tocilizumab 4 mg/kg

Patients received tocilizumab 4 mg/kg intravenously every 4 weeks for 24 weeks.

Group Type EXPERIMENTAL

Tocilizumab

Intervention Type DRUG

Tocilizumab 8 mg/kg

Patients received tocilizumab 8 mg/kg intravenously every 4 weeks for 24 weeks.

Group Type EXPERIMENTAL

Tocilizumab

Intervention Type DRUG

Placebo

Patients received placebo to tocilizumab intravenously every 4 weeks for 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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Tocilizumab

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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RoActemra Actemra

Eligibility Criteria

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Inclusion Criteria

* Adult patients ≥ 18 years of age.
* Ankylosing spondylitis as defined by the modified New York criteria for ≥ 3 months prior to baseline.
* Active disease at screening and baseline (Bath Ankylosing Spondylitis Disease Activity Index \[BASDAI\] ≥ 4.0, spinal pain visual analog scale \[VAS\] ≥ 40).
* Inadequate response or intolerant to 1 or more previous non-steroidal anti-inflammatory drugs (NSAIDs).
* Inadequate response to treatment with etanercept, infliximab, adalimumab, or golimumab because of inadequate efficacy.
* Tumor necrosis factor (TNF) antagonist therapy must have been discontinued at least 8 weeks prior to baseline (etanercept 4 weeks).
* Traditional disease-modifying anti-rheumatic drugs (DMARDs) must be withdrawn for at least 4 weeks prior to baseline (methotrexate, sulfasalazine, and hydroxychloroquine or chloroquine may be allowed if at stable dose for at least 4 weeks prior to baseline).
* Oral corticosteroids (≥ 10 mg/day prednisone or equivalent) and NSAIDs/cyclooxygenase-2 \[COX-2\] inhibitors must be at stable dose for at least 4 weeks prior to baseline.

Exclusion Criteria

* Major surgery (including joint surgery) within 8 weeks prior to screening or planned major surgery within 6 months after randomization.
* Total ankylosis of spine (as determined by investigator).
* Inflammatory rheumatic disease other than ankylosing spondylitis.
* Active, acute uveitis at baseline.
* Previous treatment with tocilizumab.
* Intra-articular or tendon injections or parenteral corticosteroids within 4 weeks prior to screening.
* History of severe allergic or anaphylactic reactions to humanized or murine monoclonal antibodies.
* Active current or history of recurrent bacterial, viral, fungal, mycobacterial, or other infection.
* History of or currently active primary or secondary immunodeficiency.
* Body weight \> 150 kg.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Huntington Beach, California, United States

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Aventura, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Decatur, Georgia, United States

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Marietta, Georgia, United States

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Idaho Falls, Idaho, United States

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Wichita, Kansas, United States

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Hagerstown, Maryland, United States

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Saint Claire Shores, Michigan, United States

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Freehold, New Jersey, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Greensboro, North Carolina, United States

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Duncansville, Pennsylvania, United States

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Austin, Texas, United States

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Houston, Texas, United States

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Heidelberg, , Australia

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Hobart, , Australia

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Sydney, , Australia

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Woodville, , Australia

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Brussels, , Belgium

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Ghent, , Belgium

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Kortrijk, , Belgium

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Liège, , Belgium

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Yvoir, , Belgium

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Cuiabá, , Brazil

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Goiânia, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Plovdiv, , Bulgaria

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Calgary, Alberta, Canada

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Hamilton, Ontario, Canada

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Kitchener, Ontario, Canada

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Mississauga, Ontario, Canada

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St. Catharines, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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St. John's, , Canada

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Bruntál, , Czechia

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Hlučín, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Uherské Hradiště, , Czechia

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Zlín, , Czechia

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Esbjerg, , Denmark

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Hellerup, , Denmark

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Vejle, , Denmark

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Besançon, , France

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Bordeaux, , France

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Boulogne-Billancourt, , France

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Créteil, , France

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Grenoble, , France

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Le Kremlin-Bicêtre, , France

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Lyon, , France

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Montpellier, , France

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Orléans, , France

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Paris, , France

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Paris, , France

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Rouen, , France

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Strasbourg, , France

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Vandœuvre-lès-Nancy, , France

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Berlin, , Germany

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Berlin, , Germany

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Cologne, , Germany

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Erlangen, , Germany

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Frankfurt, , Germany

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Gommern, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Herne, , Germany

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München, , Germany

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Regensburg, , Germany

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Rostock, , Germany

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Tübingen, , Germany

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Würzburg, , Germany

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Bangalore, , India

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Bangalore, , India

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Jaipur, , India

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New Delhi, , India

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Secunderabad, , India

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Ferrara, , Italy

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Florence, , Italy

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Monserrato, , Italy

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Padua, , Italy

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Pisa, , Italy

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Prato, , Italy

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Reggio Emilia, , Italy

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Roma, , Italy

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Siena, , Italy

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Bydgoszcz, , Poland

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Krakow, , Poland

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Lublin, , Poland

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Poznan, , Poland

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Torun, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Košice, , Slovakia

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Piešťany, , Slovakia

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Cape Town, , South Africa

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Cape Town, , South Africa

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Durban, , South Africa

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Pinelands, , South Africa

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Pretoria, , South Africa

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Stellenbosch, , South Africa

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A Coruña, , Spain

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Alcorcón, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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Lugo, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Oviedo, , Spain

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Oviedo, , Spain

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Sabadell, , Spain

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Basingstoke, , United Kingdom

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Bath, , United Kingdom

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Greenock, , United Kingdom

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Leeds, , United Kingdom

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London, , United Kingdom

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Salford, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Wigan, , United Kingdom

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Countries

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United States Australia Belgium Brazil Bulgaria Canada Czechia Denmark France Germany India Italy Lithuania Netherlands Poland Slovakia South Africa Spain United Kingdom

References

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Sieper J, Porter-Brown B, Thompson L, Harari O, Dougados M. Assessment of short-term symptomatic efficacy of tocilizumab in ankylosing spondylitis: results of randomised, placebo-controlled trials. Ann Rheum Dis. 2014 Jan;73(1):95-100. doi: 10.1136/annrheumdis-2013-203559. Epub 2013 Jun 13.

Reference Type DERIVED
PMID: 23765873 (View on PubMed)

Other Identifiers

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2009-017488-40

Identifier Type: -

Identifier Source: secondary_id

WA22908

Identifier Type: -

Identifier Source: org_study_id

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