A Study Of Tocilizumab in Patients With Moderate to Severe Active Rheumatoid Arthritis Who Have an Inadequate Response to or Are Unable to Tolerate Biologic and Non-Biologic Disease-modifying Antirheumatic Drugs (DMARDs)

NCT ID: NCT00891020

Last Updated: 2012-10-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

886 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-05-31

Study Completion Date

2011-03-31

Brief Summary

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This 3 arm randomized open label study will evaluate the safety, tolerability and efficacy of tocilizumab in patients with moderate to severe active rheumatoid arthritis, who have had inadequate response to or are unable to tolerate DMARDs. The protocol incorporates risk mitigation strategies developed in partnership with the FDA to manage known and potential risks associated with the treatment of tocilizumab. Patients will be randomized to receive tocilizumab either 4 mg/kg intravenous (iv) or 8 mg/kg iv with concomitant non-biologic DMARDs, or 8 mg/kg iv without concomitant non-biologic DMARDs, every 4 weeks, for a total of 6 infusions. The anticipated time on study treatment is 3-12 months, and the target sample size is 500-1000 individuals.

Detailed Description

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Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Tocilizumab 8 mg/kg Monotherapy

Participants received Tocilizumab 8 mg/kg as a 60 minute intravenous infusion every 4 weeks for a total of 6 infusions for 24 weeks. Participants who completed the 24 week treatment period were offered the option of entering a long-term extension phase at the investigator's discretion.

Group Type EXPERIMENTAL

tocilizumab [RoActemra/Actemra]

Intervention Type DRUG

8 mg/kg intravenous every 4 weeks for 24 weeks

Tocilizumab 4 mg/kg + DMARD

Participants received Tocilizumab (TCZ) 4 mg/kg as a 60 minute intravenous infusion every 4 weeks for a total of 6 infusions plus non-biologic disease-modifying antirheumatic drug (DMARD) of the investigator's choice for 24 weeks. Participants not achieving a 20% improvement from baseline in tender and swollen joint counts at Week 8 were to have their dosage increased to 8 mg/kg, per protocol. Beginning at Week 12 dosage increase to 8 mg/kg was at the discretion of the investigator. Participants who completed the 24 week treatment period were offered the option of entering a long-term extension phase at the investigator's discretion.

Group Type EXPERIMENTAL

tocilizumab [RoActemra/Actemra]

Intervention Type DRUG

8 mg/kg intravenous every 4 weeks for 24 weeks

tocilizumab [RoActemra/Actemra]

Intervention Type DRUG

4 mg/kg every 4 weeks for 24 weeks

Nonbiologic DMARDs of investigator's choice

Intervention Type DRUG

Nonbiologic disease-modifying antirheumatic drugs (DMARDs) As prescribed

Tocilizumab 8 mg/kg + DMARD

Participants received Tocilizumab (TCZ) 8 mg/kg as a 60 minute intravenous infusion every 4 weeks for a total of 6 infusions plus non-biologic disease-modifying antirheumatic drug (DMARD) of the investigator's choice for 24 weeks. Participants who completed the 24 week treatment period were offered the option of entering a long-term extension phase at the investigator's discretion.

Group Type EXPERIMENTAL

tocilizumab [RoActemra/Actemra]

Intervention Type DRUG

8 mg/kg intravenous every 4 weeks for 24 weeks

Nonbiologic DMARDs of investigator's choice

Intervention Type DRUG

Nonbiologic disease-modifying antirheumatic drugs (DMARDs) As prescribed

Interventions

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tocilizumab [RoActemra/Actemra]

8 mg/kg intravenous every 4 weeks for 24 weeks

Intervention Type DRUG

tocilizumab [RoActemra/Actemra]

4 mg/kg every 4 weeks for 24 weeks

Intervention Type DRUG

Nonbiologic DMARDs of investigator's choice

Nonbiologic disease-modifying antirheumatic drugs (DMARDs) As prescribed

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* adult patients, \>=18 years of age;
* moderate to severe active rheumatoid arthritis for \>6 months;
* inadequate clinical response or unable to tolerate current or prior biologic or non-biologic Disease-modifying antirheumatic drug (DMARD) therapy;
* Swollen joint count (SJC) \>/=4 and Tender joint count (TJC) \>/=4
* body weight \</=150kg
* current permitted non-biologic DMARDs must be on stable dose for \>/= 7 weeks prior to baseline;

Exclusion Criteria

* history of autoimmune disease or inflammatory joint disease other than rheumatoid arthritis;
* functional class IV as defined by the American College of Rheumatology (ACR) Classification of Functional Status in rheumatoid arthritis;
* treatment with rituximab within 6 months before screening;
* intraarticular corticosteroids within 8 weeks or intramuscular (im)/ intravenous (iv) corticosteroids within 12 weeks prior to screening;
* known active current or history of recurrent infections, or any major episode of infection requiring hospitalization or treatment with iv antibiotics within 4 weeks of screening, or oral antibiotics within 2 weeks prior to screening.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Anniston, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Huntsville, Alabama, United States

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Mobile, Alabama, United States

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Montgomery, Alabama, United States

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Tuscaloosa, Alabama, United States

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Hot Springs, Arizona, United States

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Paradise Valley, Arizona, United States

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Peoria, Arizona, United States

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Scottsdale, Arizona, United States

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Scottsdale, Arizona, United States

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Tucson, Arizona, United States

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Fayetteville, Arkansas, United States

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Fort Smith, Arkansas, United States

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Jonesboro, Arkansas, United States

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Little Rock, Arkansas, United States

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Covina, California, United States

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Escondido, California, United States

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Fullerton, California, United States

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Huntington Beach, California, United States

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La Jolla, California, United States

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Lakewood, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Murrieta, California, United States

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Newport Beach, California, United States

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Pasadena, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Leandro, California, United States

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Santa Barbara, California, United States

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Santa Maria, California, United States

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Sherman Oaks, California, United States

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Van Nuys, California, United States

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Victorville, California, United States

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Westlake Village, California, United States

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Whittier, California, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Bridgeport, Connecticut, United States

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Danbury, Connecticut, United States

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Hamden, Connecticut, United States

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Trumbull, Connecticut, United States

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Lewes, Delaware, United States

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Aventura, Florida, United States

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Boca Raton, Florida, United States

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Clearwater, Florida, United States

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Dunedin, Florida, United States

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Fort Lauderdale, Florida, United States

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Gainesville, Florida, United States

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Gainesville, Florida, United States

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Jacksonville, Florida, United States

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Lake Mary, Florida, United States

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Melbourne, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Naples, Florida, United States

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Ocala, Florida, United States

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Orlando, Florida, United States

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Palm Harbor, Florida, United States

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Sarasota, Florida, United States

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South Miami, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Gainesville, Georgia, United States

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Boise, Idaho, United States

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Idaho Falls, Idaho, United States

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Nampa, Idaho, United States

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Chicago, Illinois, United States

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Maywood, Illinois, United States

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Moline, Illinois, United States

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Morton Grove, Illinois, United States

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Peoria, Illinois, United States

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Schaumburg, Illinois, United States

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Springfield, Illinois, United States

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Vernon Hills, Illinois, United States

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Evansville, Indiana, United States

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Fort Wayne, Indiana, United States

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South Bend, Indiana, United States

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Cedar Rapids, Iowa, United States

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Lees Summit, Kansas, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Baton Rouge, Louisiana, United States

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Monroe, Louisiana, United States

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New Orleans, Louisiana, United States

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Columbia, Maryland, United States

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Ellicott City, Maryland, United States

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Frederick, Maryland, United States

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Wheaton, Maryland, United States

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Boston, Massachusetts, United States

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Fall River, Massachusetts, United States

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Pascagoula, Massachusetts, United States

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Peabody, Massachusetts, United States

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Plymouth, Massachusetts, United States

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Worcester, Massachusetts, United States

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Worcester, Massachusetts, United States

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Battle Creek, Michigan, United States

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Kalamazoo, Michigan, United States

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Lansing, Michigan, United States

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Petoskey, Michigan, United States

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Saint Clair Shores, Michigan, United States

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Duluth, Minnesota, United States

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Eagan, Minnesota, United States

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Edina, Minnesota, United States

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Saint Louis Park, Minnesota, United States

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Flowood, Mississippi, United States

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Hattiesburg, Mississippi, United States

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Jackson, Mississippi, United States

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Tupelo, Mississippi, United States

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Florissant, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Grand Island, Nebraska, United States

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Lincoln, Nebraska, United States

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Reno, Nevada, United States

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Dover, New Hampshire, United States

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Lebanon, New Hampshire, United States

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Clifton, New Jersey, United States

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Haddon Heights, New Jersey, United States

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Manalapan, New Jersey, United States

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Morristown, New Jersey, United States

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New Brunswick, New Jersey, United States

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Trenton, New Jersey, United States

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Voorhees Township, New Jersey, United States

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Las Cruces, New Mexico, United States

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Albany, New York, United States

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Binghamton, New York, United States

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Brooklyn, New York, United States

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Cooperstown, New York, United States

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Hewlett, New York, United States

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Lake Success, New York, United States

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New York, New York, United States

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Olean, New York, United States

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Orchard Park, New York, United States

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Plainview, New York, United States

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Rochester, New York, United States

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Roslyn, New York, United States

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Smithtown, New York, United States

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Syracuse, New York, United States

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Utica, New York, United States

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Asheville, North Carolina, United States

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Belmont, North Carolina, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Greenville, North Carolina, United States

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Raleigh, North Carolina, United States

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Rock Hill, North Carolina, United States

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Wilmington, North Carolina, United States

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Bismarck, North Dakota, United States

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Akron, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Gallipolis, Ohio, United States

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Mayfield, Ohio, United States

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Middleburg Heights, Ohio, United States

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Perryburg, Ohio, United States

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Zanesville, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Lake Oswego, Oregon, United States

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Bethlehem, Pennsylvania, United States

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Camp Hill, Pennsylvania, United States

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Duncansville, Pennsylvania, United States

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Lebanon, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pottstown, Pennsylvania, United States

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West Reading, Pennsylvania, United States

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Wexford, Pennsylvania, United States

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Willow Grove, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Hickory Grove, South Carolina, United States

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Myrtle Beach, South Carolina, United States

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Hendersonville, Tennessee, United States

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Hixson, Tennessee, United States

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Jackson, Tennessee, United States

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Knoxville, Tennessee, United States

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Nashville, Tennessee, United States

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Amarillo, Texas, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Carrollton, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Lubbock, Texas, United States

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Mesquite, Texas, United States

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Nassau Bay, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Tyler, Texas, United States

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Waco, Texas, United States

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Burlington, Vermont, United States

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Arlington, Virginia, United States

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Burke, Virginia, United States

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Richmond, Virginia, United States

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Virginia Beach, Virginia, United States

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Olympia, Washington, United States

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Spokane, Washington, United States

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Tacoma, Washington, United States

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Beckley, West Virginia, United States

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Clarksburg, West Virginia, United States

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Brookfield, Wisconsin, United States

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Franklin, Wisconsin, United States

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Glendale, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Onalaska, Wisconsin, United States

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Countries

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Puerto Rico United Kingdom United States

References

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Weinblatt ME, Kremer J, Cush J, Rigby W, Teng LL, Devenport J, Singh N, Lepley D, Genovese MC. Tocilizumab as monotherapy or in combination with nonbiologic disease-modifying antirheumatic drugs: twenty-four-week results of an open-label, clinical practice study. Arthritis Care Res (Hoboken). 2013 Mar;65(3):362-71. doi: 10.1002/acr.21847.

Reference Type DERIVED
PMID: 22972745 (View on PubMed)

Other Identifiers

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ML22533

Identifier Type: -

Identifier Source: org_study_id