A Study to Compare Subcutaneous Versus Intravenous Administration of RoActemra/Actemra (Tocilizumab) in Participants With Moderate to Severe Active Rheumatoid Arthritis

NCT ID: NCT01194414

Last Updated: 2016-06-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1262 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-09-30

Study Completion Date

2013-08-31

Brief Summary

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This randomized, double-blind, parallel group study compares the efficacy and safety of subcutaneous (sc) versus intravenous (iv) administration of tocilizumab in participants with moderate to severe active rheumatoid arthritis. Participants were randomized to receive either tocilizumab 162 mg sc weekly plus iv placebo every 4 weeks, or tocilizumab 8 mg/kg iv every 4 weeks plus sc placebo weekly during the double-blind period from baseline to Week 24. The double-blind period was followed by a 72-week open-label treatment with some switching of sc and iv administration. No placebo was administered in the open-label phase. Participants continued on their stable dose of disease-modifying antirheumatic drugs (DMARDs) throughout the study. Anticipated time on study treatment was 2 years.

Detailed Description

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Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Tocilizumab SC

Participants received tocilizumab 162 mg subcutaneous (SC) injection weekly plus placebo to tocilizumab intravenous (IV) infusion every 4 weeks for a total of 24 weeks in the double-blind period. Participants continued to receive tocilizumab 162 mg SC injection weekly for a total of 72 weeks in open label extension period.

Non-biologic disease-modifying anti-rheumatic drugs (DMARDs) at a stable dose continued throughout the study.

Group Type EXPERIMENTAL

tocilizumab SC

Intervention Type DRUG

Tocilizumab supplied in a single-use pre-filled syringe, with a needle safety device, delivering 162 mg/0.9 mL solution for subcutaneous injection once a week.

placebo to tocilizumab IV

Intervention Type DRUG

Placebo to tocilizumab supplied as a solution in 10 mL vials containing polysorbate 80 and sucrose in water for infusion every 4 weeks for a total of 24 weeks in the double-blind period.

Disease-modifying antirheumatic drugs (DMARDs)

Intervention Type DRUG

stable dose as prescribed

Tocilizumab IV

Participants received tocilizumab 8 mg/kg infusion (IV) every 4 weeks plus placebo to tocilizumab SC injection weekly for a total of 24 weeks in the double-blind period. Participants continued to receive tocilizumab 8 mg/kg IV infusion every 4 weeks for a total of 72 weeks in open label extension period.

Non-biologic disease-modifying anti-rheumatic drugs (DMARDs) at a stable dose continued throughout the study.

Group Type EXPERIMENTAL

tocilizumab IV

Intervention Type DRUG

Tocilizumab supplied in vials as a sterile solution for 8 mg/kg intravenous infusion every 4 weeks.

placebo to tocilizumab SC

Intervention Type DRUG

Placebo tocilizumab supplied as a single-use pre-filled syringe with a needle safety device, delivering 0.9 mL sodium chloride for subcutaneous injection once a week for 24 weeks in the double-blind period.

Disease-modifying antirheumatic drugs (DMARDs)

Intervention Type DRUG

stable dose as prescribed

Tocilizumab SC Then Tocilizumab IV

Participants who received tocilizumab 162 mg subcutaneous (SC) injection weekly plus placebo to tocilizumab IV infusion every 4 weeks for 24 weeks in double blind treatment period switched to tocilizumab 8 mg/kg IV infusion every 4 weeks for a total of 72 weeks in open label extension period.

Non-biologic disease-modifying anti-rheumatic drugs (DMARDs) at a stable dose continued throughout the study.

Group Type EXPERIMENTAL

tocilizumab SC

Intervention Type DRUG

Tocilizumab supplied in a single-use pre-filled syringe, with a needle safety device, delivering 162 mg/0.9 mL solution for subcutaneous injection once a week.

tocilizumab IV

Intervention Type DRUG

Tocilizumab supplied in vials as a sterile solution for 8 mg/kg intravenous infusion every 4 weeks.

placebo to tocilizumab IV

Intervention Type DRUG

Placebo to tocilizumab supplied as a solution in 10 mL vials containing polysorbate 80 and sucrose in water for infusion every 4 weeks for a total of 24 weeks in the double-blind period.

Disease-modifying antirheumatic drugs (DMARDs)

Intervention Type DRUG

stable dose as prescribed

Tocilizumab IV Then Tocilizumab SC

Participants who received tocilizumab 8 mg/kg infusion (IV) every 4 weeks plus placebo to tocilizumab SC injection weekly in double blind treatment period switched to tocilizumab 162 mg SC injection weekly for a total of 72 weeks in open label extension period.

Non-biologic disease-modifying anti-rheumatic drugs (DMARDs) at a stable dose will be continued throughout the study.

Group Type EXPERIMENTAL

tocilizumab SC

Intervention Type DRUG

Tocilizumab supplied in a single-use pre-filled syringe, with a needle safety device, delivering 162 mg/0.9 mL solution for subcutaneous injection once a week.

tocilizumab IV

Intervention Type DRUG

Tocilizumab supplied in vials as a sterile solution for 8 mg/kg intravenous infusion every 4 weeks.

placebo to tocilizumab SC

Intervention Type DRUG

Placebo tocilizumab supplied as a single-use pre-filled syringe with a needle safety device, delivering 0.9 mL sodium chloride for subcutaneous injection once a week for 24 weeks in the double-blind period.

Disease-modifying antirheumatic drugs (DMARDs)

Intervention Type DRUG

stable dose as prescribed

Interventions

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tocilizumab SC

Tocilizumab supplied in a single-use pre-filled syringe, with a needle safety device, delivering 162 mg/0.9 mL solution for subcutaneous injection once a week.

Intervention Type DRUG

tocilizumab IV

Tocilizumab supplied in vials as a sterile solution for 8 mg/kg intravenous infusion every 4 weeks.

Intervention Type DRUG

placebo to tocilizumab SC

Placebo tocilizumab supplied as a single-use pre-filled syringe with a needle safety device, delivering 0.9 mL sodium chloride for subcutaneous injection once a week for 24 weeks in the double-blind period.

Intervention Type DRUG

placebo to tocilizumab IV

Placebo to tocilizumab supplied as a solution in 10 mL vials containing polysorbate 80 and sucrose in water for infusion every 4 weeks for a total of 24 weeks in the double-blind period.

Intervention Type DRUG

Disease-modifying antirheumatic drugs (DMARDs)

stable dose as prescribed

Intervention Type DRUG

Other Intervention Names

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RoActemra/Actemra RoActemra/Actemra

Eligibility Criteria

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Inclusion Criteria

* Adult participants, ≥ 18 years of age
* Rheumatoid arthritis of ≥ 6 months duration, according to American College of Rheumatology (ACR) criteria
* Swollen joint count (SJC) ≥ 4 (66 joint count), tender joint count (TJC) ≥ 4 (68 joint count) at screening and baseline
* Inadequate response to current DMARD therapy
* Permitted DMARDs must be at stable dose for ≥ 8 weeks prior to baseline
* Oral corticosteroids (≤ 10 mg/day prednisone or equivalent) and NSAIDs (up to maximum recommended dose) must be at stable dose for ≥ 4 weeks prior to baseline

Exclusion Criteria

* Major surgery (including joint surgery) within 8 weeks prior to screening or planned major surgery within 6 months following randomization
* Rheumatic autoimmune disease other than RA
* Functional class IV (ACR classification)
* Diagnosis of juvenile idiopathic arthritis (JIA) or juvenile rheumatoid arthritis (JRA) and/or RA before the age of 16
* Prior history of or current inflammatory joint disease other than RA
* Intra-articular or parenteral corticosteroids within 4 weeks prior to baseline
* Previous treatment with tocilizumab
* Active current or history of recurrent infection
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Huntsville, Alabama, United States

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Tuscaloosa, Alabama, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Upland, California, United States

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Van Nuys, California, United States

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Denver, Colorado, United States

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Bridgeport, Connecticut, United States

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Delray Beach, Florida, United States

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Miami, Florida, United States

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Ocala, Florida, United States

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Orlando, Florida, United States

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Palm Harbor, Florida, United States

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Pinellas Park, Florida, United States

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South Miami, Florida, United States

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Tampa, Florida, United States

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Coeur d'Alene, Idaho, United States

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Morton Grove, Illinois, United States

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Wichita, Kansas, United States

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Monroe, Louisiana, United States

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Petoskey, Michigan, United States

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Saint Claire Shores, Michigan, United States

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Eagan, Minnesota, United States

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Florissant, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Lebanon, New Hampshire, United States

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Clifton, New Jersey, United States

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Manalapan, New Jersey, United States

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Voorhees Township, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albany, New York, United States

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Binghamton, New York, United States

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Orchard Park, New York, United States

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Asheville, North Carolina, United States

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Raleigh, North Carolina, United States

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Wilmington, North Carolina, United States

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Cincinnati, Ohio, United States

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Toledo, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Bethlehem, Pennsylvania, United States

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Charleston, South Carolina, United States

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Charleston, South Carolina, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Olympia, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Wenatchee, Washington, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Rosario, , Argentina

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Adelaide, , Australia

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Adelaide, , Australia

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Clayton, , Australia

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Geelong, , Australia

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Hobart, , Australia

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Malvern East, , Australia

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Maroochydore, , Australia

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New Lambton, , Australia

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Curitiba, , Brazil

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Goiânia, , Brazil

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Juiz de Fora, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Edmonton, Alberta, Canada

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Kelowna, British Columbia, Canada

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Vancouver, British Columbia, Canada

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St. John's, Newfoundland and Labrador, Canada

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St. John's, Newfoundland and Labrador, Canada

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Hamilton, Ontario, Canada

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Hamilton, Ontario, Canada

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Kitchener, Ontario, Canada

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Ottawa, Ontario, Canada

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St. Catharines, Ontario, Canada

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Windsor, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Rimouski, Quebec, Canada

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Sainte-Foy, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Bordeaux, , France

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Le Mans, , France

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Marseille, , France

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Montpellier, , France

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Nantes, , France

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Paris, , France

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Strasbourg, , France

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Toulouse, , France

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Bad Bramstedt, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Cologne, , Germany

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Dresden, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Gommern, , Germany

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Heidelberg, , Germany

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Herne, , Germany

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Hildesheim, , Germany

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Ludwigshafen, , Germany

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Osnabrück, , Germany

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Ratingen, , Germany

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Rostock, , Germany

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Würzburg, , Germany

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Guatemala City, , Guatemala

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Guatemala City, , Guatemala

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Hong Kong, , Hong Kong

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Hong Kong, , Hong Kong

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Arenzano, , Italy

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Bergamo, , Italy

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Catania, , Italy

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Cona (ferrara), , Italy

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Genova, , Italy

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Napoli, , Italy

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Pavia, , Italy

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Pisa, , Italy

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Potenza, , Italy

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Reggio Emilia, , Italy

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Udine, , Italy

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Varese, , Italy

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Klaipėda, , Lithuania

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Šiauliai, , Lithuania

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Vilnius, , Lithuania

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Culiacán, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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León, , Mexico

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Mexico Ctiy, , Mexico

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Mérida, , Mexico

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Miexico City, , Mexico

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Morelia, , Mexico

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Obregón, , Mexico

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Querétaro, , Mexico

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Saltillo, , Mexico

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Torreón, , Mexico

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Auckland, , New Zealand

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Hamilton, , New Zealand

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Tauranga, , New Zealand

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Wellington, , New Zealand

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Cebu, , Philippines

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Manila, , Philippines

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Quezon, , Philippines

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Bialystok, , Poland

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Lublin, , Poland

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Poznan, , Poland

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Warsaw, , Poland

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Ponce, , Puerto Rico

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Bucharest, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Iași, , Romania

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Moscow, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Ryazan, , Russia

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Saint Petersburg, , Russia

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Ulyanovsk, , Russia

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Yaroslavl, , Russia

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Yaroslavl, , Russia

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Singapore, , Singapore

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Cape Town, , South Africa

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Durban, , South Africa

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Parktown, , South Africa

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Port Elizabeth, , South Africa

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Stellenbosch, , South Africa

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A Coruña, , Spain

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Barakaldo, , Spain

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Bilbao, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Mérida, , Spain

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San Cristóbal de La Laguna, , Spain

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Santander, , Spain

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Santiago de Compostela, , Spain

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Seville, , Spain

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Torrelavega, , Spain

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Valencia, , Spain

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Khon Kaen, , Thailand

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Cambridge, , United Kingdom

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Cannock, , United Kingdom

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Coventry, , United Kingdom

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Eastbourne, , United Kingdom

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Exeter, , United Kingdom

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Harrogate, , United Kingdom

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Ipswich, , United Kingdom

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London, , United Kingdom

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Metropolitan Borough of Wirral, , United Kingdom

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Middlesbrough, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Northampton, , United Kingdom

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Nottingham, , United Kingdom

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Westcliffe-on-sea, , United Kingdom

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Countries

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United States Argentina Australia Brazil Bulgaria Canada Colombia France Germany Guatemala Hong Kong Italy Lithuania Mexico New Zealand Peru Philippines Poland Puerto Rico Romania Russia Singapore South Africa Spain Thailand United Kingdom

References

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Burmester GR, Rubbert-Roth A, Cantagrel A, Hall S, Leszczynski P, Feldman D, Rangaraj MJ, Roane G, Ludivico C, Bao M, Rowell L, Davies C, Mysler EF. Efficacy and safety of subcutaneous tocilizumab versus intravenous tocilizumab in combination with traditional DMARDs in patients with RA at week 97 (SUMMACTA). Ann Rheum Dis. 2016 Jan;75(1):68-74. doi: 10.1136/annrheumdis-2015-207281. Epub 2015 Jun 8.

Reference Type DERIVED
PMID: 26056119 (View on PubMed)

Other Identifiers

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2010-018375-22

Identifier Type: -

Identifier Source: secondary_id

WA22762

Identifier Type: -

Identifier Source: org_study_id

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