A Study to Assess the Safety and Efficacy of Tocilizumab in Patients With Active Rheumatoid Arthritis

NCT ID: NCT00109408

Last Updated: 2016-11-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

673 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-07-31

Study Completion Date

2007-12-31

Brief Summary

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This 2 arm study will assess the safety and efficacy of tocilizumab monotherapy versus methotrexate in patients with active rheumatoid arthritis (RA). Patients will be randomized to receive tocilizumab 8mg/kg iv every 4 weeks plus placebo po weekly, or methotrexate 7.5-20mg po weekly plus placebo iv every 4 weeks. The anticipated time on study treatment is 3-12 months and the target sample size is 500+ individuals.

Detailed Description

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Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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1

Group Type EXPERIMENTAL

tocilizumab [RoActemra/Actemra]

Intervention Type DRUG

8mg/kg iv every 4 weeks

2

Group Type ACTIVE_COMPARATOR

Methotrexate

Intervention Type DRUG

7.5-20mg po weekly

Interventions

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Methotrexate

7.5-20mg po weekly

Intervention Type DRUG

tocilizumab [RoActemra/Actemra]

8mg/kg iv every 4 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* adult patients at least 18 years of age with active RA for at least 3 months;
* patients of reproductive potential must be using reliable methods of contraception.

Exclusion Criteria

* major surgery (including joint surgery) within 8 weeks before entering study or planned major surgery within 6 months after entering study;
* treatment with methotrexate (MTX) within 6 months of entering study;
* patients who have stopped previous MTX treatment due to toxicity or lack of response;
* women who are pregnant or breast-feeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Pavia, , Italy

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Reggio Emilia, , Italy

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Montgomery, Alabama, United States

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Mesa, Arizona, United States

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Paradise Valley, Arizona, United States

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Phoenix, Arizona, United States

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Little Rock, Arkansas, United States

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Huntington Beach, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Palm Springs, California, United States

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Sacramento, California, United States

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San Leandro, California, United States

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Santa Maria, California, United States

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Jupiter, Florida, United States

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Palm Habor, Florida, United States

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Palm Harbor, Florida, United States

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Port Orange, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Idaho Falls, Idaho, United States

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Meridian, Idaho, United States

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Morton Grove, Illinois, United States

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Springfield, Illinois, United States

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Indianapolis, Indiana, United States

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Cedar Rapids, Iowa, United States

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Des Moines, Iowa, United States

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Bowling Green, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Slidell, Louisiana, United States

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Greenbelt, Maryland, United States

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Pittsfield, Massachusetts, United States

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Grand Rapids, Michigan, United States

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Kalamazoo, Michigan, United States

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Lansing, Michigan, United States

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Eagan, Minnesota, United States

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Saint Cloud, Minnesota, United States

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Flowood, Mississippi, United States

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Tupelo, Mississippi, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Dover, New Hampshire, United States

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Nashua, New Hampshire, United States

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Haddon Heights, New Jersey, United States

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New Brunswick, New Jersey, United States

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Albany, New York, United States

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Syracuse, New York, United States

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Fayetteville, North Carolina, United States

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Canton, Ohio, United States

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Mayfield, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Duncansville, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Willow Grove, Pennsylvania, United States

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Wyomissing, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Greenville, South Carolina, United States

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Hickory Grove, South Carolina, United States

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Hixson, Tennessee, United States

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Nashville, Tennessee, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Mesquite, Texas, United States

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Chesapeake, Virginia, United States

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Mountlake Terrace, Washington, United States

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Olympia, Washington, United States

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Spokane, Washington, United States

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Yakima, Washington, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Rosario, , Argentina

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San Juan Bautista, , Argentina

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Adelaide, , Australia

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Hobart, , Australia

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Shenton Park, , Australia

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Sydney, , Australia

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Woodville, , Australia

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Woolloongabba, , Australia

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Victoria, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Winnipeg, Manitoba, Canada

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St. John's, Newfoundland and Labrador, Canada

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Burlington, Ontario, Canada

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Hamilton, Ontario, Canada

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Kitchener, Ontario, Canada

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Mississauga, Ontario, Canada

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Ottawa, Ontario, Canada

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Guangzhou, , China

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Hefei Anhui, , China

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Jinan, , China

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Copenhagen, , Denmark

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Hillerød, , Denmark

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Hvidovre, , Denmark

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Brest, , France

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Lyon, , France

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Paris, , France

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Rouen, , France

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Ashkelon, , Israel

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Beersheba, , Israel

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Haifa, , Israel

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Haifa, , Israel

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Kfar Saba, , Israel

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Ramat Gan, , Israel

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Rishon LeZiyyon, , Israel

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Genova, , Italy

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Milan, , Italy

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Siena, , Italy

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Panevezys, , Lithuania

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Šiauliai, , Lithuania

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Vilnius, , Lithuania

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Levanger, , Norway

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Lillehammer, , Norway

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Lima, , Peru

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Lima, , Peru

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Almada, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Belgrade, , Serbia

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Niška Banja, , Serbia

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Ljubljana, , Slovenia

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Maribor, , Slovenia

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Cape Town, , South Africa

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Cape Town, , South Africa

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Diepkloof, , South Africa

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Pinelands, , South Africa

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Radiokop, , South Africa

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Alcorcón, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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Guadalajara, , Spain

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Lugo, , Spain

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Salamanca, , Spain

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San Cristóbal de La Laguna, , Spain

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Santiago de Compostela, , Spain

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Valencia, , Spain

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Countries

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Croatia Serbia and Montenegro United States Argentina Australia Canada China Denmark France Israel Italy Lithuania Mexico Norway Peru Portugal Serbia Slovenia South Africa Spain

References

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Drobinski PJ, Bay-Jensen AC, Karsdal MA, Sardar S, Siebuhr AS. Connective tissue remodelling is differently modulated by tocilizumab versus methotrexate monotherapy in patients with early rheumatoid arthritis: the AMBITION study. Arthritis Res Ther. 2021 Jan 7;23(1):13. doi: 10.1186/s13075-020-02378-7.

Reference Type DERIVED
PMID: 33413588 (View on PubMed)

Strand V, Michalska M, Birchwood C, Pei J, Tuckwell K, Finch R, Gabay C, Kavanaugh A, Jones G. Impact of tocilizumab monotherapy on patient-reported outcomes in patients with rheumatoid arthritis from two randomised controlled trials. RMD Open. 2017 Sep 14;3(2):e000496. doi: 10.1136/rmdopen-2017-000496. eCollection 2017.

Reference Type DERIVED
PMID: 28955499 (View on PubMed)

Jones G, Wallace T, McIntosh MJ, Brockwell L, Gomez-Reino JJ, Sebba A. Five-year Efficacy and Safety of Tocilizumab Monotherapy in Patients with Rheumatoid Arthritis Who Were Methotrexate- and Biologic-naive or Free of Methotrexate for 6 Months: the AMBITION Study. J Rheumatol. 2017 Feb;44(2):142-146. doi: 10.3899/jrheum.160287. Epub 2016 Dec 1.

Reference Type DERIVED
PMID: 27909081 (View on PubMed)

Wang J, Bansal AT, Martin M, Germer S, Benayed R, Essioux L, Lee JS, Begovich A, Hemmings A, Kenwright A, Taylor KE, Upmanyu R, Cutler P, Harari O, Marchini J, Criswell LA, Platt A. Genome-wide association analysis implicates the involvement of eight loci with response to tocilizumab for the treatment of rheumatoid arthritis. Pharmacogenomics J. 2013 Jun;13(3):235-41. doi: 10.1038/tpj.2012.8. Epub 2012 Apr 10.

Reference Type DERIVED
PMID: 22491018 (View on PubMed)

Jones G, Sebba A, Gu J, Lowenstein MB, Calvo A, Gomez-Reino JJ, Siri DA, Tomsic M, Alecock E, Woodworth T, Genovese MC. Comparison of tocilizumab monotherapy versus methotrexate monotherapy in patients with moderate to severe rheumatoid arthritis: the AMBITION study. Ann Rheum Dis. 2010 Jan;69(1):88-96. doi: 10.1136/ard.2008.105197.

Reference Type DERIVED
PMID: 19297346 (View on PubMed)

Other Identifiers

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WA17824

Identifier Type: -

Identifier Source: org_study_id