A Study of Tocilizumab in Combination With DMARDs in Patients With Moderate to Severe Rheumatoid Arthritis

NCT ID: NCT00531817

Last Updated: 2012-08-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

619 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-10-31

Study Completion Date

2011-03-31

Brief Summary

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This 2-arm study assessed the safety and efficacy of tocilizumab versus placebo, both in combination with disease modifying antirheumatic drugs (DMARDs), in regard to reduction in signs and symptoms, in patients with moderate to severe active rheumatoid arthritis with an inadequate response to DMARDs. Patients were randomized in a ratio of 2:1 to receive either tocilizumab 8 mg/kg intravenously (IV) or placebo IV every 4 weeks. All patients also received stable antirheumatic therapy, including permitted DMARDs. The anticipated time on study treatment was 3-12 months and the target sample size was 500+ individuals.

Detailed Description

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Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Tocilizumab 8 mg/kg + DMARDs

Group Type EXPERIMENTAL

Tocilizumab

Intervention Type DRUG

Tocilizumab intravenously at a dose of 8 mg/kg over a 1-hour infusion, every 4 weeks, for a total of 6 infusions.

Permitted DMARDs

Intervention Type DRUG

As prescribed. The following DMARDs were permitted in this study: methotrexate (MTX), chloroquine, hydroxychloroquine, parenteral gold, sulfasalazine, azathioprine, and leflunomide. These DMARDs could be used alone or in combination, except for the combination of MTX and leflunomide, which was not allowed.

Placebo + DMARDs

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo IV over a 1-hour infusion, every 4 weeks, for a total of 6 infusions.

Permitted DMARDs

Intervention Type DRUG

As prescribed. The following DMARDs were permitted in this study: methotrexate (MTX), chloroquine, hydroxychloroquine, parenteral gold, sulfasalazine, azathioprine, and leflunomide. These DMARDs could be used alone or in combination, except for the combination of MTX and leflunomide, which was not allowed.

Interventions

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Tocilizumab

Tocilizumab intravenously at a dose of 8 mg/kg over a 1-hour infusion, every 4 weeks, for a total of 6 infusions.

Intervention Type DRUG

Placebo

Placebo IV over a 1-hour infusion, every 4 weeks, for a total of 6 infusions.

Intervention Type DRUG

Permitted DMARDs

As prescribed. The following DMARDs were permitted in this study: methotrexate (MTX), chloroquine, hydroxychloroquine, parenteral gold, sulfasalazine, azathioprine, and leflunomide. These DMARDs could be used alone or in combination, except for the combination of MTX and leflunomide, which was not allowed.

Intervention Type DRUG

Other Intervention Names

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Actemra RoActemra

Eligibility Criteria

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Inclusion Criteria

* Adult patients, ≥18 years of age
* Active rheumatoid arthritis of \>6 months duration
* Received permitted DMARDs each at a stable dose for at least 7 weeks prior to baseline

Exclusion Criteria

* Rheumatic autoimmune disease or inflammatory joint disease other than rheumatoid arthritis
* Major surgery within 8 weeks prior to screening or planned within 6 months following randomization
* Unsuccessful treatment with a biologic agent, including an anti-TNF agent
* Previous treatment with tocilizumab
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Montgomery, Alabama, United States

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Lake Havasu City, Arizona, United States

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Paradise Valley, Arizona, United States

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Peoria, Arizona, United States

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Scottsdale, Arizona, United States

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Scottsdale, Arizona, United States

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Jonesboro, Arkansas, United States

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Beverly Hills, California, United States

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Escondido, California, United States

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La Jolla, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Pasadena, California, United States

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Santa Maria, California, United States

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Santa Monica, California, United States

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Upland, California, United States

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Van Nuys, California, United States

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Walnut Creek, California, United States

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Whittier, California, United States

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Colorado Springs, Colorado, United States

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Trumbull, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Dunedin, Florida, United States

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Fort Lauderdale, Florida, United States

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Lake Mary, Florida, United States

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Melbourne, Florida, United States

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Miami, Florida, United States

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Ocala, Florida, United States

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Orange Park, Florida, United States

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Orlando, Florida, United States

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Palm Harbor, Florida, United States

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Plantation, Florida, United States

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Sarasota, Florida, United States

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Tamarac, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Blue Ridge, Georgia, United States

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Fort Valley, Georgia, United States

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Tifton, Georgia, United States

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Boise, Idaho, United States

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Idaho Falls, Idaho, United States

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Nampa, Idaho, United States

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Downers Grove, Illinois, United States

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Springfield, Illinois, United States

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Evansville, Indiana, United States

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Munster, Indiana, United States

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South Bend, Indiana, United States

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Leawood, Kansas, United States

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Bowling Green, Kentucky, United States

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Lexington, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Baton Rouge, Louisiana, United States

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Monroe, Louisiana, United States

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New Orleans, Louisiana, United States

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Wheaton, Maryland, United States

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Mansfield, Massachusetts, United States

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Worcester, Massachusetts, United States

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Worcester, Massachusetts, United States

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Kalamazoo, Michigan, United States

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Saint Clair Shores, Michigan, United States

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Eagan, Minnesota, United States

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Flowood, Mississippi, United States

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Tupelo, Mississippi, United States

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Florissant, Missouri, United States

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St Louis, Missouri, United States

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Billings, Montana, United States

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Kalispell, Montana, United States

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Missoula, Montana, United States

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Grand Island, Nebraska, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Reno, Nevada, United States

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Dover, New Hampshire, United States

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Freehold, New Jersey, United States

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New Brunswick, New Jersey, United States

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Passaic, New Jersey, United States

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Teaneck, New Jersey, United States

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Mineola, New York, United States

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New York, New York, United States

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New York, New York, United States

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Orchard Park, New York, United States

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Smithtown, New York, United States

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The Bronx, New York, United States

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Belmont, North Carolina, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Greensboro, North Carolina, United States

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Greenville, North Carolina, United States

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Hickory, North Carolina, United States

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Rock Hill, North Carolina, United States

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Akron, Ohio, United States

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Beechwood, Ohio, United States

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Mayfield, Ohio, United States

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Middleburg Heights, Ohio, United States

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Perrysburg, Ohio, United States

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Zanesville, Ohio, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Lake Oswego, Oregon, United States

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Portland, Oregon, United States

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Salem, Oregon, United States

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Bethlehem, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Wexford, Pennsylvania, United States

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Willow Grove, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Florence, South Carolina, United States

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Greenville, South Carolina, United States

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Myrtle Beach, South Carolina, United States

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Rapid City, South Dakota, United States

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Rapid City, South Dakota, United States

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Sioux Falls, South Dakota, United States

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Watertown, South Dakota, United States

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Crossville, Tennessee, United States

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Hendersonville, Tennessee, United States

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Jackson, Tennessee, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Amarillo, Texas, United States

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Amarillo, Texas, United States

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Bellaire, Texas, United States

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Carrollton, Texas, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Mesquite, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Waco, Texas, United States

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Salt Lake City, Utah, United States

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Burlington, Vermont, United States

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Burke, Virginia, United States

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Reston, Virginia, United States

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Salem, Virginia, United States

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Seattle, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Beckley, West Virginia, United States

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Clarksburg, West Virginia, United States

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Milwaukee, Wisconsin, United States

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Onalaska, Wisconsin, United States

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Wausau, Wisconsin, United States

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San Juan, , Puerto Rico

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Countries

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United States Puerto Rico

References

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Yazici Y, Curtis JR, Ince A, Baraf HS, Lepley DM, Devenport JN, Kavanaugh A. Early effects of tocilizumab in the treatment of moderate to severe active rheumatoid arthritis: a one-week sub-study of a randomised controlled trial (Rapid Onset and Systemic Efficacy [ROSE] Study). Clin Exp Rheumatol. 2013 May-Jun;31(3):358-64. Epub 2013 Jan 10.

Reference Type DERIVED
PMID: 23305631 (View on PubMed)

Yazici Y, Curtis JR, Ince A, Baraf H, Malamet RL, Teng LL, Kavanaugh A. Efficacy of tocilizumab in patients with moderate to severe active rheumatoid arthritis and a previous inadequate response to disease-modifying antirheumatic drugs: the ROSE study. Ann Rheum Dis. 2012 Feb;71(2):198-205. doi: 10.1136/ard.2010.148700. Epub 2011 Sep 26.

Reference Type DERIVED
PMID: 21949007 (View on PubMed)

Other Identifiers

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ML21136

Identifier Type: -

Identifier Source: org_study_id