A Study to Assess the Long-term Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod in Adults With Active Idiopathic Inflammatory Myopathy

NCT ID: NCT05979441

Last Updated: 2026-02-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ENROLLING_BY_INVITATION

Clinical Phase

PHASE3

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-12

Study Completion Date

2028-09-30

Brief Summary

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The main purpose of this study is to measure the long-term safety and tolerability of efgartigimod PH20 SC in adult participants with Idiopathic Inflammatory Myopathy (IIM) who previously participated in ARGX-113-2007.

The study consists of a treatment period where participants will receive efgartigimod PH20 SC for up to 51 months. The treatment period will be followed by a treatment-free safety follow-up period of 56 days.

Detailed Description

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Conditions

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Myositis Active Idiopathic Inflammatory Myopathy Dermatomyositis Polymyositis Immune-Mediated Necrotizing Myopathy Antisynthetase Syndrome

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Efgartigimod PH20 SC

Participants receiving efgartigimod PH20 subcutaneously

Group Type EXPERIMENTAL

Efgartigimod PH20 SC

Intervention Type BIOLOGICAL

Subcutaneous injection of Efgartigimod PH20 given by vials or prefilled syringe (PFS)

Interventions

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Efgartigimod PH20 SC

Subcutaneous injection of Efgartigimod PH20 given by vials or prefilled syringe (PFS)

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Has completed trial ARGX-113-2007
* Being capable of providing signed informed consent and complying with protocol requirements
* Agrees to use contraceptive measures consistent with local regulations and women of childbearing potential must have a negative urine pregnancy test at baseline before receiving the study drug

Exclusion Criteria

* Intention to have major surgery during the study period or any other medical condition that has arisen since enrollment in study ARGX-113-2007, that in the investigator's opinion, would confound the results of the study or put the participant at undue risk
* Known hypersensitivity reaction to the study drug or 1 of its excipients
* Development of any malignancy, either new or recurrent, other than basal cell carcinoma of the skin, regardless of relatedness
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Neuromuscular Clinical and Research Center - Neurology

Phoenix, Arizona, United States

Site Status

Attune Health Research, Inc

Beverly Hills, California, United States

Site Status

UCI Health - ALS and Neuromuscular Center - Neurology

Orange, California, United States

Site Status

UCSF Health - ALS and Neurodegenerative Disease Center - Dermatology

San Francisco, California, United States

Site Status

Yale Cancer Center-Yale University School Of Medicine

New Haven, Connecticut, United States

Site Status

UF Health - Rheumatology Medical Specialties Medical Plaza

Gainesville, Florida, United States

Site Status

Mayo Clinic - Florida - Neurology

Jacksonville, Florida, United States

Site Status

Emory Healthcare - Emory Clinic - Rheumatology

Atlanta, Georgia, United States

Site Status

Northwestern Medicine - Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

Northwell Health Physician Partners Rheumatology

Great Neck, New York, United States

Site Status

University of North Carolina (UNC) School of Medicine

Chapel Hill, North Carolina, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Austin Neuromuscular Center (National Neuromuscular Research Institute, PLLC)

Austin, Texas, United States

Site Status

Nerve And Muscle Center Of Texas

Houston, Texas, United States

Site Status

Framingham Centro Medico

La Plata, , Argentina

Site Status

Centro Dermatologico Schejtman

San Miguel, , Argentina

Site Status

Centro Medico Privado de Reumatologia

San Miguel de Tucumán, , Argentina

Site Status

Tirol Kliniken - A.o. Landeskrankenhaus Innsbruck - Neurology

Innsbruck, , Austria

Site Status

AZ Sint-Lucas - Campus Sint-Lucas - Neurology

Ghent, , Belgium

Site Status

Universitair Ziekenhuis Leuven Gasthuisberg Campus

Leuven, , Belgium

Site Status

Medical Centre Artmed

Plovdiv, , Bulgaria

Site Status

Multiprofile hospital for active treatment Kaspela EOOD

Plovdiv, , Bulgaria

Site Status

Peking Union Medical College Hospital

Beijing, , China

Site Status

Sichuan Provincial Academy of Medical Sciences and Sichuan Provincial People's Hospital

Chengdu, , China

Site Status

Cyprus Institute of Neurology and Genetics

Nicosia, , Cyprus

Site Status

Revmatologicky Ustav

Prague, , Czechia

Site Status

Copenhagen University Hospital-Rigshospitalet University Hospital

Copenhagen, , Denmark

Site Status

Reference Center Neuro-Muscular Diseases - CHU Paris Group Hospitalier La Pitie Salpetriere-Charles Foix

Paris, , France

Site Status

Aversi Clinic

Tbilisi, , Georgia

Site Status

LLC MediClub Georgia

Tbilisi, , Georgia

Site Status

New Hospitals

Tbilisi, , Georgia

Site Status

The First Medical Center

Tbilisi, , Georgia

Site Status

Charite Universitaetsmedizin Berlin - Campus Charite Mitte (CCM) - Rheumatology

Berlin, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Rheumazentrum Ruhrgebiet

Herne, , Germany

Site Status

Universitatsmedizin Mannheim GmbH

Mannheim, , Germany

Site Status

Universitaetsklinikum Tuebingen (UKT)

Tübingen, , Germany

Site Status

Klinikum der Universitaet Ulm

Ulm, , Germany

Site Status

National and Kapodistrian University of Athens - Eginition Hospital

Athens, , Greece

Site Status

ATTIKON University General Hospital - Neurology

Athens, , Greece

Site Status

University College Dublin (UCD) - St. Vincent's University Hospital (SVUH)

Dublin, , Ireland

Site Status

Azienda Ospedaliero Universitaria Consorziale Policlinico

Bari, , Italy

Site Status

Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - Ospedale San Raffaele Hospital

Milan, , Italy

Site Status

Azienda Ospedaliero Universitaria Pisana - Ospedale Santa Chiara - Rheumatology

Pisa, , Italy

Site Status

Ospedale Sant'Andrea Hospital

Roma, , Italy

Site Status

Fondazione Policlinico Universitario Agostino Gemelli - Neurology

Roma, , Italy

Site Status

Azienda sanitaria universitaria Friuli Centrale - ASUFC

Udine, , Italy

Site Status

Juntendo University Hospital

Bunkyō City, , Japan

Site Status

The University of Tokyo Hospital

Bunkyō City, , Japan

Site Status

Japan Community Healthcare Organization Chukyo Hospital

Nagoya, , Japan

Site Status

Wakayama Medical University Hospital

Wakayama, , Japan

Site Status

Santaros University Clinic

Vilnius, , Lithuania

Site Status

Hospital Angeles Clinica Londres

Mexico City, , Mexico

Site Status

Amsterdam UMC Research BV

Amsterdam, , Netherlands

Site Status

Clinica San Juan de Dios - sede Arequipa - Rheumatology

Arequipa, , Peru

Site Status

Instituto Peruano Del Hueso Y La Articulacion Sac-Privado-Lima,Centro De Investigacion Iphar

Lima, , Peru

Site Status

Investigaciones Clinicas S.A.C.

Lima, , Peru

Site Status

USK-WAM Centralny Szpital Weteranow - Szpital Kniniczny ul. Zeromskiego 113 - Rheumatology

Lodz, , Poland

Site Status

Centrum Wsparcia Badan Klinicznych Pomorskiego Uniwersytetu Medycznego w Szczecinie (CWBK PUM) - Rheumatology

Szczecin, , Poland

Site Status

Centro Hospitalar do Porto - Hospital Santo Antonio

Porto, , Portugal

Site Status

Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Institute of Rheumatology

Belgrade, , Serbia

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia - Neurology

Valencia, , Spain

Site Status

Karolinska Universitestssjukhus Solna

Solna, , Sweden

Site Status

Chung Shan Medical University Hospital

Taichung, , Taiwan

Site Status

King Chulalongkorn Memorial Hospital - Neurology

Bangkok, , Thailand

Site Status

Phramongkutklao Hospital

Bangkok, , Thailand

Site Status

Ramathibodi hospital

Bangkok, , Thailand

Site Status

Siriraj Hospital, Mahidol University of Internal medicine

Bangkok, , Thailand

Site Status

Faculty Of Medicine, Khon Kaen University

Khon Kaen, , Thailand

Site Status

Aintree University Hospital - Liverpool University Hospitals NHS Foundation Trust

Liverpool, , United Kingdom

Site Status

The Royal Free Hospital

London, , United Kingdom

Site Status

Northern Care Allicance NHS Foundation Trust - Salford Royal - Rheumatology

Salford, , United Kingdom

Site Status

Countries

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United States Argentina Austria Belgium Bulgaria China Cyprus Czechia Denmark France Georgia Germany Greece Ireland Italy Japan Lithuania Mexico Netherlands Peru Poland Portugal Serbia South Korea Spain Sweden Taiwan Thailand United Kingdom

Related Links

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Other Identifiers

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2022-502851-79-00

Identifier Type: CTIS

Identifier Source: secondary_id

ARGX-113-2011

Identifier Type: -

Identifier Source: org_study_id

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