A Safety and Tolerability Study of ARGX-113 in Patients With Myasthenia Gravis Who Have Generalized Muscle Weakness.

NCT ID: NCT03770403

Last Updated: 2023-07-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

151 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-03-01

Study Completion Date

2022-06-30

Brief Summary

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This is a Long-Term, Single-Arm, Open-Label, Multicenter Phase 3 follow-on trial of the ARGX-113-1704 study to evaluate the safety and tolerability of ARGX-113 in patients with gMG. Patients who have completed at least 1 cycle of treatment and at least 1 year of trial ARGX-113-1705 and have started Part B are eligible to enroll in the open-label trial ARGX-113-2002 to receive efgartigimod by SC administration.

Detailed Description

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Conditions

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Generalized Myasthenia Gravis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ARGX-113

Group Type EXPERIMENTAL

ARGX-113

Intervention Type BIOLOGICAL

Intravenous administration of ARGX-113

Interventions

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ARGX-113

Intravenous administration of ARGX-113

Intervention Type BIOLOGICAL

Other Intervention Names

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efgartigimod

Eligibility Criteria

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Inclusion Criteria

1. Patients with the ability to understand the requirements of the trial, provide written informed consent, and comply with the trial protocol procedures.
2. Patients who participated in trial ARGX-113-1704 and are eligible for roll over, as specified in the protocol.

Exclusion Criteria

1. Patients who discontinued early from trial ARGX-113-1704 or patients who discontinued early from randomized treatment for pregnancy or rescue reasons or an (S)AE that might jeopardize the safety of the patient in that trial.
2. Pregnant and lactating women, and those intending to become pregnant during the trial or within 90 days after the last dosing. Women or childbearing potential should have a negative urine pregnancy test at SEB.
3. Male patients who are sexually active and do not intend to use effective methods of contraception during the trial or within 90 days after the last dosing or male patients who plan to donate sperm during the trial or within 90 days after the last dosing.
4. Patients with known Hepatitis B Virus (HBV), Hepatitis C Virus (HCV) or Human Immunodeficiency Virus (HIV) seropositivity.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sabine Coppieters, MD

Role: STUDY_DIRECTOR

argenx

Locations

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Investigator Site 42

Carlsbad, California, United States

Site Status

Investigator Site 8

Los Angeles, California, United States

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Investigator Site 33

Orange, California, United States

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Investigator Site 21

Palo Alto, California, United States

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Investigator Site 41

Jacksonville, Florida, United States

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Investigator Site 4

Tampa, Florida, United States

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Investigator Site 14

Kansas City, Kansas, United States

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Investigator Site 32

Detroit, Michigan, United States

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Investigator Site 2

Chapel Hill, North Carolina, United States

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Investigator Site 18

Cleveland, Ohio, United States

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Investigator Site 12

Portland, Oregon, United States

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Investigator Site 1

Cordova, Tennessee, United States

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Investigator Site 3

San Antonio, Texas, United States

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Investigator Site 37

Charlottesville, Virginia, United States

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Investigator Site 11

Edegem, , Belgium

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Investigator Site 7

Ghent, , Belgium

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Investigator Site 20

Toronto, Ontario, Canada

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Investigator Site 25

Montreal, Quebec, Canada

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Investigator Site 16

Brno, , Czechia

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Investigator Site 19

Ostrava-Poruba, , Czechia

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Investigator Site 30

Prague, , Czechia

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Investigator Site 49

Aarhus, , Denmark

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Investigator Site 17

Copenhagen, , Denmark

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Investigator Site 50

Bordeaux, , France

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Investigator Site 51

Marseille, , France

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Investigator Site 45

Tbilisi, , Georgia

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Investigator Site 31

Tbilisi, , Georgia

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Investigator Site 46

Tbilisi, , Georgia

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Investigator Site 28

Berlin, , Germany

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Investigator Site 35

Budapest, , Hungary

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Investigator Site 52

Szeged, , Hungary

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Investigator Site 10

Milan, MI, Italy

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Investigator Site 5

Napoli, , Italy

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Investigator Site 38

Roma, , Italy

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Investigator Site 24

Sapporo, Hokkaido, Japan

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Investigator Site 13

Hanamaki-shi, Iwate, Japan

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Investigator Site 27

Sendai, Miyagi, Japan

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Investigator Site 23

Ōsaka-sayama, Osaka, Japan

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Investigator Site 22

Suita, Osaka, Japan

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Investigator Site 40

Meguro City, Tokyo, Japan

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Investigator Site 43

Shinjuku-Ku, Tokyo, Japan

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Investigator Site 47

Chiba, , Japan

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Investigator Site 44

Hiroshima, , Japan

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Investigator Site 48

Minato, , Japan

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Investigator Site 36

Leiden, , Netherlands

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Investigator Site 9

Gdansk, , Poland

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Investigator Site 29

Katowice, , Poland

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Investigator Site 6

Krakow, , Poland

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Investigator Site 15

Warsaw, , Poland

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Investigator Site 34

Novosibirsk, , Russia

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Investigator Site 39

Samara, , Russia

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Investigator Site 26

Belgrade, , Serbia

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Countries

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United States Belgium Canada Czechia Denmark France Georgia Germany Hungary Italy Japan Netherlands Poland Russia Serbia

References

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Howard JF Jr, Bril V, Vu T, Karam C, Peric S, De Bleecker JL, Murai H, Meisel A, Beydoun SR, Pasnoor M, Guglietta A, Van Hoorick B, Steeland S, T'joen C, Utsugisawa K, Verschuuren J, Mantegazza R; ADAPT+ Study Group. Long-term safety, tolerability, and efficacy of efgartigimod (ADAPT+): interim results from a phase 3 open-label extension study in participants with generalized myasthenia gravis. Front Neurol. 2024 Jan 17;14:1284444. doi: 10.3389/fneur.2023.1284444. eCollection 2023.

Reference Type DERIVED
PMID: 38318236 (View on PubMed)

Howard JF Jr, Bril V, Vu T, Karam C, Peric S, Margania T, Murai H, Bilinska M, Shakarishvili R, Smilowski M, Guglietta A, Ulrichts P, Vangeneugden T, Utsugisawa K, Verschuuren J, Mantegazza R; ADAPT Investigator Study Group. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial. Lancet Neurol. 2021 Jul;20(7):526-536. doi: 10.1016/S1474-4422(21)00159-9.

Reference Type DERIVED
PMID: 34146511 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002133-37

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ARGX-113-1705

Identifier Type: -

Identifier Source: org_study_id

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