A Study to Assess Efficacy and Safety of Efgartigimod PH20 SC in Adults With Ocular Myasthenia Gravis

NCT ID: NCT06558279

Last Updated: 2025-12-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

141 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-09-18

Study Completion Date

2027-12-31

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of efgartigimod PH20 SC given by a pre-filled syringe in adult patients with ocular myasthenia gravis. The study consists of a part A (approximately 7 weeks) and a part B (up to 2 years). In part A, half of the participants will receive efgartigimod PH20 SC and the other half will receive placebo. In part B, all participants will receive efgartigimod PH20 SC. The participants will be in the study for about up to 2 years and 12 weeks.

Detailed Description

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Conditions

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Myasthenia Gravis, Ocular

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Efgartigimod PH20 SC in part A+B

Participants receiving efgartigimod PH20 SC during part A and part B

Group Type EXPERIMENTAL

Efgartigimod PH20 SC

Intervention Type COMBINATION_PRODUCT

Subcutaneous efgartigimod PH20 SC given by prefilled syringe

Placebo PH20 SC in Part A + Efgartigimod PH20 SC in Part B

Participants receiving placebo PH20 SC in Part A and Efgartigimod PH20 SC in Part B

Group Type EXPERIMENTAL

Efgartigimod PH20 SC

Intervention Type COMBINATION_PRODUCT

Subcutaneous efgartigimod PH20 SC given by prefilled syringe

Placebo PH20 SC

Intervention Type OTHER

Subcutaneous placebo PH20 SC given by prefilled syringe

Interventions

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Efgartigimod PH20 SC

Subcutaneous efgartigimod PH20 SC given by prefilled syringe

Intervention Type COMBINATION_PRODUCT

Placebo PH20 SC

Subcutaneous placebo PH20 SC given by prefilled syringe

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Is at least 18 years of age and the local legal age of consent for clinical studies
* Has been diagnosed with myasthenia gravis and supported by seropositivity for AChR-Ab; or abnormal neuromuscular transmission demonstrated by abnormal neurophysiology testing and history on positive edrophonium chloride testing or demonstrated improvement on MG therapy"
* Is MGFA Class I (any ocular muscle weakness)
* Has a screening and baseline MGII (PRO) ocular score of at least 6 with at least 2 ocular items with a score of at least 2

Exclusion Criteria

* Other diseases that lead to eyelid drooping, peripheral muscle weakness, or diplopia
* Known autoimmune disease or any medical condition other than indication under study that would interfere with an accurate assessment of clinical symptoms of ocular myasthenia gravis or puts the participant at undue risk
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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HonorHealth Neurology - Bob Bové Neuroscience Institute

Scottsdale, Arizona, United States

Site Status

Loma Linda University Health

Loma Linda, California, United States

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USC Roski Eye Institute - Los Angeles

Los Angeles, California, United States

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University of California San Francisco

San Francisco, California, United States

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Neurology Offices of South Florida

Boca Raton, Florida, United States

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SFM Clinical Research, LLC

Boca Raton, Florida, United States

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Neurology Associates PA

Maitland, Florida, United States

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University of South Florida

Tampa, Florida, United States

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Northwestern Memorial Hospital

Chicago, Illinois, United States

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University of California Irvine

Columbia, Maryland, United States

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Massachusetts General Hospital

Boston, Massachusetts, United States

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Henry Ford Health System

Detroit, Michigan, United States

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Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

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University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

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Duke Neurological Disorders Clinic

Durham, North Carolina, United States

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Cleveland Clinic

Cleveland, Ohio, United States

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Martha Morehouse Medical plaza

Columbus, Ohio, United States

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Penn Medicine University City

Philadelphia, Pennsylvania, United States

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National Neuromuscular Research Institute

Austin, Texas, United States

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Houston Methodist Neurological Institute

Houston, Texas, United States

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Box Hill Hospital

Box Hill, , Australia

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The Alfred Hospital

Melbourne, , Australia

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Gold Coast University Hospital

Southport, , Australia

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Universitätsklinikum AKH Wien

Vienna, , Austria

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UZ Leuven

Leuven, , Belgium

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Hôpital de la Citadelle

Liège, , Belgium

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Maritime Neurology

Halifax, , Canada

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London Health Sciences Centre

London, , Canada

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Centre Hospitalier de l'Universite de Montreal

Montreal, , Canada

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Ottawa Hospital Research Institute

Ottawa, , Canada

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Hopital de L'enfant Jesus

Québec, , Canada

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Toronto General Hospital

Toronto, , Canada

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Xiangya Hospital Central South University

Changsha, , China

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Sichuan Academy of Medical Sciences & Sichuan Provincial People's Hospital

Chengdu, , China

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The First Affiliated Hospital of Chongqing Medical University

Chongqing, , China

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Fujian Medical University Union Hospital

Fuzhou, , China

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Guangdong Province Traditional Chinese Medical Hospital

Guangzhou, , China

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The First Affiliated Hospital of Guangzhou University Chinese Medicine

Guangzhou, , China

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Qilu Hospital of Shandong University

Jinan, , China

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The First Affiliated Hospital of Nanchang University - Xianghu Campus

Nanchang, , China

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Huashan Hospital Fudan University

Shanghai, , China

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Shijiazhuang People's Hospital - Fangbeilu Campus

Shijiazhuang, , China

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Tongji Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

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Renmin Hospital of Wuhan University - Main Campus

Wuhan, , China

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Cyprus Institute of Neurology and Genetics

Égkomi, , Cyprus

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Fakultni nemocnice Brno

Brno, , Czechia

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Nemocnice Pardubickeho kraje, a.s., Pardubicka nemocnice

Pardubice, , Czechia

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Aarhus Universitetshospital

Aarhus N, , Denmark

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Rigshospitalet

Copenhagen, , Denmark

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Turun Yliopistollinen Keskussairaala

Turku, , Finland

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Hôpital Fondation Adolphe de Rothschild

Paris, , France

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Petre Sarajishvili Institute of Neurology

Tbilisi, , Georgia

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New Hospitals

Tbilisi, , Georgia

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Pineo Medical Ecosystem

Tbilisi, , Georgia

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LLC Caucasus Medical Centre

Tbilisi, , Georgia

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Charité - Universitätsmedizin Berlin

Berlin, , Germany

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Universität Georg August

Göttingen, , Germany

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Eginitio Hospital

Athens, , Greece

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University General Hospital of Patras

Pátrai, , Greece

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ASST Papa Giovanni XXIII - Ospedale Papa Giovanni XXIII

Bergamo, , Italy

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IRCCS Istituto dell Scienze Neurologiche di Bologna

Bologna, , Italy

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Ospedale San Raffaele S.r.l.

Milan, , Italy

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Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, , Italy

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AORN Antonio Cardarelli

Napoli, , Italy

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Azienda Ospedaliero-Universitaria Sant'Andrea

Roma, , Italy

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Chiba University Hospital

Chūōku, , Japan

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Kyushu University Hospital

Fukuoka, , Japan

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General Hanamaki Hospital

Hanamaki-shi, , Japan

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Hiroshima University Hospital

Hiroshima, , Japan

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Saitama Medical Center

Kawagoe, , Japan

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National Hospital Organization Utano National Hospital

Kyoto, , Japan

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IUHW Narita Hospital

Narita, , Japan

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National Hospital Organization Hokkaido Medical Center

Sapporo, , Japan

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Kindai University Hospital

Sayama, , Japan

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Tokyo Medical University Hospital

Shinjuku-Ku, , Japan

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Osaka University Hospital

Suita-Shi, , Japan

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Leids Universitair Medisch Centrum

Leiden, , Netherlands

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MICS Centrum Medyczne Bydgoszcz

Bydgoszcz, , Poland

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Centrum Medyczne Neurologia Slaska

Katowice, , Poland

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SP ZOZ Szpital Uniwersytecki

Krakow, , Poland

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Krakowska Akademia Neurologii

Krakow, , Poland

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CLINIREM Sp z o.o.

Lublin, , Poland

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ULS de Santa Maria, EPE - Hospital de Santa Maria

Lisbon, , Portugal

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ULS de Santo António, EPE - Hospital de Santo António

Porto, , Portugal

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University Clinical Center of Serbia

Belgrade, , Serbia

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University Clinical Center Nis

Niš, , Serbia

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Kyungpook National University Chilgok hospital

Daegu, , South Korea

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Korea University Anam Hospital

Seoul, , South Korea

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Severance Hospital Yonsei University Health System

Seoul, , South Korea

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Hospital Universitario Vall d'Hebron

Barcelona, , Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Clinico San Carlos

Madrid, , Spain

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Hospital Universitario Ramon y Cajal

Madrid, , Spain

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Hospital Universitario de Donostia

San Sebastián, , Spain

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Hospital Clinico Universitario de Valencia

Valencia, , Spain

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Sahlgrenska Universitetssjukhuset

Gothenburg, , Sweden

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Mediclinic Parkview

Dubai, , United Arab Emirates

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Royal Sussex County Hospital

Brighton, , United Kingdom

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Panthera Biopartners - Glasgow

Glasgow, , United Kingdom

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Leeds General Infirmary

Leeds, , United Kingdom

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Dementech Neurosciences Clinical Academic Centre

London, , United Kingdom

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Southampton General Hospital

Southampton, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada China Cyprus Czechia Denmark Finland France Georgia Germany Greece Italy Japan Netherlands Poland Portugal Serbia South Korea Spain Sweden United Arab Emirates United Kingdom

Other Identifiers

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2024-514133-38-00

Identifier Type: CTIS

Identifier Source: secondary_id

ARGX-113-2315

Identifier Type: -

Identifier Source: org_study_id

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