An Efficacy and Safety Study of ARGX-113 in Patients With Myasthenia Gravis Who Have Generalized Muscle Weakness

NCT ID: NCT03669588

Last Updated: 2022-02-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

167 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-08-22

Study Completion Date

2020-04-06

Brief Summary

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A randomized, double-blind, placebo controlled, multicenter Phase 3 trial to evaluate the efficacy, safety, tolerability, quality of life and impact on normal daily activities of ARGX-113 in patients with gMG.

Detailed Description

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Conditions

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Generalized Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ARGX-113

Group Type EXPERIMENTAL

ARGX-113

Intervention Type BIOLOGICAL

Intravenous administration of ARGX-113

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Intravenous administration of placebo

Interventions

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ARGX-113

Intravenous administration of ARGX-113

Intervention Type BIOLOGICAL

Placebo

Intravenous administration of placebo

Intervention Type BIOLOGICAL

Other Intervention Names

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efgartigimod

Eligibility Criteria

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Inclusion Criteria

1. Patients with the ability to understand the requirements of the trial, provide written informed consent, and comply with the trial protocol procedures.
2. Male or female patients aged ≥ 18 years.
3. Diagnosis of MG with generalized muscle weakness meeting the clinical criteria for diagnosis of MG as defined by the Myasthenia Gravis Foundation of America (MGFA) class II, III, IVa and IVb.

Exclusion Criteria

1. Pregnant and lactating women, and those intending to become pregnant during the trial or within 90 days after the last dosing.
2. Male patients who are sexually active and do not intend to use effective methods of contraception during the trial or within 90 days after the last dosing or male patients who plan to donate sperm during the trial or within 90 days after the last dosing.
3. MGFA Class I and V patients.
4. Patients with worsening muscle weakness secondary to concurrent infections or medications.
5. Patients with known seropositivity or who test positive for an active viral infection at Screening with:

* Hepatitis B Virus (HBV) (except patients who are seropositive because of HBV vaccination)
* Hepatitis C Virus (HCV)
* Human Immunodeficiency Virus (HIV)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Antonio Guglietta, MD

Role: STUDY_DIRECTOR

argenx

Locations

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Investigator Site 29

Phoenix, Arizona, United States

Site Status

Investigator Site 66

Carlsbad, California, United States

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Investigator Site 5

Los Angeles, California, United States

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Investigator Site 49

Los Angeles, California, United States

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Investigator Site 18

Orange, California, United States

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Investigator Site 40

Palo Alto, California, United States

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Investigator Site 59

San Francisco, California, United States

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Investigator Site 58

Aurora, Colorado, United States

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Investigator Site 34

Jacksonville, Florida, United States

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Investigator Site 4

Tampa, Florida, United States

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Investigator Site 30

Springfield, Illinois, United States

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Investigator Site 25

Iowa City, Iowa, United States

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Investigator Site 21

Kansas City, Kansas, United States

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Investigator Site 27

Boston, Massachusetts, United States

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Investigator Site 48

Detroit, Michigan, United States

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Investigator Site 53

Buffalo, New York, United States

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Investigator Site 3

Chapel Hill, North Carolina, United States

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Investigator Site 20

Cleveland, Ohio, United States

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Investigator Site 9

Portland, Oregon, United States

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Investigator Site 17

Charleston, South Carolina, United States

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Investigator Site

Cordova, Tennessee, United States

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Investigator Site 44

Houston, Texas, United States

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Investigator Site 6

San Antonio, Texas, United States

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Investigator Site 2

Charlottesville, Virginia, United States

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Investigator Site 16

Seattle, Washington, United States

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Investigator Site 11

Edegem, , Belgium

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Investigator Site 8

Ghent, , Belgium

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Investigator Site 38

Edmonton, Alberta, Canada

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Investigator Site 24

Toronto, Ontario, Canada

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Investigator Site 22

Montreal, Quebec, Canada

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Investigator Site 32

Brno, , Czechia

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Investigator Site 35

Ostrava-Poruba, , Czechia

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Investigator Site 51

Prague, , Czechia

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Investigator Site 36

Aarhus, , Denmark

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Investigator Site 15

Copenhagen, , Denmark

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Investigator Site 13

Bordeaux, , France

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Investigator Site 52

Marseille, , France

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Investigator Site 46

Tbilisi, , Georgia

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Investigator Site 45

Tbilisi, , Georgia

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Investigator Site 47

Tbilisi, , Georgia

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Investigator Site 33

Berlin, , Germany

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Investigator Site 55

Budapest, , Hungary

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Investigator Site 54

Szeged, , Hungary

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Investigator Site 10

Milan, , Italy

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Investigator Site 12

Napoli, , Italy

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Investigator Site 42

Chiba, Chiba, Japan

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Investigator Site 26

Sapporo, Hokkaido, Japan

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Investigator Site 19

Hanamaki, Iwate, Japan

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Investigator Site 43

Sendai, Miyagi, Japan

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Investigator Site 28

Ōsaka-sayama, Osaka, Japan

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Investigator Site 50

Suita, Osaka, Japan

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Investigator Site 31

Meguro City, Tokyo, Japan

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Investigator Site 41

Minato-Ku, Tokyo, Japan

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Investigator Site 39

Shinjuku-Ku, Tokyo, Japan

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Investigator Site 37

Leiden, , Netherlands

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Investigator Site 7

Gdansk, , Poland

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Investigator Site 57

Katowice, , Poland

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Investigator Site 14

Krakow, , Poland

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Investigator Site 23

Warsaw, , Poland

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Investigator Site 64

Krasnoyarsk, , Russia

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Investigator Site 62

Nizhny Novgorod, , Russia

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Investigator Site 65

Novosibirsk, , Russia

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Investigator Site 60

Samara, , Russia

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Investigator Site 61

Belgrade, , Serbia

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Investigator Site 63

Edgbaston, , United Kingdom

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Investigator Site 56

Liverpool, , United Kingdom

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Countries

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United States Belgium Canada Czechia Denmark France Georgia Germany Hungary Italy Japan Netherlands Poland Russia Serbia United Kingdom

References

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Janssen MF, Dewilde S, Wolfe GI, Muppidi S, Phillips G. Psychometric properties of MG-ADL items and MG-ADL score: An assessment of distributional characteristics, validity and factor structure in two large datasets. J Neurol Sci. 2024 Aug 15;463:123135. doi: 10.1016/j.jns.2024.123135. Epub 2024 Jul 22.

Reference Type DERIVED
PMID: 39068745 (View on PubMed)

Howard JF Jr, Bril V, Vu T, Karam C, Peric S, Margania T, Murai H, Bilinska M, Shakarishvili R, Smilowski M, Guglietta A, Ulrichts P, Vangeneugden T, Utsugisawa K, Verschuuren J, Mantegazza R; ADAPT Investigator Study Group. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial. Lancet Neurol. 2021 Jul;20(7):526-536. doi: 10.1016/S1474-4422(21)00159-9.

Reference Type DERIVED
PMID: 34146511 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002132-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ARGX-113-1704

Identifier Type: -

Identifier Source: org_study_id

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