A Study to Assess the Long-term Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod in Adults With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP, an Autoimmune Disorder That Affects the Peripheral Nerves)

NCT ID: NCT04280718

Last Updated: 2025-06-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

229 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-18

Study Completion Date

2027-04-30

Brief Summary

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This is the open-label extension study of phase II ARGX-113-1802 to evaluate the long-term safety and efficacy of the subcutaneous formulation of efgartigimod in adults with CIDP.

Patients already stabilized on efgartigimod PH20 SC will also have the opportunity to participate in a sub study to explore less frequent dosing of efgartigimod PH20 SC.

Detailed Description

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Conditions

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Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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efgartigimod PH20 SC

Patients treated with efgartigimod PH20 SC

Group Type EXPERIMENTAL

Efgartigimod PH20 SC

Intervention Type BIOLOGICAL

Subcutaneous administration of efgartigimod

Interventions

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Efgartigimod PH20 SC

Subcutaneous administration of efgartigimod

Intervention Type BIOLOGICAL

Other Intervention Names

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ARGX-113

Eligibility Criteria

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Inclusion Criteria

1. Ability to understand the requirements of the trial, provide written informed consent (including consent for the use and disclosure of research-related health information), willingness and ability to comply with the trial protocol procedures (including required trial visits) of this trial.
2. Male or female patient with one of the following options:

* Have completed the Week-48 visit of Stage B of the ARGX-113-1802 trial and are considered to be eligible for treatment with efgartigimod PH20 SC; or
* Have deteriorated during Stage B of the ARGX-113-1802 trial and are considered to be eligible for treatment with efgartigimod PH20 SC, or
* Have been offered the participation in the OLE trial due to early termination of the ARGX-113-1802 trial (because sufficient events for the primary endpoint analysis of the that trial have been reached and it is stopped) and are considered to be eligible for treatment with efgartigimod PH20 SC treatment; or
* Have completed the Week-48 visit of the previous cycle of the OLE trial and are considered to be eligible to continue with efgartigimod PH20 SC treatment.
3. Women of childbearing potential who have a negative urine pregnancy test at baseline before IMP administration.
4. Women of childbearing potential must use an acceptable method of contraception from signing the ICF until the date of the last administration of IMP.

Exclusion Criteria

1. Week-48/ED visit in the ARGX-113-1802 trial or the Week-48 visit of the previous OLE participation occurred more than 14 days prior to SD1 of the OLE trial or the start of a new treatment cycle in the OLE trial and more than 21 days since the last dose of IMP.
2. Pregnant and lactating women and those intending to become pregnant during the trial.
3. Patients with clinical evidence of other significant serious disease or patients who underwent a recent or have a planned major surgery, or patients who (intend to) use prohibited medications (see protocol) and therapies during the trial, or any other reason which could confound the results of the trial or put the patient at undue risk.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Investigator site 0010065

Birmingham, Alabama, United States

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Investigator site 0010013

Phoenix, Arizona, United States

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Investigator site 0010055

Scottsdale, Arizona, United States

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Investigator site 0010032

Carlsbad, California, United States

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Investigator site 10190

Pomona, California, United States

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Investigator site 0010160

Rancho Mirage, California, United States

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Investigator site 0010071

San Francisco, California, United States

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Investigator site 0010057

Centennial, Colorado, United States

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Investigator site 0010072

Boca Raton, Florida, United States

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Investigator site 0010144

Coral Springs, Florida, United States

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Investigator site 0010023

Jacksonville, Florida, United States

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Investigator site 0010068

Maitland, Florida, United States

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Investigator site 0010059

Miami, Florida, United States

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Investigator site 0010006

Tampa, Florida, United States

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Investigator site 0010011

Iowa City, Iowa, United States

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Investigator site 0010015

Fairway, Kansas, United States

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Investigator site 10147

Lexington, Kentucky, United States

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Investigator site 10168

New York, New York, United States

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Investigator site 0010003

Chapel Hill, North Carolina, United States

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Investigator site 0010064

Columbus, Ohio, United States

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Investigator site 0010007

Philadelphia, Pennsylvania, United States

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Investigator site 0010047

Philadelphia, Pennsylvania, United States

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Investigator Site 0010066

Austin, Texas, United States

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Investigator site 0010009

San Antonio, Texas, United States

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Investigator site 0010061

Richmond, Virginia, United States

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Investigator site 0430007

Innsbruck, , Austria

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Investigator site 0430008

Linz, , Austria

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Investigator site 0430005

Vienna, , Austria

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Investigator site 0320016

Edegem, , Belgium

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Investigator site 0320009

Leuven, , Belgium

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Investigator site 320024

Liège, , Belgium

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Investigator site 320022

Woluwe-Saint-Lambert, , Belgium

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Investigator site 3590007

Pleven, , Bulgaria

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Investigator site 3590005

Sofia, , Bulgaria

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Investigator site 3590008

Sofia, , Bulgaria

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Investigator site 3590006

Sofia, , Bulgaria

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Investigator site 0860033

Beijing, , China

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Investigator site 860041

Changsha, , China

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Investigator site 0860036

Chengdu, , China

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Investigator site 860049

Chifeng, , China

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Investigator site 0860038

Fuzhou, , China

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Investigator site 0860050

Guangzhou, , China

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Investigator site 0860032

Guanzhou, , China

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Investigator site 0860045

Guiyang, , China

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Investigator site 0860035

Hangzhou, , China

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Investigator site 0860031

Jinan, , China

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Investigator site 0860040

Nanchang, , China

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Investigator site 0860043

Nanjing, , China

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Investigator site 0860028

Shanghai, , China

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Investigator site 860047

Shanghai, , China

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Investigator site 0860042

Tianjin, , China

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Investigator site 0860034

Wuhan, , China

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Investigator site 0860029

Wuhan, , China

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Investigator site 0860048

Xi'an, , China

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Investigator site 0860054

Xianyang, , China

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Investigator site 4200010

Hradec Králové, , Czechia

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Investigator site 0450002

Aarhus, , Denmark

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Investigator site 0450001

Copenhagen, , Denmark

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Investigator site 0450003

Odense, , Denmark

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Investigator site 00330034

Angers, , France

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Investigator site 0330013

Bordeaux, , France

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Investigator site 330033

Clermont-Ferrand, , France

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Investigator site 0330023

Le Kremlin-Bicêtre, , France

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Investigator site 0330024

Limoges, , France

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Investigator site 330022

Nantes, , France

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Investigator site 0330021

Nice, , France

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Investigator site 0330035

Paris, , France

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Investigator site 0330020

Strasbourg, , France

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Investigator site 9950020

Kutaisi, , Georgia

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Investigator site 9950004

Tbilisi, , Georgia

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Investigator site 9950005

Tbilisi, , Georgia

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Investigator site 9950002

Tbilisi, , Georgia

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Investigator Site 9950003

Tbilisi, , Georgia

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Investigator site 490044

Bochum, , Germany

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Investigator site 0490013

Cologne, , Germany

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Investigator site 490045

Essen, , Germany

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Investigator site 490021

Göttingen, , Germany

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Investigator site 0490016

Kiel, , Germany

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Investigator site 0490019

Potsdam, , Germany

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Investigator site 9720004

Tel Aviv, , Israel

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Investigator site 0390022

Brescia, , Italy

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Investigator site 390029

Florence, , Italy

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Investigator site 0390024

Genova, , Italy

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Investigator site 390027

Messina, , Italy

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Investigator site 0390003

Milan, , Italy

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Investigator site 0390026

Milan, , Italy

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Investigator site 0390023

Pisa, , Italy

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Investigator site 0390008

Roma, , Italy

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Investigator site 0390042

Torino, , Italy

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Investigator site 0810035

Bunkyō City, , Japan

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Investigator site 0810002

Chiba, , Japan

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Investigator site 0810030

Fuchū, , Japan

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Investigator site 0810031

Fukuoka, , Japan

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Investigator site 0810065

Ginowan, , Japan

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Investigator site 0810066

Hakodate, , Japan

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Investigator site 0810058

Hiroshima, , Japan

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Investigator site 0810029

Kawagoe, , Japan

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Investigator site 0810026

Kodaira, , Japan

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Investigator site 810061

Kyoto, , Japan

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Investigator site 0810027

Mibu, , Japan

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Investigator site 0810032

Nagoya, , Japan

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Investigator site 0810003

Osaka, , Japan

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Investigator site 0810007

Osaka, , Japan

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Investigator site 0810063

Suita, , Japan

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Investigator site 0810036

tabashi City, , Japan

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Investigator site 0810064

Tokushima, , Japan

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Investigator site 0810060

Yokohama, , Japan

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Investigator site 31

Riga, , Latvia

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Investigator site 0310010

Amsterdam, , Netherlands

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Investigator site 0310011

Rotterdam, , Netherlands

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Investigator site 0480024

Krakow, , Poland

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Investigator site 0480018

Krakow, , Poland

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Investigator site 0480020

Lodz, , Poland

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Investigator Site 0480017

Lublin, , Poland

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Investigator site 0480022

Warsaw, , Poland

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Investigator site 040002

Brasov, , Romania

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Investigator site 040001

Bucharest, , Romania

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Investigator site 040004

Constanța, , Romania

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Investigator site 040003

Timișoara, , Romania

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Investigator site 070017

Kazan', , Russia

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Investigator site 0070023

Kazan', , Russia

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Investigator site 0070020

Moscow, , Russia

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Investigator site 70021

Moscow, , Russia

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Investigator site 0070019

Rostov-on-Don, , Russia

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Investigator site 0070014

Saint Petersburg, , Russia

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Investigator site 0070021

Saransk, , Russia

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Investigator site 3810001

Belgrade, , Serbia

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Investigator site 3810003

Belgrade, , Serbia

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Investigator site 3810004

Kragujevac, , Serbia

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Investigator site 0340021

Badalona, , Spain

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Investigator site 0340038

Barcelona, , Spain

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Investigator site 0340018

Madrid, , Spain

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Investigator site 8860013

Tainan City, , Taiwan

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Investigator site 8860012

Taipei, , Taiwan

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Investigator site 8860016

Taipei, , Taiwan

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Investigator site 8860017

Taoyuan District, , Taiwan

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Investigator site 900025

Bursa, , Turkey (Türkiye)

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Investigator site 900021

Izmir, , Turkey (Türkiye)

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Investigator site 900022

Samsun, , Turkey (Türkiye)

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Investigator Site 3800012

Dnipro, , Ukraine

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Investigator Site 3800010

Ivano-Frankivsk, , Ukraine

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Investigator site 3100013

Kyiv, , Ukraine

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Investigator site 3800008

Lutsk, , Ukraine

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Investigator site 3800011

Zaporizhzhya, , Ukraine

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Investigator site 440026

London, , United Kingdom

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Investigator site 0440016

Oxford, , United Kingdom

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Investigator site 0440018

Sheffield, , United Kingdom

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Countries

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United States Austria Belgium Bulgaria China Czechia Denmark France Georgia Germany Israel Italy Japan Latvia Netherlands Poland Romania Russia Serbia Spain Taiwan Turkey (Türkiye) Ukraine United Kingdom

Other Identifiers

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2019-003107-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ARGX-113-1902

Identifier Type: -

Identifier Source: org_study_id

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